JP2024527742A5 - - Google Patents
Info
- Publication number
- JP2024527742A5 JP2024527742A5 JP2024501135A JP2024501135A JP2024527742A5 JP 2024527742 A5 JP2024527742 A5 JP 2024527742A5 JP 2024501135 A JP2024501135 A JP 2024501135A JP 2024501135 A JP2024501135 A JP 2024501135A JP 2024527742 A5 JP2024527742 A5 JP 2024527742A5
- Authority
- JP
- Japan
- Prior art keywords
- intrathecal
- approximately
- meters
- composition according
- composition
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (5)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202163229936P | 2021-08-05 | 2021-08-05 | |
| US63/229,936 | 2021-08-05 | ||
| US202163239881P | 2021-09-01 | 2021-09-01 | |
| US63/239,881 | 2021-09-01 | ||
| PCT/US2022/074622 WO2023015304A1 (en) | 2021-08-05 | 2022-08-05 | Adeno-associated virus particles and methods of use thereof |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2024527742A JP2024527742A (ja) | 2024-07-26 |
| JP2024527742A5 true JP2024527742A5 (https=) | 2025-08-14 |
Family
ID=85156338
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024501135A Pending JP2024527742A (ja) | 2021-08-05 | 2022-08-05 | アデノ随伴ウイルス粒子及びその使用方法 |
Country Status (8)
| Country | Link |
|---|---|
| US (1) | US20250041450A1 (https=) |
| EP (1) | EP4380626A4 (https=) |
| JP (1) | JP2024527742A (https=) |
| KR (1) | KR20240045203A (https=) |
| AU (1) | AU2022325165A1 (https=) |
| CA (1) | CA3224482A1 (https=) |
| MX (1) | MX2024001634A (https=) |
| WO (1) | WO2023015304A1 (https=) |
Families Citing this family (2)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| WO2025250909A1 (en) | 2024-05-31 | 2025-12-04 | Sarepta Therapeutics, Inc. | Muscle-tropic recombinant aav |
| CN119144658A (zh) * | 2024-09-13 | 2024-12-17 | 南京鼓楼医院 | 一种调控平滑肌收缩的aav载体及其构建方法和应用 |
Family Cites Families (10)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US9624282B2 (en) * | 2012-11-26 | 2017-04-18 | The Curators Of The University Of Missouri | Microdystrophin peptides and methods for treating muscular dystrophy using the same |
| PL3097197T3 (pl) * | 2014-01-21 | 2021-06-28 | Vrije Universiteit Brussel | Mięśniowo-specyficzne elementy regulatorowe kwasów nukleinowych oraz sposoby i ich zastosowanie |
| CA2971303C (en) * | 2016-06-21 | 2026-03-03 | Bamboo Therapeutics, Inc. | Optimized mini-dystrophin genes and expression cassettes and their use |
| JP7676111B2 (ja) * | 2017-03-17 | 2025-05-14 | リサーチ インスティチュート アット ネイションワイド チルドレンズ ホスピタル | 筋ジストロフィーを治療するための筋肉特異的マイクロジストロフィンのアデノ随伴ウイルスベクター送達 |
| AU2018269050A1 (en) * | 2017-05-19 | 2020-01-16 | Encoded Therapeutics, Inc. | High activity regulatory elements |
| US20200405824A1 (en) * | 2019-06-26 | 2020-12-31 | University Of Washington | Use of ribonucleotide reductase alone or in combination with micro-dystrophin to treat duchenne muscular dystrophy striated muscle disease |
| EP3990030A1 (en) * | 2019-06-27 | 2022-05-04 | Pfizer Inc. | Methods of treating duchenne muscular dystrophy using aav mini-dystrophin gene therapy |
| AU2020368539A1 (en) * | 2019-10-16 | 2022-04-28 | Massachusetts Institute Of Technology | Engineered muscle targeting compositions |
| WO2022029543A1 (en) * | 2020-08-06 | 2022-02-10 | Intas Pharmaceuticals Ltd. | Adeno-associated virus vector delivery of micro-dystrophin to treat muscular dystrophy |
| JP7642809B2 (ja) * | 2020-11-12 | 2025-03-10 | プレシジョン バイオサイエンシズ，インク． | ジストロフィン遺伝子内の認識配列に特異性を有する遺伝子操作されたメガヌクレアーゼ |
-
2022
- 2022-08-05 US US18/294,792 patent/US20250041450A1/en active Pending
- 2022-08-05 MX MX2024001634A patent/MX2024001634A/es unknown
- 2022-08-05 AU AU2022325165A patent/AU2022325165A1/en active Pending
- 2022-08-05 CA CA3224482A patent/CA3224482A1/en active Pending
- 2022-08-05 EP EP22854128.0A patent/EP4380626A4/en active Pending
- 2022-08-05 WO PCT/US2022/074622 patent/WO2023015304A1/en not_active Ceased
- 2022-08-05 JP JP2024501135A patent/JP2024527742A/ja active Pending
- 2022-08-05 KR KR1020247002648A patent/KR20240045203A/ko active Pending
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