JP2020527167A5 - - Google Patents

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Publication number
JP2020527167A5
JP2020527167A5 JP2020521498A JP2020521498A JP2020527167A5 JP 2020527167 A5 JP2020527167 A5 JP 2020527167A5 JP 2020521498 A JP2020521498 A JP 2020521498A JP 2020521498 A JP2020521498 A JP 2020521498A JP 2020527167 A5 JP2020527167 A5 JP 2020527167A5
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JP
Japan
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composition
viral vector
composition according
patient
effective amount
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JP2020521498A
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English (en)
Japanese (ja)
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JP2020527167A (ja
JP7193874B2 (ja
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Priority claimed from PCT/US2018/040913 external-priority patent/WO2019010301A1/en
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Publication of JP2020527167A5 publication Critical patent/JP2020527167A5/ja
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JP2020521498A 2017-07-06 2018-07-05 筋肉Aキナーゼアンカータンパク質(mAKAP)作用の阻害による心臓病の処置 Active JP7193874B2 (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201762529224P 2017-07-06 2017-07-06
US62/529,224 2017-07-06
PCT/US2018/040913 WO2019010301A1 (en) 2017-07-06 2018-07-05 TREATMENT OF CARDIOPATHIES BY INHIBITING THE ACTION OF PROTEINS FROM ANCHORING TO MUSCLE PROTEIN KINASES A (MAKAP)

Publications (3)

Publication Number Publication Date
JP2020527167A JP2020527167A (ja) 2020-09-03
JP2020527167A5 true JP2020527167A5 (https=) 2021-08-05
JP7193874B2 JP7193874B2 (ja) 2022-12-21

Family

ID=64904482

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2020521498A Active JP7193874B2 (ja) 2017-07-06 2018-07-05 筋肉Aキナーゼアンカータンパク質(mAKAP)作用の阻害による心臓病の処置

Country Status (7)

Country Link
US (1) US10907153B2 (https=)
EP (1) EP3658157B1 (https=)
JP (1) JP7193874B2 (https=)
AU (1) AU2018297274B2 (https=)
CA (1) CA3065816C (https=)
ES (1) ES2958662T3 (https=)
WO (1) WO2019010301A1 (https=)

Families Citing this family (5)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US9132174B2 (en) 2013-03-15 2015-09-15 Anchored Rsk3 Inhibitors, Llc Treatment of heart disease by inhibition of the action of ribosomal S6 kinase 3 (RSK3)
WO2020051296A1 (en) * 2018-09-06 2020-03-12 Icahn School Of Medicine At Mount Sinai Compositions and methods for the treatment of heart disease
CA3139974A1 (en) * 2019-05-15 2020-11-19 University Of Miami Treatment of heart disease by disruption of the anchoring of pp2a
EP4103214B1 (en) 2020-02-13 2026-04-29 Tenaya Therapeutics, Inc. Gene therapy vectors for treating heart disease
JP2026505638A (ja) * 2023-02-13 2026-02-16 シーアールアイ バイオテック,インコーポレイテッド 心筋細胞における選択的発現のためのヒトトロポニンt遺伝子のプロモーター-エンハンサー配列

Family Cites Families (7)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US6489125B1 (en) 2000-05-10 2002-12-03 The Trustees Of Columbia University In The City Of New York Methods for identifying chemical compounds that inhibit dissociation of FKBP12.6 binding protein from type 2 ryanodine receptor
AU2003295600A1 (en) * 2002-11-14 2004-06-15 Dharmacon, Inc. Functional and hyperfunctional sirna
JP2007505158A (ja) * 2003-05-21 2007-03-08 ボード オブ リージェンツ ザ ユニバーシティー オブ テキサス システム 心肥大および心不全の処置としてのプロテインキナーゼC−μ(PKD)の阻害
US9217155B2 (en) * 2008-05-28 2015-12-22 University Of Massachusetts Isolation of novel AAV'S and uses thereof
US8734809B2 (en) * 2009-05-28 2014-05-27 University Of Massachusetts AAV's and uses thereof
US20130136729A1 (en) 2011-11-11 2013-05-30 University of Virginia Patent Foundation, d/b/a University of Virginia Licensing & Ventures Group Compositions and methods for targeting and treating diseases and injuries using adeno-associated virus vectors
US9132174B2 (en) * 2013-03-15 2015-09-15 Anchored Rsk3 Inhibitors, Llc Treatment of heart disease by inhibition of the action of ribosomal S6 kinase 3 (RSK3)

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