JP2021510301A5 - - Google Patents
Info
- Publication number
- JP2021510301A5 JP2021510301A5 JP2020538584A JP2020538584A JP2021510301A5 JP 2021510301 A5 JP2021510301 A5 JP 2021510301A5 JP 2020538584 A JP2020538584 A JP 2020538584A JP 2020538584 A JP2020538584 A JP 2020538584A JP 2021510301 A5 JP2021510301 A5 JP 2021510301A5
- Authority
- JP
- Japan
- Prior art keywords
- sequence
- tcu
- vector
- nucleotides
- aav
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Granted
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| GB1800546.2 | 2018-01-12 | ||
| GBGB1800546.2A GB201800546D0 (en) | 2018-01-12 | 2018-01-12 | Treatment |
| PCT/GB2019/050092 WO2019138250A1 (en) | 2018-01-12 | 2019-01-14 | Compositions and methods for treating retinal disorders |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2021510301A JP2021510301A (ja) | 2021-04-22 |
| JP2021510301A5 true JP2021510301A5 (https=) | 2022-01-21 |
| JP7289306B2 JP7289306B2 (ja) | 2023-06-09 |
Family
ID=61256183
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2020538584A Active JP7289306B2 (ja) | 2018-01-12 | 2019-01-14 | 網膜障害を治療するための組成物及び方法 |
Country Status (26)
| Country | Link |
|---|---|
| US (2) | US11680276B2 (https=) |
| EP (1) | EP3737423B1 (https=) |
| JP (1) | JP7289306B2 (https=) |
| KR (1) | KR102786552B1 (https=) |
| CN (1) | CN111936172A (https=) |
| AU (1) | AU2019206314B2 (https=) |
| BR (1) | BR112020014191A2 (https=) |
| CA (1) | CA3088079A1 (https=) |
| DK (1) | DK3737423T3 (https=) |
| EA (1) | EA202091655A1 (https=) |
| ES (1) | ES2988499T3 (https=) |
| FI (1) | FI3737423T3 (https=) |
| GB (1) | GB201800546D0 (https=) |
| HR (1) | HRP20241483T1 (https=) |
| HU (1) | HUE068987T2 (https=) |
| IL (1) | IL275985A (https=) |
| LT (1) | LT3737423T (https=) |
| MX (1) | MX2020007366A (https=) |
| PH (1) | PH12020551071A1 (https=) |
| PL (1) | PL3737423T3 (https=) |
| PT (1) | PT3737423T (https=) |
| RS (1) | RS66227B1 (https=) |
| SG (1) | SG11202006618PA (https=) |
| SI (1) | SI3737423T1 (https=) |
| SM (1) | SMT202400410T1 (https=) |
| WO (1) | WO2019138250A1 (https=) |
Families Citing this family (6)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US11241460B2 (en) | 2013-03-15 | 2022-02-08 | Astellas Institute For Regenerative Medicine | Photoreceptors and photoreceptor progenitors produced from pluripotent stem cells |
| EP4292600A3 (en) | 2013-03-15 | 2024-04-10 | Astellas Institute for Regenerative Medicine | Photoreceptors and photoreceptor progenitors produced from pluripotent stem cells |
| GB2584664B (en) * | 2019-06-10 | 2023-05-24 | Newcells Biotech Ltd | Improved retinal organoids and methods of making the same |
| CN113025616B (zh) * | 2021-04-21 | 2023-05-02 | 中国热带农业科学院橡胶研究所 | 一种橡胶树泛素基因启动子proHbUBI2及其克隆与应用 |
| AU2022275948A1 (en) * | 2021-05-20 | 2023-12-21 | Artema Therapeutics, Inc. | Kcnv2 variants and their use |
| WO2023039175A2 (en) * | 2021-09-09 | 2023-03-16 | Applied Genetic Technologies Corporation | Predictors of achromatopsia treatment efficacy |
Family Cites Families (6)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| WO2008073303A2 (en) * | 2006-12-07 | 2008-06-19 | Switchgear Genomics | Transcriptional regulatory elements of biological pathways, tools, and methods |
| US20120172419A1 (en) | 2009-09-15 | 2012-07-05 | Medical College Of Wisconsin Research Foundation Inc. | Reagents and methods for modulating cone photoreceptor activity |
| CN103608455B (zh) * | 2011-01-07 | 2019-01-15 | 应用遗传科技公司 | 用于治疗色盲和其它疾病的启动子、表达盒、载体、药盒和方法 |
| EP3800191B1 (en) * | 2014-03-17 | 2025-08-20 | Adverum Biotechnologies, Inc. | Compositions and methods for enhanced gene expression in cone cells |
| US11021519B2 (en) * | 2015-03-02 | 2021-06-01 | Adverum Biotechnologies, Inc. | Compositions and methods for intravitreal delivery of polynucleotides to retinal cones |
| WO2017144080A1 (en) * | 2016-02-23 | 2017-08-31 | Eyeserv Gmbh | Gene therapy for the treatment of a disease of retinal cone cells |
-
2018
- 2018-01-12 GB GBGB1800546.2A patent/GB201800546D0/en not_active Ceased
-
2019
- 2019-01-14 CA CA3088079A patent/CA3088079A1/en active Pending
- 2019-01-14 EP EP19701018.4A patent/EP3737423B1/en active Active
- 2019-01-14 HR HRP20241483TT patent/HRP20241483T1/hr unknown
- 2019-01-14 PL PL19701018.4T patent/PL3737423T3/pl unknown
- 2019-01-14 EA EA202091655A patent/EA202091655A1/ru unknown
- 2019-01-14 HU HUE19701018A patent/HUE068987T2/hu unknown
- 2019-01-14 CN CN201980018443.4A patent/CN111936172A/zh active Pending
- 2019-01-14 JP JP2020538584A patent/JP7289306B2/ja active Active
- 2019-01-14 KR KR1020207023349A patent/KR102786552B1/ko active Active
- 2019-01-14 PT PT197010184T patent/PT3737423T/pt unknown
- 2019-01-14 RS RS20241186A patent/RS66227B1/sr unknown
- 2019-01-14 SI SI201930833T patent/SI3737423T1/sl unknown
- 2019-01-14 BR BR112020014191A patent/BR112020014191A2/pt unknown
- 2019-01-14 ES ES19701018T patent/ES2988499T3/es active Active
- 2019-01-14 SM SM20240410T patent/SMT202400410T1/it unknown
- 2019-01-14 US US16/961,857 patent/US11680276B2/en active Active
- 2019-01-14 SG SG11202006618PA patent/SG11202006618PA/en unknown
- 2019-01-14 MX MX2020007366A patent/MX2020007366A/es unknown
- 2019-01-14 DK DK19701018.4T patent/DK3737423T3/da active
- 2019-01-14 LT LTEPPCT/GB2019/050092T patent/LT3737423T/lt unknown
- 2019-01-14 WO PCT/GB2019/050092 patent/WO2019138250A1/en not_active Ceased
- 2019-01-14 FI FIEP19701018.4T patent/FI3737423T3/fi active
- 2019-01-14 AU AU2019206314A patent/AU2019206314B2/en active Active
-
2020
- 2020-07-10 PH PH12020551071A patent/PH12020551071A1/en unknown
- 2020-07-12 IL IL275985A patent/IL275985A/en unknown
-
2023
- 2023-06-16 US US18/336,409 patent/US12467066B2/en active Active
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