JP2024523707A5 - - Google Patents

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Publication number
JP2024523707A5
JP2024523707A5 JP2024500231A JP2024500231A JP2024523707A5 JP 2024523707 A5 JP2024523707 A5 JP 2024523707A5 JP 2024500231 A JP2024500231 A JP 2024500231A JP 2024500231 A JP2024500231 A JP 2024500231A JP 2024523707 A5 JP2024523707 A5 JP 2024523707A5
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JP
Japan
Prior art keywords
expression cassette
seq
sequence
item
polynucleotide sequence
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024500231A
Other languages
English (en)
Japanese (ja)
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JP2024523707A (ja
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Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/073574 external-priority patent/WO2023283649A1/en
Publication of JP2024523707A publication Critical patent/JP2024523707A/ja
Publication of JP2024523707A5 publication Critical patent/JP2024523707A5/ja
Pending legal-status Critical Current

Links

JP2024500231A 2021-07-08 2022-07-08 遺伝子治療のための最適化された発現カセット Pending JP2024523707A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202163219651P 2021-07-08 2021-07-08
US63/219,651 2021-07-08
PCT/US2022/073574 WO2023283649A1 (en) 2021-07-08 2022-07-08 Optimized expression cassettes for gene therapy

Publications (2)

Publication Number Publication Date
JP2024523707A JP2024523707A (ja) 2024-06-28
JP2024523707A5 true JP2024523707A5 (https=) 2025-07-16

Family

ID=83270905

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024500231A Pending JP2024523707A (ja) 2021-07-08 2022-07-08 遺伝子治療のための最適化された発現カセット

Country Status (12)

Country Link
US (2) US12151001B2 (https=)
EP (1) EP4367251A1 (https=)
JP (1) JP2024523707A (https=)
KR (1) KR20240032971A (https=)
AR (1) AR126407A1 (https=)
AU (1) AU2022307365A1 (https=)
CA (1) CA3224488A1 (https=)
CO (1) CO2024001148A2 (https=)
IL (1) IL309742A (https=)
MX (1) MX2024000175A (https=)
TW (1) TW202317768A (https=)
WO (1) WO2023283649A1 (https=)

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