JP7037574B2 - 脊髄性筋萎縮症の治療に有用な組成物 - Google Patents

脊髄性筋萎縮症の治療に有用な組成物 Download PDF

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JP7037574B2
JP7037574B2 JP2019547087A JP2019547087A JP7037574B2 JP 7037574 B2 JP7037574 B2 JP 7037574B2 JP 2019547087 A JP2019547087 A JP 2019547087A JP 2019547087 A JP2019547087 A JP 2019547087A JP 7037574 B2 JP7037574 B2 JP 7037574B2
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aavhu68
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ウイルソン，ジェームス・エム
ヒンデラー，クリスチャン
カッツ，ネイサン
ワン，チャン
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ザ・トラステイーズ・オブ・ザ・ユニバーシテイ・オブ・ペンシルベニア
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JP2019547087A 2017-02-28 2018-02-27 脊髄性筋萎縮症の治療に有用な組成物 Active JP7037574B2 (ja)

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US201762464756P 2017-02-28 2017-02-28
US62/464,756 2017-02-28
US201762515902P 2017-06-06 2017-06-06
US62/515,902 2017-06-06
US201862618437P 2018-01-17 2018-01-17
US62/618,437 2018-01-17
PCT/US2018/019996 WO2018160585A2 (en) 2017-02-28 2018-02-27 Compositions useful in treatment of spinal muscular atrophy

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CN (1) CN110741089B (enExample)
AU (1) AU2018227442B2 (enExample)
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CN112852882A (zh) * 2021-02-04 2021-05-28 中吉智药(南京)生物技术有限公司 一种杆状病毒感染昆虫细胞生产aav基因药物的系统及方法
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CN118119710A (zh) * 2021-10-15 2024-05-31 上海天泽云泰生物医药有限公司 用于治疗脊髓性肌萎缩的重组腺相关病毒载体
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EP4437113A4 (en) * 2021-11-23 2026-04-08 Univ Massachusetts GENE THERAPY FOR SPINAL MUSCULAR ATROPHY
CN114177346B (zh) * 2021-12-24 2023-05-26 中国人民解放军军事科学院军事医学研究院 一种止血组合物及止血贴与其应用
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