JP2022530264A5 - - Google Patents
Info
- Publication number
- JP2022530264A5 JP2022530264A5 JP2021564486A JP2021564486A JP2022530264A5 JP 2022530264 A5 JP2022530264 A5 JP 2022530264A5 JP 2021564486 A JP2021564486 A JP 2021564486A JP 2021564486 A JP2021564486 A JP 2021564486A JP 2022530264 A5 JP2022530264 A5 JP 2022530264A5
- Authority
- JP
- Japan
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201962840360P | 2019-04-29 | 2019-04-29 | |
| US62/840,360 | 2019-04-29 | ||
| PCT/US2020/030427 WO2020223322A1 (en) | 2019-04-29 | 2020-04-29 | Intrathecal and intravenous combination gene therapy for the treatment of infantile batten disease |
Publications (4)
| Publication Number | Publication Date |
|---|---|
| JP2022530264A JP2022530264A (ja) | 2022-06-28 |
| JP2022530264A5 true JP2022530264A5 (https=) | 2023-05-12 |
| JPWO2020223322A5 JPWO2020223322A5 (https=) | 2023-05-12 |
| JP7788594B2 JP7788594B2 (ja) | 2025-12-19 |
Family
ID=73029200
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2021564486A Active JP7788594B2 (ja) | 2019-04-29 | 2020-04-29 | 乳児バッテン病の治療のための髄腔内および静脈内組合せ遺伝子療法 |
Country Status (12)
| Country | Link |
|---|---|
| US (1) | US20220193268A1 (https=) |
| EP (1) | EP3963081A4 (https=) |
| JP (1) | JP7788594B2 (https=) |
| KR (1) | KR20220046513A (https=) |
| CN (1) | CN114269935A (https=) |
| AU (1) | AU2020264438A1 (https=) |
| BR (1) | BR112021021632A8 (https=) |
| CA (1) | CA3138274A1 (https=) |
| IL (1) | IL287608A (https=) |
| MX (1) | MX2021013275A (https=) |
| SG (1) | SG11202111908XA (https=) |
| WO (1) | WO2020223322A1 (https=) |
Families Citing this family (1)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| AU2023303015A1 (en) * | 2022-07-06 | 2025-01-23 | Research Institute At Nationwide Children's Hospital | Adeno-associated virus delivery of cln1 polynucleotide |
Family Cites Families (5)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| CA2794196A1 (en) * | 2010-03-23 | 2011-09-29 | Intrexon Corporation | Vectors conditionally expressing therapeutic proteins, host cells comprising the vectors, and uses thereof |
| CN107249646B (zh) * | 2014-12-16 | 2021-06-29 | 内布拉斯加大学董事会 | 用于青少年巴滕病的基因疗法 |
| RU2764919C2 (ru) * | 2016-06-13 | 2022-01-24 | Дзе Юниверсити Оф Норт Каролина Эт Чепел Хилл | Оптимизированные гены и экспрессионные кассеты cln1, и их применение |
| US20200370069A1 (en) * | 2017-07-08 | 2020-11-26 | Genethon | Treatment of spinal muscular atrophy |
| WO2019046815A1 (en) * | 2017-08-31 | 2019-03-07 | Poseida Therapeutics, Inc. | TRANSPOSON SYSTEM AND METHODS OF USE |
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2020
- 2020-04-29 EP EP20798198.6A patent/EP3963081A4/en active Pending
- 2020-04-29 SG SG11202111908XA patent/SG11202111908XA/en unknown
- 2020-04-29 BR BR112021021632A patent/BR112021021632A8/pt not_active Application Discontinuation
- 2020-04-29 US US17/607,315 patent/US20220193268A1/en active Pending
- 2020-04-29 WO PCT/US2020/030427 patent/WO2020223322A1/en not_active Ceased
- 2020-04-29 KR KR1020217038864A patent/KR20220046513A/ko not_active Withdrawn
- 2020-04-29 AU AU2020264438A patent/AU2020264438A1/en active Pending
- 2020-04-29 JP JP2021564486A patent/JP7788594B2/ja active Active
- 2020-04-29 CA CA3138274A patent/CA3138274A1/en not_active Abandoned
- 2020-04-29 CN CN202080047719.4A patent/CN114269935A/zh active Pending
- 2020-04-29 MX MX2021013275A patent/MX2021013275A/es unknown
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2021
- 2021-10-27 IL IL287608A patent/IL287608A/en unknown