JP2025507338A5 - - Google Patents

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Publication number
JP2025507338A5
JP2025507338A5 JP2024547150A JP2024547150A JP2025507338A5 JP 2025507338 A5 JP2025507338 A5 JP 2025507338A5 JP 2024547150 A JP2024547150 A JP 2024547150A JP 2024547150 A JP2024547150 A JP 2024547150A JP 2025507338 A5 JP2025507338 A5 JP 2025507338A5
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JP
Japan
Application number
JP2024547150A
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Japanese (ja)
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JP2025507338A (ja
JPWO2023154693A5 (https=
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Publication date
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Priority claimed from PCT/US2023/062101 external-priority patent/WO2023154693A1/en
Publication of JP2025507338A publication Critical patent/JP2025507338A/ja
Publication of JP2025507338A5 publication Critical patent/JP2025507338A5/ja
Publication of JPWO2023154693A5 publication Critical patent/JPWO2023154693A5/ja
Pending legal-status Critical Current

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JP2024547150A 2022-02-08 2023-02-07 Aavカプシドバリアント及びその使用 Pending JP2025507338A (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US202263307742P 2022-02-08 2022-02-08
US63/307,742 2022-02-08
US202263339574P 2022-05-09 2022-05-09
US63/339,574 2022-05-09
PCT/US2023/062101 WO2023154693A1 (en) 2022-02-08 2023-02-07 Aav capsid variants and uses thereof

Publications (3)

Publication Number Publication Date
JP2025507338A JP2025507338A (ja) 2025-03-18
JP2025507338A5 true JP2025507338A5 (https=) 2026-02-05
JPWO2023154693A5 JPWO2023154693A5 (https=) 2026-02-05

Family

ID=85505478

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024547150A Pending JP2025507338A (ja) 2022-02-08 2023-02-07 Aavカプシドバリアント及びその使用

Country Status (11)

Country Link
US (1) US20250161485A1 (https=)
EP (1) EP4476241A1 (https=)
JP (1) JP2025507338A (https=)
KR (1) KR20240161976A (https=)
CN (1) CN119072486A (https=)
AU (1) AU2023217698A1 (https=)
CA (1) CA3249551A1 (https=)
IL (1) IL314156A (https=)
MX (1) MX2024009660A (https=)
TW (1) TW202346599A (https=)
WO (1) WO2023154693A1 (https=)

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Publication number Priority date Publication date Assignee Title
EP3861010A1 (en) 2018-10-02 2021-08-11 Voyager Therapeutics, Inc. Redirection of tropism of aav capsids
CN116096734A (zh) 2020-05-13 2023-05-09 沃雅戈治疗公司 Aav衣壳的向性的重定向
MX2024004936A (es) 2021-11-02 2024-05-08 Voyager Therapeutics Inc Variantes de capsides de aav y sus usos.
WO2025038802A1 (en) * 2023-08-16 2025-02-20 Voyager Therapeutics, Inc. Compositions and methods for the treatment of disorders related to ataxin-2
WO2025038796A1 (en) * 2023-08-16 2025-02-20 Voyager Therapeutics, Inc. Compositions and methods for the treatment of disorders related to cdkl5 deficiency
WO2025038795A1 (en) * 2023-08-16 2025-02-20 Voyager Therapeutics, Inc. Compositions and methods for the treatment of disorders related to dystrophia myotonica protein kinase
WO2025038805A1 (en) * 2023-08-16 2025-02-20 Voyager Therapeutics, Inc. Compositions and methods for the treatment of disorders related to glucosylceramidase beta 1 deficiency
WO2025038430A1 (en) * 2023-08-16 2025-02-20 Voyager Therapeutics, Inc. Aav capsid variants and uses thereof
AR133562A1 (es) * 2023-08-16 2025-10-08 Voyager Therapeutics Inc Composiciones y métodos para el tratamiento de trastornos relacionados con la deficiencia de frataxina
CN117402222B (zh) * 2023-11-17 2024-03-29 广州派真生物技术有限公司 腺相关病毒突变体及其应用
KR102844372B1 (ko) * 2023-12-06 2025-08-11 주식회사 글루진테라퓨틱스 뇌 성상교세포 특이적 유전자 전달이 가능한 아데노부속바이러스 변이체와 이의 응용
US20250273289A1 (en) * 2024-02-23 2025-08-28 Tata Consultancy Services Limited Insilico method and system for designing a baseline peptide bioreceptor for sensing a biomarker for dysglycemic disorders
CN119552222B (zh) * 2025-01-24 2025-08-08 中国人民解放军军事科学院军事医学研究院 腺相关病毒视网膜细胞嗜性衣壳突变体及应用

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