JP2025509828A5 - - Google Patents
Info
- Publication number
- JP2025509828A5 JP2025509828A5 JP2024555341A JP2024555341A JP2025509828A5 JP 2025509828 A5 JP2025509828 A5 JP 2025509828A5 JP 2024555341 A JP2024555341 A JP 2024555341A JP 2024555341 A JP2024555341 A JP 2024555341A JP 2025509828 A5 JP2025509828 A5 JP 2025509828A5
- Authority
- JP
- Japan
- Prior art keywords
- nucleic acid
- sequence
- promoter
- expression
- raav
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202263321264P | 2022-03-18 | 2022-03-18 | |
| US63/321,264 | 2022-03-18 | ||
| PCT/US2023/064673 WO2023178339A2 (en) | 2022-03-18 | 2023-03-18 | Methods and compositions for treating tnnt2 related cardiomyopathy with a viral vector |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2025509828A JP2025509828A (ja) | 2025-04-11 |
| JP2025509828A5 true JP2025509828A5 (https=) | 2026-03-27 |
Family
ID=88024553
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024555341A Pending JP2025509828A (ja) | 2022-03-18 | 2023-03-18 | ウイルスベクターによるｔｎｎｔ２関連心筋症を処置するための方法および組成物 |
Country Status (8)
| Country | Link |
|---|---|
| US (1) | US20250195694A1 (https=) |
| EP (1) | EP4493702A4 (https=) |
| JP (1) | JP2025509828A (https=) |
| KR (1) | KR20250007509A (https=) |
| AU (1) | AU2023234604A1 (https=) |
| CA (1) | CA3254775A1 (https=) |
| IL (1) | IL315697A (https=) |
| WO (1) | WO2023178339A2 (https=) |
Families Citing this family (3)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| WO2025214477A1 (en) * | 2024-04-12 | 2025-10-16 | Skyline Therapeutics (Shanghai) Co., Ltd. | Treatment of genetic cardiomyopathies with aav gene therapy vectors |
| WO2025226841A1 (en) * | 2024-04-24 | 2025-10-30 | Kate Therapeutics, Inc. | Gene therapy approach for treating disorders associated with tnnt2 |
| WO2025235807A1 (en) * | 2024-05-10 | 2025-11-13 | Solid Biosciences, Inc. | Compositions and methods to improve graft survival |
Family Cites Families (10)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| JP5553547B2 (ja) * | 2009-07-14 | 2014-07-16 | 俊一 梶岡 | トロポニン含有医薬組成物 |
| US9783805B2 (en) * | 2013-02-28 | 2017-10-10 | City Of Hope | Replication capable rAAV vectors encoding inhibitory siRNA and methods of their use |
| EP2792742A1 (en) * | 2013-04-17 | 2014-10-22 | Universitätsklinikum Hamburg-Eppendorf (UKE) | Gene-therapy vectors for treating cardiomyopathy |
| US20210363193A1 (en) * | 2018-04-27 | 2021-11-25 | Universität Heidelberg | Modified aav capsid polypeptides for treatment of muscular diseases |
| WO2020198337A1 (en) * | 2019-03-25 | 2020-10-01 | Ohio State Innovation Foundation | Engineered mrna sequences and uses thereof |
| EP3947700A4 (en) * | 2019-04-01 | 2023-01-04 | Tenaya Therapeutics, Inc. | Adeno-associated virus with engineered capsid |
| EP3997227A1 (en) * | 2019-07-10 | 2022-05-18 | Locanabio, Inc. | Rna-targeting knockdown and replacement compositions and methods for use |
| WO2021154923A2 (en) * | 2020-01-29 | 2021-08-05 | Voyager Therapeutics, Inc. | Methods and systems for producing aav particles |
| WO2021163357A2 (en) * | 2020-02-13 | 2021-08-19 | Tenaya Therapeutics, Inc. | Gene therapy vectors for treating heart disease |
| CA3242351A1 (en) * | 2021-12-10 | 2023-06-15 | University Of Florida Research Foundation, Incorporated | Methods and compositions for treating bag-3 related cardiomyopathy with a viral vector |
-
2023
- 2023-03-18 EP EP23771729.3A patent/EP4493702A4/en active Pending
- 2023-03-18 US US18/847,734 patent/US20250195694A1/en active Pending
- 2023-03-18 CA CA3254775A patent/CA3254775A1/en active Pending
- 2023-03-18 AU AU2023234604A patent/AU2023234604A1/en active Pending
- 2023-03-18 JP JP2024555341A patent/JP2025509828A/ja active Pending
- 2023-03-18 WO PCT/US2023/064673 patent/WO2023178339A2/en not_active Ceased
- 2023-03-18 KR KR1020247034272A patent/KR20250007509A/ko active Pending
- 2023-03-18 IL IL315697A patent/IL315697A/en unknown