JP2018509154A5 - - Google Patents
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- JP2018509154A5 JP2018509154A5 JP2017547425A JP2017547425A JP2018509154A5 JP 2018509154 A5 JP2018509154 A5 JP 2018509154A5 JP 2017547425 A JP2017547425 A JP 2017547425A JP 2017547425 A JP2017547425 A JP 2017547425A JP 2018509154 A5 JP2018509154 A5 JP 2018509154A5
- Authority
- JP
- Japan
- Prior art keywords
- vector
- nucleotide sequence
- mammal
- motomeko
- sequence encoding
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
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Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201562131661P | 2015-03-11 | 2015-03-11 | |
| US62/131,661 | 2015-03-11 | ||
| PCT/US2016/022072 WO2016145345A1 (en) | 2015-03-11 | 2016-03-11 | Rp2 and rpgr vectors for treating x-linked retinitis pigmentosa |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2020167984A Division JP2021019611A (ja) | 2015-03-11 | 2020-10-02 | Ｘ連鎖性網膜色素変性症の治療のためのｒｐ２及びｒｐｇｒベクター |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2018509154A JP2018509154A (ja) | 2018-04-05 |
| JP2018509154A5 true JP2018509154A5 (https=) | 2019-04-18 |
| JP6935049B2 JP6935049B2 (ja) | 2021-09-15 |
Family
ID=56879752
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2017547425A Active JP6935049B2 (ja) | 2015-03-11 | 2016-03-11 | Ｘ連鎖性網膜色素変性症の治療のためのｒｐ２及びｒｐｇｒベクター |
| JP2020167984A Pending JP2021019611A (ja) | 2015-03-11 | 2020-10-02 | Ｘ連鎖性網膜色素変性症の治療のためのｒｐ２及びｒｐｇｒベクター |
Family Applications After (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2020167984A Pending JP2021019611A (ja) | 2015-03-11 | 2020-10-02 | Ｘ連鎖性網膜色素変性症の治療のためのｒｐ２及びｒｐｇｒベクター |
Country Status (6)
| Country | Link |
|---|---|
| US (2) | US10646588B2 (https=) |
| EP (2) | EP3268481B1 (https=) |
| JP (2) | JP6935049B2 (https=) |
| AU (1) | AU2016228751B2 (https=) |
| CA (1) | CA2979229A1 (https=) |
| WO (1) | WO2016145345A1 (https=) |
Families Citing this family (6)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| EP3268481B1 (en) | 2015-03-11 | 2020-05-27 | The United States of America, as represented by The Secretary, Department of Health and Human Services | Rpgr vectors for treating x-linked retinitis pigmentosa |
| KR102704296B1 (ko) * | 2017-11-15 | 2024-09-05 | 더 리젠츠 오브 더 유니버시티 오브 미시간 | Rdh12 암호화 영역을 포함하는 바이러스 벡터 및 망막 이영양증을 치료하는 방법 |
| US20210348193A1 (en) * | 2018-09-21 | 2021-11-11 | Nightstarx Limited | Compositions and methods for treating retinitis pigmentosa |
| CA3131023A1 (en) * | 2019-02-22 | 2020-08-27 | Michael R. Volkert | Oxr1 gene therapy |
| CN115279902A (zh) * | 2019-08-30 | 2022-11-01 | 贝勒医学院 | 用于调控基因表达的系统 |
| WO2021178668A1 (en) * | 2020-03-04 | 2021-09-10 | University Of Massachusetts | Compositions and methods for modulating rpgr expression |
Family Cites Families (13)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| AU722375B2 (en) | 1996-09-06 | 2000-08-03 | Trustees Of The University Of Pennsylvania, The | Methods using cre-lox for production of recombinant adeno-associated viruses |
| ES2751999T3 (es) | 2008-01-29 | 2020-04-02 | Applied Genetic Tech Corporation | Producción recombinante de virus adeno-asociados usando células BHK en suspensión |
| US20100081707A1 (en) * | 2008-02-21 | 2010-04-01 | Ali Robin R | Devices and methods for delivering polynucleotides into retinal cells of the macula and fovea |
| EP2714709B1 (en) * | 2011-05-26 | 2018-04-18 | University of Washington | Compositions for use in cell and gene based methods to improve cardiac function |
| EP2872183B1 (en) * | 2012-07-11 | 2018-09-26 | The Trustees Of The University Of Pennsylvania | Aav-mediated gene therapy for rpgr x-linked retinal degeneration |
| WO2014127196A1 (en) * | 2013-02-15 | 2014-08-21 | The United States Of America, As Represented By The Secretary, Dept. Of Health And Human Services | Aav8 retinoschisin expression vector for treating x-linked retinoschisis |
| EP2970972B1 (en) * | 2013-03-11 | 2018-08-15 | Fondazione Telethon | Mir-204 and mir-211 and uses thereof |
| US9534225B2 (en) * | 2014-04-15 | 2017-01-03 | Applied Genetic Technologies Corporation | Codon optimized nucleic acid encoding a retinitis pigmentosa gtpase regulator (RPGR) |
| LT3137497T (lt) * | 2014-05-02 | 2021-07-26 | Genzyme Corporation | Aav vektoriai, skirti tinklainės ir cns genų terapijai |
| GB201412011D0 (en) | 2014-07-04 | 2014-08-20 | Ucl Business Plc | Treatments |
| HUE068183T2 (hu) * | 2014-07-24 | 2024-12-28 | Massachusetts Eye & Ear Infirmary | RPGR génterápia a retinitis pigmentosa terápiájára |
| SI3265571T1 (sl) * | 2015-03-03 | 2022-10-28 | Fondazione Telethon | Več vektorski sistem in njegove uporabe |
| EP3268481B1 (en) * | 2015-03-11 | 2020-05-27 | The United States of America, as represented by The Secretary, Department of Health and Human Services | Rpgr vectors for treating x-linked retinitis pigmentosa |
-
2016
- 2016-03-11 EP EP16762623.3A patent/EP3268481B1/en active Active
- 2016-03-11 JP JP2017547425A patent/JP6935049B2/ja active Active
- 2016-03-11 EP EP20176667.2A patent/EP3719134B1/en active Active
- 2016-03-11 AU AU2016228751A patent/AU2016228751B2/en active Active
- 2016-03-11 US US15/556,746 patent/US10646588B2/en active Active
- 2016-03-11 WO PCT/US2016/022072 patent/WO2016145345A1/en not_active Ceased
- 2016-03-11 CA CA2979229A patent/CA2979229A1/en active Pending
-
2020
- 2020-04-21 US US16/854,605 patent/US11617801B2/en active Active
- 2020-10-02 JP JP2020167984A patent/JP2021019611A/ja active Pending
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