JP2023537904A5 - - Google Patents
Info
- Publication number
- JP2023537904A5 JP2023537904A5 JP2023507761A JP2023507761A JP2023537904A5 JP 2023537904 A5 JP2023537904 A5 JP 2023537904A5 JP 2023507761 A JP2023507761 A JP 2023507761A JP 2023507761 A JP2023507761 A JP 2023507761A JP 2023537904 A5 JP2023537904 A5 JP 2023537904A5
- Authority
- JP
- Japan
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202063063852P | 2020-08-10 | 2020-08-10 | |
| US63/063,852 | 2020-08-10 | ||
| PCT/US2021/045443 WO2022035900A1 (en) | 2020-08-10 | 2021-08-10 | Gene therapies for neurodegenerative disorders |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2023537904A JP2023537904A (ja) | 2023-09-06 |
| JPWO2022035900A5 JPWO2022035900A5 (https=) | 2024-08-21 |
| JP2023537904A5 true JP2023537904A5 (https=) | 2024-08-21 |
Family
ID=77951788
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023507761A Pending JP2023537904A (ja) | 2020-08-10 | 2021-08-10 | 神経変性障害のための遺伝子療法 |
Country Status (10)
| Country | Link |
|---|---|
| US (1) | US20230346979A1 (https=) |
| EP (1) | EP4192517A1 (https=) |
| JP (1) | JP2023537904A (https=) |
| KR (1) | KR20230066360A (https=) |
| CN (1) | CN116437968A (https=) |
| AU (1) | AU2021325891A1 (https=) |
| CA (1) | CA3190864A1 (https=) |
| IL (1) | IL300409A (https=) |
| MX (1) | MX2023001564A (https=) |
| WO (1) | WO2022035900A1 (https=) |
Families Citing this family (10)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| KR102709597B1 (ko) | 2017-10-03 | 2024-09-26 | 프리베일 테라퓨틱스, 인크. | 리소좀 장애를 위한 유전자 요법 |
| PL3953377T3 (pl) | 2019-04-10 | 2026-02-16 | Prevail Therapeutics, Inc. | Terapie genowe zaburzeń lizosomalnych |
| CN116672341A (zh) * | 2022-02-23 | 2023-09-01 | 中国科学院上海药物研究所 | 雷帕霉素在治疗渐冻症和额颞叶痴呆中的应用 |
| EP4598940A1 (en) | 2022-10-04 | 2025-08-13 | Eli Lilly and Company | Gene therapy for trem2-associated diseases and disorders |
| EP4615981A1 (en) | 2022-11-11 | 2025-09-17 | Eli Lilly and Company | Synthetic nucleic acids including astrocyte-directed promoter constructs and methods of using the same |
| KR20250131772A (ko) * | 2022-11-13 | 2025-09-03 | 알렉시온 파마 인터내셔널 오퍼레이션즈 리미티드 | 전두측두엽 치매에 대한 유전자 요법 |
| WO2024163823A1 (en) * | 2023-02-02 | 2024-08-08 | Shape Therapeutics Inc. | Tissue-specific enhancers for regulating transcription |
| AU2024237478A1 (en) * | 2023-03-16 | 2025-10-30 | Genzyme Corporation | Treatment of dry age-related macular degeneration |
| WO2025251041A1 (en) * | 2024-05-31 | 2025-12-04 | Bluerock Therapeutics Lp | METHODS AND COMPOSITIONS FOR TREATING PROGRANULIN DEFICIENCIES USING iPSC-DERIVED CELLS |
| WO2026043765A1 (en) | 2024-08-21 | 2026-02-26 | Eli Lilly And Company | Engineered regulatory splice elements for gene therapies |
Family Cites Families (11)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| ES2385679T3 (es) | 2006-08-24 | 2012-07-30 | Virovek, Inc. | Expresión de células de insecto de genes con marcos de lectura abiertos superpuestos, métodos y composiciones de éstos |
| CN107002096A (zh) * | 2014-10-06 | 2017-08-01 | 阿罗根有限公司 | 基于aav的基因疗法 |
| HK1256341A1 (zh) * | 2015-05-15 | 2019-09-20 | 明尼苏达大学董事会 | 用於治疗性递送到中枢神经系统的腺相关物 |
| WO2017151884A1 (en) * | 2016-03-02 | 2017-09-08 | The Children's Hospital Of Philadelphia | Therapy for frontotemporal dementia |
| KR20230079511A (ko) | 2016-04-21 | 2023-06-07 | 바이로베크 인코포레이티드 | 곤충 세포에서의 aav 생산, 및 이를 위한 방법 및 조성물 |
| KR102719222B1 (ko) * | 2017-05-11 | 2024-10-21 | 더 트러스티스 오브 더 유니버시티 오브 펜실베니아 | 신경 세로이드 지질갈색소증에 대한 유전자 요법 |
| MA50016A (fr) * | 2017-07-06 | 2020-07-08 | Univ Pennsylvania | Thérapie génique médiée par aav9 pour traiter la mucopolysaccharidose de type i |
| EP3692075A4 (en) | 2017-10-03 | 2022-02-09 | Prevail Therapeutics, Inc. | GENE THERAPIES FOR LYSOSOMAL DISEASES |
| BR112020006671A2 (pt) | 2017-10-03 | 2020-12-01 | Prevail Therapeutics, Inc. | terapias genéticas para distúrbios lisossômicos |
| KR102709597B1 (ko) * | 2017-10-03 | 2024-09-26 | 프리베일 테라퓨틱스, 인크. | 리소좀 장애를 위한 유전자 요법 |
| PL3953377T3 (pl) | 2019-04-10 | 2026-02-16 | Prevail Therapeutics, Inc. | Terapie genowe zaburzeń lizosomalnych |
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2021
- 2021-08-10 US US18/041,199 patent/US20230346979A1/en active Pending
- 2021-08-10 IL IL300409A patent/IL300409A/en unknown
- 2021-08-10 MX MX2023001564A patent/MX2023001564A/es unknown
- 2021-08-10 JP JP2023507761A patent/JP2023537904A/ja active Pending
- 2021-08-10 CN CN202180068282.7A patent/CN116437968A/zh active Pending
- 2021-08-10 EP EP21778589.8A patent/EP4192517A1/en active Pending
- 2021-08-10 WO PCT/US2021/045443 patent/WO2022035900A1/en not_active Ceased
- 2021-08-10 KR KR1020237008510A patent/KR20230066360A/ko active Pending
- 2021-08-10 AU AU2021325891A patent/AU2021325891A1/en active Pending
- 2021-08-10 CA CA3190864A patent/CA3190864A1/en active Pending