JP2021500922A5 - - Google Patents
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- Publication number
- JP2021500922A5 JP2021500922A5 JP2020542710A JP2020542710A JP2021500922A5 JP 2021500922 A5 JP2021500922 A5 JP 2021500922A5 JP 2020542710 A JP2020542710 A JP 2020542710A JP 2020542710 A JP2020542710 A JP 2020542710A JP 2021500922 A5 JP2021500922 A5 JP 2021500922A5
- Authority
- JP
- Japan
- Prior art keywords
- promoter
- cfh
- item
- aav vector
- aav
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Withdrawn
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201762574814P | 2017-10-20 | 2017-10-20 | |
| US62/574,814 | 2017-10-20 | ||
| PCT/US2018/056709 WO2019079718A1 (en) | 2017-10-20 | 2018-10-19 | COMPOSITIONS AND METHODS FOR TREATING AGE-RELATED MACULAR DEGENERATION |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2021500922A JP2021500922A (ja) | 2021-01-14 |
| JP2021500922A5 true JP2021500922A5 (https=) | 2021-11-25 |
Family
ID=66174265
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2020542710A Withdrawn JP2021500922A (ja) | 2017-10-20 | 2018-10-19 | 加齢黄斑変性を処置するための組成物および方法 |
Country Status (7)
| Country | Link |
|---|---|
| US (1) | US20210188927A1 (https=) |
| EP (1) | EP3697920A4 (https=) |
| JP (1) | JP2021500922A (https=) |
| CN (1) | CN111788311A (https=) |
| AU (1) | AU2018351491A1 (https=) |
| CA (1) | CA3079553A1 (https=) |
| WO (1) | WO2019079718A1 (https=) |
Families Citing this family (10)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US20210338838A1 (en) * | 2018-07-20 | 2021-11-04 | University Of Utah Research Foundation | Gene therapy for macular degeneration |
| CA3117551A1 (en) * | 2018-10-23 | 2020-04-30 | Gemini Therapeutics Inc. | Compositions and methods for treating age-related macular degeneration and other diseases |
| GB201821089D0 (en) | 2018-12-21 | 2019-02-06 | Gyroscope Therapeutics Ltd | Codon-optimised complement factor I |
| EP4048321A4 (en) * | 2019-10-22 | 2023-11-22 | Applied Genetic Technologies Corporation | ADENO-ASSOCIATED VIRUS (AAV) VECTORS FOR THE TREATMENT OF AGE-RELATED MACULAR DEGENERATION AND OTHER EYE DISEASES AND DISORDERS |
| WO2021081395A1 (en) * | 2019-10-23 | 2021-04-29 | Gemini Therapeutics Inc. | Methods for treating patients having cfh mutations with recombinant cfh proteins |
| GB202003618D0 (en) | 2020-03-12 | 2020-04-29 | Univ Bristol | Gene Therapy |
| CA3182800A1 (en) | 2020-06-14 | 2021-12-23 | Vertex Pharmaceuticals Inc. | Complement factor i-related compositions and methods |
| CR20230202A (es) * | 2020-10-16 | 2023-06-13 | Gyroscope Therapeutics Ltd | Ácido nucleico que codifica una entidad anti-vegf y un regulador del complemento negativo y sus usos para el tratamiento de la degeneración macular relacionada con la edad |
| US20240024416A1 (en) * | 2020-10-30 | 2024-01-25 | Gemini Therapeutics Sub, Inc. | Methods for treating inflammatory ocular diseases with complement factor h |
| CN115786308B (zh) * | 2022-11-24 | 2024-05-31 | 江苏海洋大学 | 一种提高右旋糖酐酶热稳定性的方法及突变体 |
Family Cites Families (4)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| JP2005333845A (ja) * | 2004-05-25 | 2005-12-08 | Tokyoto Igaku Kenkyu Kiko | ミトコンドリア局在型ＤｓＲｅｄ２及びＥＣＦＰ発現ベクター |
| US7745389B2 (en) * | 2005-02-14 | 2010-06-29 | University Of Iowa Research Foundation | Methods for treatment of age-related macular degeneration |
| CN108291216B (zh) * | 2015-09-24 | 2022-09-16 | 宾夕法尼亚州大学信托人 | 用于治疗补体介导的疾病的组合物和方法 |
| GB201519086D0 (en) * | 2015-10-28 | 2015-12-09 | Syncona Partners Llp | Gene Therapy |
-
2018
- 2018-10-19 EP EP18869436.8A patent/EP3697920A4/en not_active Withdrawn
- 2018-10-19 CA CA3079553A patent/CA3079553A1/en not_active Abandoned
- 2018-10-19 CN CN201880078342.1A patent/CN111788311A/zh active Pending
- 2018-10-19 JP JP2020542710A patent/JP2021500922A/ja not_active Withdrawn
- 2018-10-19 WO PCT/US2018/056709 patent/WO2019079718A1/en not_active Ceased
- 2018-10-19 US US16/757,268 patent/US20210188927A1/en not_active Abandoned
- 2018-10-19 AU AU2018351491A patent/AU2018351491A1/en not_active Abandoned
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