JP2021534154A5 - - Google Patents

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Publication number
JP2021534154A5
JP2021534154A5 JP2021507686A JP2021507686A JP2021534154A5 JP 2021534154 A5 JP2021534154 A5 JP 2021534154A5 JP 2021507686 A JP2021507686 A JP 2021507686A JP 2021507686 A JP2021507686 A JP 2021507686A JP 2021534154 A5 JP2021534154 A5 JP 2021534154A5
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JP
Japan
Prior art keywords
aso
administered
combination according
subject
raav
Prior art date
Application number
JP2021507686A
Other languages
English (en)
Japanese (ja)
Other versions
JPWO2020037161A5 (https=
JP2021534154A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2019/046720 external-priority patent/WO2020037161A1/en
Publication of JP2021534154A publication Critical patent/JP2021534154A/ja
Publication of JPWO2020037161A5 publication Critical patent/JPWO2020037161A5/ja
Publication of JP2021534154A5 publication Critical patent/JP2021534154A5/ja
Priority to JP2024096579A priority Critical patent/JP2024111074A/ja
Priority to JP2025187453A priority patent/JP2026009384A/ja
Withdrawn legal-status Critical Current

Links

JP2021507686A 2018-08-15 2019-08-15 脊髄性筋萎縮症のための併用療法 Withdrawn JP2021534154A (ja)

Priority Applications (2)

Application Number Priority Date Filing Date Title
JP2024096579A JP2024111074A (ja) 2018-08-15 2024-06-14 脊髄性筋萎縮症のための併用療法
JP2025187453A JP2026009384A (ja) 2018-08-15 2025-11-06 脊髄性筋萎縮症のための併用療法

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US201862764893P 2018-08-15 2018-08-15
US62/764,893 2018-08-15
US201862783189P 2018-12-20 2018-12-20
US62/783,189 2018-12-20
PCT/US2019/046720 WO2020037161A1 (en) 2018-08-15 2019-08-15 Combination therapy for spinal muscular atrophy

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2024096579A Division JP2024111074A (ja) 2018-08-15 2024-06-14 脊髄性筋萎縮症のための併用療法

Publications (3)

Publication Number Publication Date
JP2021534154A JP2021534154A (ja) 2021-12-09
JPWO2020037161A5 JPWO2020037161A5 (https=) 2022-08-22
JP2021534154A5 true JP2021534154A5 (https=) 2022-08-22

Family

ID=69525927

Family Applications (3)

Application Number Title Priority Date Filing Date
JP2021507686A Withdrawn JP2021534154A (ja) 2018-08-15 2019-08-15 脊髄性筋萎縮症のための併用療法
JP2024096579A Pending JP2024111074A (ja) 2018-08-15 2024-06-14 脊髄性筋萎縮症のための併用療法
JP2025187453A Pending JP2026009384A (ja) 2018-08-15 2025-11-06 脊髄性筋萎縮症のための併用療法

Family Applications After (2)

Application Number Title Priority Date Filing Date
JP2024096579A Pending JP2024111074A (ja) 2018-08-15 2024-06-14 脊髄性筋萎縮症のための併用療法
JP2025187453A Pending JP2026009384A (ja) 2018-08-15 2025-11-06 脊髄性筋萎縮症のための併用療法

Country Status (4)

Country Link
US (1) US20210308281A1 (https=)
EP (1) EP3837374A4 (https=)
JP (3) JP2021534154A (https=)
WO (1) WO2020037161A1 (https=)

Families Citing this family (6)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
AU2020316997A1 (en) * 2019-07-19 2022-03-10 Biogen Ma Inc. Methods of treating or preventing spinal muscular atrophy
US20220280548A1 (en) * 2019-08-15 2022-09-08 Biogen Ma Inc. Combination therapy for spinal muscular atrophy
JP2023535832A (ja) * 2020-07-31 2023-08-21 ラクティゲン セラピューティクス Ｓａｒｎａとｍｒｎａ調節剤によるｓｍａの併用治療
WO2023168427A1 (en) 2022-03-03 2023-09-07 Yale University Compositions and methods for delivering therapeutic polynucleotides for exon skipping
WO2023240236A1 (en) 2022-06-10 2023-12-14 Voyager Therapeutics, Inc. Compositions and methods for the treatment of spinal muscular atrophy related disorders
IL326390A (en) 2023-08-10 2026-04-01 Univ Pennsylvania Compositions and methods for treating spinal muscular atrophy

Family Cites Families (5)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
PT3305302T (pt) * 2009-06-17 2018-12-14 Biogen Ma Inc Composições e métodos de modulação de excisões de smn2 em um sujeito
BR112018011975A2 (pt) * 2015-12-14 2018-12-11 Univ Pennsylvania composições úteis no tratamento de atrofia muscular espinhal
MX2020004830A (es) * 2017-11-08 2020-11-11 Avexis Inc Medios y metodo para preparar vectores virales y usos de los mismos.
CN112601557B (zh) * 2018-06-08 2025-06-06 诺华股份有限公司 用于测量药物产品效力的基于细胞的测定
WO2020113034A1 (en) * 2018-11-30 2020-06-04 Avexis, Inc. Aav viral vectors and uses thereof

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