KR20230043123A - Glut1 발현을 위한 아데노-연관 바이러스 벡터 및 이의 사용 - Google Patents

Glut1 발현을 위한 아데노-연관 바이러스 벡터 및 이의 사용 Download PDF

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KR20230043123A
KR20230043123A KR1020237003435A KR20237003435A KR20230043123A KR 20230043123 A KR20230043123 A KR 20230043123A KR 1020237003435 A KR1020237003435 A KR 1020237003435A KR 20237003435 A KR20237003435 A KR 20237003435A KR 20230043123 A KR20230043123 A KR 20230043123A
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크리스토퍼 딘 헤르조그
체스터 비텐코트 새크라멘토
라이 프라바카
데이비드 릭스
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스페이스크래프트 세븐, 엘엘씨
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KR1020237003435A 2020-08-05 2021-08-03 Glut1 발현을 위한 아데노-연관 바이러스 벡터 및 이의 사용 Pending KR20230043123A (ko)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202063061726P 2020-08-05 2020-08-05
US63/061,726 2020-08-05
PCT/US2021/044416 WO2022031760A1 (en) 2020-08-05 2021-08-03 Adeno-associated viral vector for glut1 expression and uses thereof

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KR20230043123A true KR20230043123A (ko) 2023-03-30

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KR1020237003435A Pending KR20230043123A (ko) 2020-08-05 2021-08-03 Glut1 발현을 위한 아데노-연관 바이러스 벡터 및 이의 사용

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US (1) US20230272422A1 (https=)
EP (1) EP4192960A4 (https=)
JP (1) JP7853952B2 (https=)
KR (1) KR20230043123A (https=)
CN (1) CN116113700A (https=)
AU (1) AU2021321412A1 (https=)
BR (1) BR112023001418A2 (https=)
CA (1) CA3184233A1 (https=)
IL (1) IL300185A (https=)
MX (1) MX2023001419A (https=)
WO (1) WO2022031760A1 (https=)

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HUE055862T2 (hu) 2016-04-20 2021-12-28 Centro De Investig Energeticas Készítmények és eljárások PKLR fokozott génexpressziójára
SG11202002263TA (en) 2017-10-16 2020-04-29 Centro De Investigaciones Energeticas Medioambientales Y Tecnologicas Lentiviral vectors for delivery of pklr to treat pyruvate kinase deficiency
WO2019200167A1 (en) 2018-04-11 2019-10-17 Rocket Pharmaceuticals, Ltd. Compositions and methods for stem cell transplant
MX2020011386A (es) 2018-04-27 2021-01-29 Spacecraft Seven Llc Terapia genica para la degeneracion del snc.
KR20230043869A (ko) 2020-08-07 2023-03-31 스페이스크래프트 세븐, 엘엘씨 Aav 벡터를 사용한 플라코필린-2(pkp2) 유전자 요법
CN114457045B (zh) * 2022-02-25 2023-07-14 中国人民解放军军事科学院军事医学研究院 抑制Slc2a1的RNAi腺相关病毒及其制备和应用
WO2025082176A1 (zh) * 2023-10-19 2025-04-24 北京脑科学与类脑研究所 一种脑血管内皮细胞嵌合型启动子和重组表达载体及应用
WO2025137149A1 (en) * 2023-12-19 2025-06-26 The Trustees Of Columbia University In The City Of New York Compositions and methods for therapeutic vectors targeting brain microvasculature

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* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US8071740B2 (en) 2000-11-17 2011-12-06 Vascular Biogenics Ltd. Promoters exhibiting endothelial cell specificity and methods of using same for regulation of angiogenesis
US20070161031A1 (en) * 2005-12-16 2007-07-12 The Board Of Trustees Of The Leland Stanford Junior University Functional arrays for high throughput characterization of gene expression regulatory elements
KR20240119152A (ko) 2015-03-10 2024-08-06 더 트러스티스 오브 컬럼비아 유니버시티 인 더 시티 오브 뉴욕 재조합 glut1 아데노-관련 바이러스 벡터 작제물 및 glut1 발현을 회복하기 위한 관련된 방법
US11446375B2 (en) 2015-12-22 2022-09-20 Vrije Universiteit Brussel Endothelium-specific nucleic acid regulatory elements and methods and use thereof
JP6996728B2 (ja) * 2016-01-07 2022-01-17 学校法人自治医科大学 グルコーストランスポーター１発現用アデノ随伴ウイルスベクター

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MX2023001419A (es) 2023-05-16
IL300185A (en) 2023-03-01
BR112023001418A2 (pt) 2023-03-07
CA3184233A1 (en) 2022-02-10
JP2023536902A (ja) 2023-08-30
JP7853952B2 (ja) 2026-04-30
EP4192960A4 (en) 2024-11-27
AU2021321412A1 (en) 2023-04-06
WO2022031760A1 (en) 2022-02-10
CN116113700A (zh) 2023-05-12
EP4192960A1 (en) 2023-06-14
US20230272422A1 (en) 2023-08-31

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