JP2021533801A5 - - Google Patents
Info
- Publication number
- JP2021533801A5 JP2021533801A5 JP2021509904A JP2021509904A JP2021533801A5 JP 2021533801 A5 JP2021533801 A5 JP 2021533801A5 JP 2021509904 A JP2021509904 A JP 2021509904A JP 2021509904 A JP2021509904 A JP 2021509904A JP 2021533801 A5 JP2021533801 A5 JP 2021533801A5
- Authority
- JP
- Japan
- Prior art keywords
- sequence
- nucleic acid
- recombinant nucleic
- vector
- nucleotide sequence
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Granted
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| CN201810968173.0A CN110857440B (zh) | 2018-08-23 | 2018-08-23 | 重组人ⅱ型线粒体动力蛋白样gtp酶基因序列及其应用 |
| CN201810968173.0 | 2018-08-23 | ||
| PCT/CN2019/102352 WO2020038473A1 (zh) | 2018-08-23 | 2019-08-23 | 重组人ⅱ型线粒体动力蛋白样gtp酶基因序列及其应用 |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2021533801A JP2021533801A (ja) | 2021-12-09 |
| JP2021533801A5 true JP2021533801A5 (https=) | 2022-08-31 |
| JP7285022B2 JP7285022B2 (ja) | 2023-06-01 |
Family
ID=69592310
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2021509904A Active JP7285022B2 (ja) | 2018-08-23 | 2019-08-23 | 組換えヒトＩＩ型ミトコンドリアダイニン様ＧＴＰａｓｅの遺伝子配列及びその使用 |
Country Status (11)
| Country | Link |
|---|---|
| US (1) | US11459584B2 (https=) |
| EP (1) | EP3851535A4 (https=) |
| JP (1) | JP7285022B2 (https=) |
| KR (1) | KR102612148B1 (https=) |
| CN (1) | CN110857440B (https=) |
| AU (1) | AU2019323501B2 (https=) |
| BR (1) | BR112021002566A2 (https=) |
| CA (1) | CA3110153A1 (https=) |
| MX (1) | MX2021002135A (https=) |
| SG (1) | SG11202101236WA (https=) |
| WO (1) | WO2020038473A1 (https=) |
Families Citing this family (5)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| CN110857440B (zh) | 2018-08-23 | 2021-02-19 | 武汉纽福斯生物科技有限公司 | 重组人ⅱ型线粒体动力蛋白样gtp酶基因序列及其应用 |
| CN111849998A (zh) * | 2020-07-29 | 2020-10-30 | 武汉纽福斯生物科技有限公司 | 编码人卵黄状黄斑病蛋白1的核酸分子及其应用 |
| CN117904156A (zh) * | 2022-10-17 | 2024-04-19 | 武汉纽福斯生物科技有限公司 | 人线粒体动力蛋白样gtp酶及应用 |
| WO2024226729A2 (en) * | 2023-04-26 | 2024-10-31 | Astellas Gene Therapies, Inc. | Compositions and methods for opa1 gene therapy |
| CN117304293B (zh) * | 2023-10-07 | 2025-08-08 | 浙江大学 | 一种鸡opa1抗原决定簇及其应用 |
Family Cites Families (21)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US4797368A (en) | 1985-03-15 | 1989-01-10 | The United States Of America As Represented By The Department Of Health And Human Services | Adeno-associated virus as eukaryotic expression vector |
| US5139941A (en) | 1985-10-31 | 1992-08-18 | University Of Florida Research Foundation, Inc. | AAV transduction vectors |
| WO1991018088A1 (en) | 1990-05-23 | 1991-11-28 | The United States Of America, Represented By The Secretary, United States Department Of Commerce | Adeno-associated virus (aav)-based eucaryotic vectors |
| US5173414A (en) | 1990-10-30 | 1992-12-22 | Applied Immune Sciences, Inc. | Production of recombinant adeno-associated virus vectors |
| US5252479A (en) | 1991-11-08 | 1993-10-12 | Research Corporation Technologies, Inc. | Safe vector for gene therapy |
| US6989264B2 (en) | 1997-09-05 | 2006-01-24 | Targeted Genetics Corporation | Methods for generating high titer helper-free preparations of released recombinant AAV vectors |
