CN112567035A - 肌萎缩侧索硬化症及脊髓相关病症的治疗 - Google Patents

肌萎缩侧索硬化症及脊髓相关病症的治疗 Download PDF

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CN112567035A
CN112567035A CN201980052747.2A CN201980052747A CN112567035A CN 112567035 A CN112567035 A CN 112567035A CN 201980052747 A CN201980052747 A CN 201980052747A CN 112567035 A CN112567035 A CN 112567035A
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aav
vhu
sequence
clv
nucleotides
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D·W-Y·沙
陈庆敏
J·卡罗尔索珀
H·帕泽克
侯金兆
S·M·赫尔施
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Voyager Therapeutics Inc
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CN201980052747.2A 2018-07-02 2019-07-02 肌萎缩侧索硬化症及脊髓相关病症的治疗 Pending CN112567035A (zh)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US201862693040P 2018-07-02 2018-07-02
US62/693,040 2018-07-02
US201862746104P 2018-10-16 2018-10-16
US62/746,104 2018-10-16
PCT/US2019/040230 WO2020010042A1 (en) 2018-07-02 2019-07-02 Treatment of amyotrophic lateral sclerosis and disorders associated with the spinal cord

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CN112567035A true CN112567035A (zh) 2021-03-26

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US (1) US20210254103A1 (https=)
EP (1) EP3818161A1 (https=)
JP (1) JP7565218B2 (https=)
CN (1) CN112567035A (https=)
AU (1) AU2019299861A1 (https=)
CA (1) CA3103963A1 (https=)
WO (1) WO2020010042A1 (https=)

Cited By (1)

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WO2025045130A1 (zh) * 2023-08-29 2025-03-06 石药集团中奇制药技术（石家庄）有限公司 一种抑制sod1基因表达的dsrna分子及其应用

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CN119876138A (zh) 2014-11-14 2025-04-25 沃雅戈治疗公司 调节性多核苷酸
CA3193811A1 (en) 2014-11-14 2016-05-19 Voyager Therapeutics, Inc. Compositions and methods of treating amyotrophic lateral sclerosis (als)
CA3024448C (en) 2016-05-18 2025-09-09 Voyager Therapeutics, Inc. MODULATING POLYNUCLEOTIDES
EP3618839A4 (en) 2017-05-05 2021-06-09 Voyager Therapeutics, Inc. COMPOSITIONS AND METHODS OF TREATMENT OF AMYOTROPHIC LATERAL SCLEROSIS (ALS)
TW202413649A (zh) 2017-10-16 2024-04-01 美商航海家醫療公司 肌萎縮性脊髓側索硬化症(als)之治療
WO2019079242A1 (en) 2017-10-16 2019-04-25 Voyager Therapeutics, Inc. TREATMENT OF AMYOTROPHIC LATERAL SCLEROSIS (ALS)
WO2020223296A1 (en) * 2019-04-29 2020-11-05 Voyager Therapeutics, Inc. Treatment of amyotrophic lateral sclerosis and disorders associated with the spinal cord
WO2022174000A2 (en) 2021-02-12 2022-08-18 Alnylam Pharmaceuticals, Inc. Superoxide dismutase 1 (sod1) irna compositions and methods of use thereof for treating or preventing superoxide dismutase 1- (sod1-) associated neurodegenerative diseases
WO2024226761A2 (en) 2023-04-26 2024-10-31 Voyager Therapeutics, Inc. Compositions and methods for treating amyotrophic lateral sclerosis

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