JP2023536902A5 - - Google Patents
Info
- Publication number
- JP2023536902A5 JP2023536902A5 JP2023507555A JP2023507555A JP2023536902A5 JP 2023536902 A5 JP2023536902 A5 JP 2023536902A5 JP 2023507555 A JP2023507555 A JP 2023507555A JP 2023507555 A JP2023507555 A JP 2023507555A JP 2023536902 A5 JP2023536902 A5 JP 2023536902A5
- Authority
- JP
- Japan
- Prior art keywords
- promoter
- vector
- expression cassette
- pharmaceutical composition
- identity
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Granted
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202063061726P | 2020-08-05 | 2020-08-05 | |
| US63/061,726 | 2020-08-05 | ||
| PCT/US2021/044416 WO2022031760A1 (en) | 2020-08-05 | 2021-08-03 | Adeno-associated viral vector for glut1 expression and uses thereof |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2023536902A JP2023536902A (ja) | 2023-08-30 |
| JP2023536902A5 true JP2023536902A5 (https=) | 2024-08-13 |
| JP7853952B2 JP7853952B2 (ja) | 2026-04-30 |
Family
ID=80118621
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023507555A Active JP7853952B2 (ja) | 2020-08-05 | 2021-08-03 | Glut1発現のためのアデノ随伴ウイルスベクターおよびその使用 |
Country Status (11)
| Country | Link |
|---|---|
| US (1) | US20230272422A1 (https=) |
| EP (1) | EP4192960A4 (https=) |
| JP (1) | JP7853952B2 (https=) |
| KR (1) | KR20230043123A (https=) |
| CN (1) | CN116113700A (https=) |
| AU (1) | AU2021321412A1 (https=) |
| BR (1) | BR112023001418A2 (https=) |
| CA (1) | CA3184233A1 (https=) |
| IL (1) | IL300185A (https=) |
| MX (1) | MX2023001419A (https=) |
| WO (1) | WO2022031760A1 (https=) |
Families Citing this family (8)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| HUE055862T2 (hu) | 2016-04-20 | 2021-12-28 | Centro De Investig Energeticas | Készítmények és eljárások PKLR fokozott génexpressziójára |
| SG11202002263TA (en) | 2017-10-16 | 2020-04-29 | Centro De Investigaciones Energeticas Medioambientales Y Tecnologicas | Lentiviral vectors for delivery of pklr to treat pyruvate kinase deficiency |
| WO2019200167A1 (en) | 2018-04-11 | 2019-10-17 | Rocket Pharmaceuticals, Ltd. | Compositions and methods for stem cell transplant |
| MX2020011386A (es) | 2018-04-27 | 2021-01-29 | Spacecraft Seven Llc | Terapia genica para la degeneracion del snc. |
| KR20230043869A (ko) | 2020-08-07 | 2023-03-31 | 스페이스크래프트 세븐, 엘엘씨 | Aav 벡터를 사용한 플라코필린-2(pkp2) 유전자 요법 |
| CN114457045B (zh) * | 2022-02-25 | 2023-07-14 | 中国人民解放军军事科学院军事医学研究院 | 抑制Slc2a1的RNAi腺相关病毒及其制备和应用 |
| WO2025082176A1 (zh) * | 2023-10-19 | 2025-04-24 | 北京脑科学与类脑研究所 | 一种脑血管内皮细胞嵌合型启动子和重组表达载体及应用 |
| WO2025137149A1 (en) * | 2023-12-19 | 2025-06-26 | The Trustees Of Columbia University In The City Of New York | Compositions and methods for therapeutic vectors targeting brain microvasculature |
Family Cites Families (5)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US8071740B2 (en) | 2000-11-17 | 2011-12-06 | Vascular Biogenics Ltd. | Promoters exhibiting endothelial cell specificity and methods of using same for regulation of angiogenesis |
| US20070161031A1 (en) * | 2005-12-16 | 2007-07-12 | The Board Of Trustees Of The Leland Stanford Junior University | Functional arrays for high throughput characterization of gene expression regulatory elements |
| KR20240119152A (ko) | 2015-03-10 | 2024-08-06 | 더 트러스티스 오브 컬럼비아 유니버시티 인 더 시티 오브 뉴욕 | 재조합 glut1 아데노-관련 바이러스 벡터 작제물 및 glut1 발현을 회복하기 위한 관련된 방법 |
| US11446375B2 (en) | 2015-12-22 | 2022-09-20 | Vrije Universiteit Brussel | Endothelium-specific nucleic acid regulatory elements and methods and use thereof |
| JP6996728B2 (ja) * | 2016-01-07 | 2022-01-17 | 学校法人自治医科大学 | グルコーストランスポーター1発現用アデノ随伴ウイルスベクター |
-
2021
- 2021-08-03 CN CN202180057450.2A patent/CN116113700A/zh active Pending
- 2021-08-03 EP EP21854255.3A patent/EP4192960A4/en active Pending
- 2021-08-03 BR BR112023001418A patent/BR112023001418A2/pt unknown
- 2021-08-03 WO PCT/US2021/044416 patent/WO2022031760A1/en not_active Ceased
- 2021-08-03 US US18/019,393 patent/US20230272422A1/en active Pending
- 2021-08-03 MX MX2023001419A patent/MX2023001419A/es unknown
- 2021-08-03 CA CA3184233A patent/CA3184233A1/en active Pending
- 2021-08-03 JP JP2023507555A patent/JP7853952B2/ja active Active
- 2021-08-03 IL IL300185A patent/IL300185A/en unknown
- 2021-08-03 AU AU2021321412A patent/AU2021321412A1/en active Pending
- 2021-08-03 KR KR1020237003435A patent/KR20230043123A/ko active Pending
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