CA3055619A1 - Compositions useful in treatment of spinal muscular atrophy - Google Patents
Compositions useful in treatment of spinal muscular atrophy Download PDFInfo
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- CA3055619A1 CA3055619A1 CA3055619A CA3055619A CA3055619A1 CA 3055619 A1 CA3055619 A1 CA 3055619A1 CA 3055619 A CA3055619 A CA 3055619A CA 3055619 A CA3055619 A CA 3055619A CA 3055619 A1 CA3055619 A1 CA 3055619A1
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- aavhu68
- acid sequence
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Classifications
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- A61K48/005—Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases; Gene therapy characterised by an aspect of the 'active' part of the composition delivered, i.e. the nucleic acid delivered
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- C07K14/435—Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof from animals; from humans
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- C12—BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
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| US11827906B2 (en) | 2017-02-28 | 2023-11-28 | The Trustees Of The University Of Pennsylvania | Adeno-associated virus (AAV) clade f vector and uses therefor |
| JOP20190200A1 (ar) * | 2017-02-28 | 2019-08-27 | Univ Pennsylvania | تركيبات نافعة في معالجة ضمور العضل النخاعي |
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| CN114177346B (zh) * | 2021-12-24 | 2023-05-26 | 中国人民解放军军事科学院军事医学研究院 | 一种止血组合物及止血贴与其应用 |
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| JP7483774B2 (ja) | 2024-05-15 |
| BR112019016444A2 (pt) | 2020-04-07 |
| PE20191261A1 (es) | 2019-09-18 |
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