JP2024545507A5 - - Google Patents

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Publication number
JP2024545507A5
JP2024545507A5 JP2024534532A JP2024534532A JP2024545507A5 JP 2024545507 A5 JP2024545507 A5 JP 2024545507A5 JP 2024534532 A JP2024534532 A JP 2024534532A JP 2024534532 A JP2024534532 A JP 2024534532A JP 2024545507 A5 JP2024545507 A5 JP 2024545507A5
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JP
Japan
Application number
JP2024534532A
Other languages
Japanese (ja)
Other versions
JPWO2023108129A5 (https=
JP2024545507A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/081282 external-priority patent/WO2023108129A1/en
Publication of JP2024545507A publication Critical patent/JP2024545507A/ja
Publication of JP2024545507A5 publication Critical patent/JP2024545507A5/ja
Publication of JPWO2023108129A5 publication Critical patent/JPWO2023108129A5/ja
Pending legal-status Critical Current

Links

JP2024534532A 2021-12-10 2022-12-09 Aavベクターを用いたトロポニンc(tnnc1)遺伝子治療 Pending JP2024545507A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202163288255P 2021-12-10 2021-12-10
US63/288,255 2021-12-10
PCT/US2022/081282 WO2023108129A1 (en) 2021-12-10 2022-12-09 Troponin c (tnnc1) gene therapy using aav vector

Publications (3)

Publication Number Publication Date
JP2024545507A JP2024545507A (ja) 2024-12-09
JP2024545507A5 true JP2024545507A5 (https=) 2025-10-29
JPWO2023108129A5 JPWO2023108129A5 (https=) 2025-10-29

Family

ID=86731323

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024534532A Pending JP2024545507A (ja) 2021-12-10 2022-12-09 Aavベクターを用いたトロポニンc(tnnc1)遺伝子治療

Country Status (6)

Country Link
US (1) US20240335566A1 (https=)
EP (1) EP4444893A4 (https=)
JP (1) JP2024545507A (https=)
CN (1) CN118613591A (https=)
CA (1) CA3240616A1 (https=)
WO (1) WO2023108129A1 (https=)

Families Citing this family (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CA3021572A1 (en) 2016-04-20 2017-10-26 Centro De Investigaciones Energeticas, Medioambientales Y Tecnologicas Compositions and methods for enhanced gene expression of pklr
EP3697452A4 (en) 2017-10-16 2021-11-24 Centro de Investigaciones Energéticas, Medioambientales y Tecnológicas, O.A., M.P. LENTIVIRAL VECTORS FOR ADMINISTRATION OF PKLR TO TREAT PYRUVATE KINASE DEFECTS
BR112020020841A2 (pt) 2018-04-11 2021-01-19 Fundacion Para La Investigacion Biomedica Del Hospital Infantil Universitario Nino Jesus Composições e métodos para transplante de célulastronco

Family Cites Families (6)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
JP5553547B2 (ja) * 2009-07-14 2014-07-16 俊一 梶岡 トロポニン含有医薬組成物
AU2012258525B2 (en) * 2011-05-26 2017-02-23 University Of Washington Cell and gene based methods to improve cardiac function
EP2792742A1 (en) * 2013-04-17 2014-10-22 Universitätsklinikum Hamburg-Eppendorf (UKE) Gene-therapy vectors for treating cardiomyopathy
CA3057899A1 (en) * 2017-03-27 2018-10-04 Vrije Universiteit Brussel Diaphragm-specific nucleic acid regulatory elements and methods and use thereof
CN114450411A (zh) * 2019-04-01 2022-05-06 特纳亚治疗股份有限公司 具有工程化衣壳的腺相关病毒
AR126660A1 (es) * 2021-07-28 2023-11-01 Univ Brussel Vrije Mejorando la eficacia de la terapia génica dirigida a músculos

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