JP6822841B2 - オルニチントランスカルバミラーゼ（ｏｔｃ）欠損症の処置において有用な組成物 - Google Patents

オルニチントランスカルバミラーゼ（ｏｔｃ）欠損症の処置において有用な組成物 Download PDF

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JP6822841B2
JP6822841B2 JP2016556768A JP2016556768A JP6822841B2 JP 6822841 B2 JP6822841 B2 JP 6822841B2 JP 2016556768 A JP2016556768 A JP 2016556768A JP 2016556768 A JP2016556768 A JP 2016556768A JP 6822841 B2 JP6822841 B2 JP 6822841B2
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nucleic acid
sequence
hotc
acid sequence
seq
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JP2017512466A5 (OSRAM
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ワング，リリ
ウイルソン，ジエームス・エム
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ザ・トラステイーズ・オブ・ザ・ユニバーシテイ・オブ・ペンシルベニア
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JP2016556768A 2014-03-09 2015-03-09 オルニチントランスカルバミラーゼ（ｏｔｃ）欠損症の処置において有用な組成物 Active JP6822841B2 (ja)

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US201461950157P 2014-03-09 2014-03-09
US61/950,157 2014-03-09
PCT/US2015/019513 WO2015138348A1 (en) 2014-03-09 2015-03-09 Compositions useful in treatment of ornithine transcarbamylase (otc) deficiency

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