JP2019524090A5 - - Google Patents

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Publication number
JP2019524090A5
JP2019524090A5 JP2019500531A JP2019500531A JP2019524090A5 JP 2019524090 A5 JP2019524090 A5 JP 2019524090A5 JP 2019500531 A JP2019500531 A JP 2019500531A JP 2019500531 A JP2019500531 A JP 2019500531A JP 2019524090 A5 JP2019524090 A5 JP 2019524090A5
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JP
Japan
Prior art keywords
rdh12
composition
functional
nucleic acid
acid sequence
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JP2019500531A
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English (en)
Japanese (ja)
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JP7101656B2 (ja
JP2019524090A (ja
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Priority claimed from PCT/US2017/041122 external-priority patent/WO2018009814A1/en
Publication of JP2019524090A publication Critical patent/JP2019524090A/ja
Publication of JP2019524090A5 publication Critical patent/JP2019524090A5/ja
Priority to JP2022076693A priority Critical patent/JP7572990B2/ja
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JP2019500531A 2016-07-08 2017-07-07 Rdh12が関与する疾患及び疾病を治療する方法及び組成物 Active JP7101656B2 (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2022076693A JP7572990B2 (ja) 2016-07-08 2022-05-06 Rdh12が関与する疾患及び疾病を治療する方法及び組成物

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201662359777P 2016-07-08 2016-07-08
US62/359,777 2016-07-08
PCT/US2017/041122 WO2018009814A1 (en) 2016-07-08 2017-07-07 Methods and compositions for treatment of disorders and diseases involving rdh12

Related Child Applications (1)

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JP2022076693A Division JP7572990B2 (ja) 2016-07-08 2022-05-06 Rdh12が関与する疾患及び疾病を治療する方法及び組成物

Publications (3)

Publication Number Publication Date
JP2019524090A JP2019524090A (ja) 2019-09-05
JP2019524090A5 true JP2019524090A5 (https=) 2020-07-16
JP7101656B2 JP7101656B2 (ja) 2022-07-15

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JP2019500531A Active JP7101656B2 (ja) 2016-07-08 2017-07-07 Rdh12が関与する疾患及び疾病を治療する方法及び組成物
JP2022076693A Active JP7572990B2 (ja) 2016-07-08 2022-05-06 Rdh12が関与する疾患及び疾病を治療する方法及び組成物

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JP2022076693A Active JP7572990B2 (ja) 2016-07-08 2022-05-06 Rdh12が関与する疾患及び疾病を治療する方法及び組成物

Country Status (11)

Country Link
US (4) US11197936B2 (https=)
EP (1) EP3481958B1 (https=)
JP (2) JP7101656B2 (https=)
KR (2) KR102799528B1 (https=)
CN (1) CN110191954B (https=)
AU (2) AU2017292010B2 (https=)
BR (1) BR112019000171A2 (https=)
CA (1) CA3029646A1 (https=)
IL (3) IL297095B2 (https=)
RU (1) RU2764920C2 (https=)
WO (1) WO2018009814A1 (https=)

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CN108291216B (zh) * 2015-09-24 2022-09-16 宾夕法尼亚州大学信托人 用于治疗补体介导的疾病的组合物和方法
WO2018009814A1 (en) 2016-07-08 2018-01-11 The Trustees Of The University Of Pennsylvania Methods and compositions for treatment of disorders and diseases involving rdh12
EP3619019A4 (en) 2017-05-04 2021-01-20 Lehigh University SYSTEM FOR GENERATIVE MANUFACTURING WITH ADJUSTABLE MATERIAL PROPERTIES
KR102704296B1 (ko) * 2017-11-15 2024-09-05 더 리젠츠 오브 더 유니버시티 오브 미시간 Rdh12 암호화 영역을 포함하는 바이러스 벡터 및 망막 이영양증을 치료하는 방법
WO2022165313A1 (en) 2021-02-01 2022-08-04 Regenxbio Inc. Gene therapy for neuronal ceroid lipofuscinoses
TR2021022284A2 (tr) * 2021-12-31 2022-01-21 T C Ueskuedar Ueniversitesi Retinitis pigmentosa (rp) hastalığının tedavisinde kullanılmak üzere retinol dehidrojenaz 12 (rdh12) gen mutasyonlarına yönelik crıspr-pe sistemi.
CN115725659A (zh) * 2022-04-01 2023-03-03 首都医科大学附属北京同仁医院 一种应用视网膜原位基因编辑制作非人灵长类动物先天性黑矇模型的方法
JP7168814B1 (ja) 2022-07-01 2022-11-09 東洋インキScホールディングス株式会社 積層体の分離回収方法
CN118453915A (zh) * 2024-04-29 2024-08-09 中国医学科学院北京协和医院 一种针对rdh12突变的基因治疗药物

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TR2021022284A2 (tr) 2021-12-31 2022-01-21 T C Ueskuedar Ueniversitesi Retinitis pigmentosa (rp) hastalığının tedavisinde kullanılmak üzere retinol dehidrojenaz 12 (rdh12) gen mutasyonlarına yönelik crıspr-pe sistemi.

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