JP2024546103A5 - - Google Patents
Info
- Publication number
- JP2024546103A5 JP2024546103A5 JP2024534162A JP2024534162A JP2024546103A5 JP 2024546103 A5 JP2024546103 A5 JP 2024546103A5 JP 2024534162 A JP2024534162 A JP 2024534162A JP 2024534162 A JP2024534162 A JP 2024534162A JP 2024546103 A5 JP2024546103 A5 JP 2024546103A5
- Authority
- JP
- Japan
- Prior art keywords
- vector
- approximately
- polynucleotide
- promoter
- jph2
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202163287393P | 2021-12-08 | 2021-12-08 | |
| US63/287,393 | 2021-12-08 | ||
| PCT/US2022/081122 WO2023108029A2 (en) | 2021-12-08 | 2022-12-07 | Junctophilin-2 (jph2) gene therapy using aav vector |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2024546103A JP2024546103A (ja) | 2024-12-17 |
| JP2024546103A5 true JP2024546103A5 (https=) | 2025-10-29 |
Family
ID=86731395
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024534162A Pending JP2024546103A (ja) | 2021-12-08 | 2022-12-07 | Ａａｖベクターを用いたジャンクトフィリン－２（ｊｐｈ２）遺伝子治療 |
Country Status (6)
| Country | Link |
|---|---|
| US (1) | US20240335565A1 (https=) |
| EP (1) | EP4444892A4 (https=) |
| JP (1) | JP2024546103A (https=) |
| CN (1) | CN118660969A (https=) |
| CA (1) | CA3240080A1 (https=) |
| WO (1) | WO2023108029A2 (https=) |
Families Citing this family (4)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| HUE055862T2 (hu) | 2016-04-20 | 2021-12-28 | Centro De Investig Energeticas | Készítmények és eljárások PKLR fokozott génexpressziójára |
| SG11202002263TA (en) | 2017-10-16 | 2020-04-29 | Centro De Investigaciones Energeticas Medioambientales Y Tecnologicas | Lentiviral vectors for delivery of pklr to treat pyruvate kinase deficiency |
| WO2019200167A1 (en) | 2018-04-11 | 2019-10-17 | Rocket Pharmaceuticals, Ltd. | Compositions and methods for stem cell transplant |
| WO2025212838A1 (en) * | 2024-04-03 | 2025-10-09 | Research Institute At Nationwide Children's Hospital | Products and methods for treating diseases or disorders associated with dux4 overexpression |
Family Cites Families (3)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US20040043382A1 (en) * | 2001-03-08 | 2004-03-04 | Muralidhara Padigaru | Novel proteins and nucleic acids encoding same |
| US11351270B2 (en) * | 2016-06-07 | 2022-06-07 | University Of Iowa Research Foundation | Junctophilin-2 fragments and uses therefor |
| KR20240032971A (ko) * | 2021-07-08 | 2024-03-12 | 테나야 테라퓨틱스, 인코포레이티드 | 유전자 요법을 위한 최적화된 발현 카세트 |
-
2022
- 2022-12-07 JP JP2024534162A patent/JP2024546103A/ja active Pending
- 2022-12-07 EP EP22905350.9A patent/EP4444892A4/en active Pending
- 2022-12-07 CA CA3240080A patent/CA3240080A1/en active Pending
- 2022-12-07 WO PCT/US2022/081122 patent/WO2023108029A2/en not_active Ceased
- 2022-12-07 US US18/718,021 patent/US20240335565A1/en active Pending
- 2022-12-07 CN CN202280090617.XA patent/CN118660969A/zh active Pending
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