JP2022526021A5 - - Google Patents

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Publication number
JP2022526021A5
JP2022526021A5 JP2021559877A JP2021559877A JP2022526021A5 JP 2022526021 A5 JP2022526021 A5 JP 2022526021A5 JP 2021559877 A JP2021559877 A JP 2021559877A JP 2021559877 A JP2021559877 A JP 2021559877A JP 2022526021 A5 JP2022526021 A5 JP 2022526021A5
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JP
Japan
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pharmaceutical composition
approximately
raav
composition according
itr
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JP2021559877A
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English (en)
Japanese (ja)
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JP2022526021A (ja
JP7664848B2 (ja
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Priority claimed from PCT/US2020/027788 external-priority patent/WO2020210713A1/en
Publication of JP2022526021A publication Critical patent/JP2022526021A/ja
Publication of JP2022526021A5 publication Critical patent/JP2022526021A5/ja
Application granted granted Critical
Publication of JP7664848B2 publication Critical patent/JP7664848B2/ja
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JP2021559877A 2019-04-10 2020-04-10 リソソーム障害のための遺伝子療法 Active JP7664848B2 (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US201962831840P 2019-04-10 2019-04-10
US62/831,840 2019-04-10
US202062990246P 2020-03-16 2020-03-16
US62/990,246 2020-03-16
PCT/US2020/027788 WO2020210713A1 (en) 2019-04-10 2020-04-10 Gene therapies for lysosomal disorders

Publications (3)

Publication Number Publication Date
JP2022526021A JP2022526021A (ja) 2022-05-20
JP2022526021A5 true JP2022526021A5 (https=) 2024-01-19
JP7664848B2 JP7664848B2 (ja) 2025-04-18

Family

ID=70554182

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2021559877A Active JP7664848B2 (ja) 2019-04-10 2020-04-10 リソソーム障害のための遺伝子療法

Country Status (11)

Country Link
US (2) US11903985B2 (https=)
EP (1) EP3953378A1 (https=)
JP (1) JP7664848B2 (https=)
KR (1) KR20220006527A (https=)
CN (1) CN114026115A (https=)
AU (1) AU2020270984B2 (https=)
BR (1) BR112021019880A2 (https=)
CA (1) CA3136117A1 (https=)
IL (1) IL286901A (https=)
MX (1) MX2021012184A (https=)
WO (1) WO2020210713A1 (https=)

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BR112020006661A2 (pt) 2017-10-03 2020-10-13 Prevail Therapeutics, Inc. terapias de genes para distúrbios lipossomais
AU2018346104B2 (en) 2017-10-03 2023-07-27 Prevail Therapeutics, Inc. Gene therapies for lysosomal disorders
BR112020008033A2 (pt) 2017-10-23 2020-10-27 Prevail Therapeutics, Inc. terapias gênicas para doença neurodegenerativa
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