JP2021500922A5 - - Google Patents
Download PDFInfo
- Publication number
- JP2021500922A5 JP2021500922A5 JP2020542710A JP2020542710A JP2021500922A5 JP 2021500922 A5 JP2021500922 A5 JP 2021500922A5 JP 2020542710 A JP2020542710 A JP 2020542710A JP 2020542710 A JP2020542710 A JP 2020542710A JP 2021500922 A5 JP2021500922 A5 JP 2021500922A5
- Authority
- JP
- Japan
- Prior art keywords
- promoter
- cfh
- item
- aav vector
- aav
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Withdrawn
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201762574814P | 2017-10-20 | 2017-10-20 | |
| US62/574,814 | 2017-10-20 | ||
| PCT/US2018/056709 WO2019079718A1 (en) | 2017-10-20 | 2018-10-19 | COMPOSITIONS AND METHODS FOR TREATING AGE-RELATED MACULAR DEGENERATION |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2021500922A JP2021500922A (ja) | 2021-01-14 |
| JP2021500922A5 true JP2021500922A5 (https=) | 2021-11-25 |
Family
ID=66174265
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2020542710A Withdrawn JP2021500922A (ja) | 2017-10-20 | 2018-10-19 | 加齢黄斑変性を処置するための組成物および方法 |
Country Status (7)
| Country | Link |
|---|---|
| US (1) | US20210188927A1 (https=) |
| EP (1) | EP3697920A4 (https=) |
| JP (1) | JP2021500922A (https=) |
| CN (1) | CN111788311A (https=) |
| AU (1) | AU2018351491A1 (https=) |
| CA (1) | CA3079553A1 (https=) |
| WO (1) | WO2019079718A1 (https=) |
Families Citing this family (10)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| EP3824095A4 (en) * | 2018-07-20 | 2022-04-20 | University of Utah Research Foundation | GENE THERAPY FOR MACULATE GENERATION |
| CA3117551A1 (en) * | 2018-10-23 | 2020-04-30 | Gemini Therapeutics Inc. | Compositions and methods for treating age-related macular degeneration and other diseases |
| GB201821089D0 (en) | 2018-12-21 | 2019-02-06 | Gyroscope Therapeutics Ltd | Codon-optimised complement factor I |
| CA3158517A1 (en) * | 2019-10-22 | 2021-04-29 | Applied Genetic Technologies Corporation | Adeno-associated virus (aav)vectors for the treatment of age-related macular degeneration and other ocular diseases and disorders |
| EP4048318A4 (en) * | 2019-10-23 | 2023-11-22 | Gemini Therapeutics Sub, Inc. | METHOD FOR TREATING PATIENTS WITH CFH MUTATIONS USING RECOMBINANT CFH PROTEINS |
| GB202003618D0 (en) | 2020-03-12 | 2020-04-29 | Univ Bristol | Gene Therapy |
| AU2021293174A1 (en) | 2020-06-14 | 2023-01-19 | Vertex Pharmaceuticals Incorporated | Complement Factor I-related compositions and methods |
| MX2023004377A (es) * | 2020-10-16 | 2023-06-28 | Gyroscope Therapeutics Ltd | Acido nucleico que codifica una entidad anti-vegf y un regulador del complemento negativo y sus usos para el tratamiento de la degeneracion macular relacionada con la edad. |
| EP4236986A1 (en) * | 2020-10-30 | 2023-09-06 | Gemini Therapeutics Sub, Inc. | Methods for treating inflammatory ocular diseases with complement factor h |
| CN115786308B (zh) * | 2022-11-24 | 2024-05-31 | 江苏海洋大学 | 一种提高右旋糖酐酶热稳定性的方法及突变体 |
Family Cites Families (4)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| JP2005333845A (ja) * | 2004-05-25 | 2005-12-08 | Tokyoto Igaku Kenkyu Kiko | ミトコンドリア局在型ＤｓＲｅｄ２及びＥＣＦＰ発現ベクター |
| EP2357254A1 (en) * | 2005-02-14 | 2011-08-17 | University of Iowa Research Foundation | Methods and reagents for treatment and diagnosis of age-related macular degeneration |
| CN108291216B (zh) * | 2015-09-24 | 2022-09-16 | 宾夕法尼亚州大学信托人 | 用于治疗补体介导的疾病的组合物和方法 |
| GB201519086D0 (en) * | 2015-10-28 | 2015-12-09 | Syncona Partners Llp | Gene Therapy |
-
2018
- 2018-10-19 CN CN201880078342.1A patent/CN111788311A/zh active Pending
- 2018-10-19 JP JP2020542710A patent/JP2021500922A/ja not_active Withdrawn
- 2018-10-19 EP EP18869436.8A patent/EP3697920A4/en not_active Withdrawn
- 2018-10-19 AU AU2018351491A patent/AU2018351491A1/en not_active Abandoned
- 2018-10-19 WO PCT/US2018/056709 patent/WO2019079718A1/en not_active Ceased
- 2018-10-19 CA CA3079553A patent/CA3079553A1/en not_active Abandoned
- 2018-10-19 US US16/757,268 patent/US20210188927A1/en not_active Abandoned
Similar Documents
| Publication | Publication Date | Title |
|---|---|---|
| JP2021500922A5 (https=) | ||
| JP2022141670A5 (https=) | ||
| JP2025179046A5 (https=) | ||
| JP2025039615A (ja) | 変異体キャプシドを有するアデノ関連ウイルスビリオンおよびその使用方法 | |
| JP2022500066A5 (https=) | ||
| JP2021503914A5 (https=) | ||
| IL273261B2 (en) | Adeno-associated virus variant capsids and methods of using them | |
| JP2018508519A5 (https=) | ||
| JP2022091764A (ja) | 血管性浮腫の治療としてのｃ１ｅｉのアデノ随伴ウイルス介在性送達 | |
| RU2018142768A (ru) | Варианты капсидов аденоассоциированного вируса и способы их применения | |
| JP7654562B2 (ja) | 線維芽細胞増殖因子２３関連低リン血症性疾患の遺伝子療法 | |
| JP2023088902A5 (https=) | ||
| KR20190020745A (ko) | Abc4a를 발현시키기 위한 이중 중첩 아데노-관련 바이러스 벡터 시스템 | |
| IL262852B1 (en) | Treatment of complement-mediated disorders | |
| US11744851B2 (en) | Enhancing AAV-mediated transduction of ocular tissues with hyaluronic acid | |
| JP2020512822A5 (https=) | ||
| JPWO2020069461A5 (https=) | ||
| KR20190038583A (ko) | 알데히드 데히드로게나제 결핍의 치료를 위한 유전자 요법 | |
| JP2018509154A5 (https=) | ||
| KR20260005328A (ko) | 항vegf 단백질을 코딩하는 핵산, 폴리뉴클레오타이드 발현 카세트 및 재조합 아데노 관련 바이러스 | |
| CN114126667A (zh) | 使用糖苷水解酶的基因疗法载体向视网膜细胞的改进递送 | |
| CN117947041A (zh) | 编码重组补体因子h多肽的核酸分子及用途 | |
| JP2024528997A (ja) | 放射線誘発性唾液機能低下を予防するためのａｑｐ１遺伝子療法 | |
| EP4301863A1 (en) | Compositions and methods for the treatment of hemophilia | |
| CN117003833A (zh) | 肝脏特异性的腺相关病毒血清型及应用 |