| US6566118B1 (en) | 1997-09-05 | 2003-05-20 | Targeted Genetics Corporation | Methods for generating high titer helper-free preparations of released recombinant AAV vectors |
| CA2379166C (en) | 1999-08-09 | 2013-03-26 | Targeted Genetics Corporation | Enhancement of expression of a single-stranded, heterologous nucleotide sequence from recombinant viral vectors by designing the sequence such that it forms instrastrand base pairs |
| EP1771571A2 (en) | 2004-07-30 | 2007-04-11 | Targeted Genetics Corporation | Recombinant aav based vaccine methods |
| PT1880008E (pt) * | 2005-05-03 | 2015-08-27 | Inserm Inst Nat De La Santé Et De La Rech Médicale | Expressão de proteína mitocondrial através de uma abordagem alotópica melhorada |
| WO2007134818A2 (en) * | 2006-05-18 | 2007-11-29 | Univ Muenchen L Maximilians | Method for diagnosing mitochondrial dysfunction |
| CN102634527B (zh) * | 2012-04-11 | 2013-11-06 | 华中科技大学同济医学院附属同济医院 | 重组人nadh脱氢酶亚单位4基因及其表达载体构建方法 |
| AU2013293270B2 (en) * | 2012-07-25 | 2018-08-16 | Massachusetts Institute Of Technology | Inducible DNA binding proteins and genome perturbation tools and applications thereof |
| AR095983A1 (es) * | 2013-04-03 | 2015-11-25 | Aliophtha Ag | Factores artificiales de transcripción para el tratamiento de enfermedades causadas por haploinsuficiencia de opa1 |
| CN104450747B (zh) * | 2014-09-23 | 2018-02-09 | 武汉纽福斯生物科技有限公司 | 用于治疗Leber遗传性视神经病变的重组腺相关病毒‑NADH脱氢酶亚单位4基因全长以及药剂 |
| EP3289080B1 (en) * | 2015-04-30 | 2021-08-25 | The Trustees of Columbia University in the City of New York | Gene therapy for autosomal dominant diseases |
| WO2017191274A2 (en) | 2016-05-04 | 2017-11-09 | Curevac Ag | Rna encoding a therapeutic protein |
| EP3548039B1 (en) * | 2016-12-04 | 2023-07-19 | Alavi Khorassani Moghadam, Marcel Victor | Ribavirin for use in the treatment of a mitochondrial disease |
| WO2018146588A1 (en) | 2017-02-08 | 2018-08-16 | Friedrich Miescher Institute For Biomedical Research | Synp88, a promoter for the specific expression of genes in retinal ganglion cells |
| CN111068071A (zh) * | 2018-10-22 | 2020-04-28 | 武汉纽福斯生物科技有限公司 | 基因治疗Leber遗传学视神经病变 |
| CN110857440B (zh) | 2018-08-23 | 2021-02-19 | 武汉纽福斯生物科技有限公司 | 重组人ⅱ型线粒体动力蛋白样gtp酶基因序列及其应用 |
-
2018
- 2018-08-23 CN CN201810968173.0A patent/CN110857440B/zh active Active
-
2019
- 2019-08-23 MX MX2021002135A patent/MX2021002135A/es unknown
- 2019-08-23 AU AU2019323501A patent/AU2019323501B2/en active Active
- 2019-08-23 BR BR112021002566-9A patent/BR112021002566A2/pt not_active IP Right Cessation
- 2019-08-23 EP EP19851390.5A patent/EP3851535A4/en not_active Withdrawn
- 2019-08-23 WO PCT/CN2019/102352 patent/WO2020038473A1/zh not_active Ceased
- 2019-08-23 JP JP2021509904A patent/JP7285022B2/ja active Active
- 2019-08-23 CA CA3110153A patent/CA3110153A1/en active Pending
- 2019-08-23 SG SG11202101236WA patent/SG11202101236WA/en unknown
- 2019-08-23 KR KR1020217008407A patent/KR102612148B1/ko active Active
-
2021
- 2021-02-23 US US17/182,903 patent/US11459584B2/en active Active
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