JP2025505662A5 - - Google Patents
Info
- Publication number
- JP2025505662A5 JP2025505662A5 JP2024547024A JP2024547024A JP2025505662A5 JP 2025505662 A5 JP2025505662 A5 JP 2025505662A5 JP 2024547024 A JP2024547024 A JP 2024547024A JP 2024547024 A JP2024547024 A JP 2024547024A JP 2025505662 A5 JP2025505662 A5 JP 2025505662A5
- Authority
- JP
- Japan
- Prior art keywords
- seq
- raav
- pharmaceutical composition
- promoter
- glut1
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Withdrawn
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202263307963P | 2022-02-08 | 2022-02-08 | |
| US63/307,963 | 2022-02-08 | ||
| PCT/US2023/062231 WO2023154763A2 (en) | 2022-02-08 | 2023-02-08 | Adeno-associated viral vector for glut1 expression and uses thereof |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2025505662A JP2025505662A (ja) | 2025-02-28 |
| JP2025505662A5 true JP2025505662A5 (https=) | 2026-02-02 |
Family
ID=87565090
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024547024A Withdrawn JP2025505662A (ja) | 2022-02-08 | 2023-02-08 | Ｇｌｕｔ１発現用アデノ随伴ウイルスベクターおよびその使用 |
Country Status (11)
| Country | Link |
|---|---|
| US (1) | US20250135040A1 (https=) |
| EP (1) | EP4475873A2 (https=) |
| JP (1) | JP2025505662A (https=) |
| KR (1) | KR20240142487A (https=) |
| CN (1) | CN118843473A (https=) |
| AU (1) | AU2023217712A1 (https=) |
| CA (1) | CA3243383A1 (https=) |
| CL (1) | CL2024002376A1 (https=) |
| IL (1) | IL314602A (https=) |
| MX (1) | MX2024009685A (https=) |
| WO (1) | WO2023154763A2 (https=) |
Families Citing this family (4)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| HUE055862T2 (hu) | 2016-04-20 | 2021-12-28 | Centro De Investig Energeticas | Készítmények és eljárások PKLR fokozott génexpressziójára |
| SG11202002263TA (en) | 2017-10-16 | 2020-04-29 | Centro De Investigaciones Energeticas Medioambientales Y Tecnologicas | Lentiviral vectors for delivery of pklr to treat pyruvate kinase deficiency |
| WO2019200167A1 (en) | 2018-04-11 | 2019-10-17 | Rocket Pharmaceuticals, Ltd. | Compositions and methods for stem cell transplant |
| MX2020011386A (es) | 2018-04-27 | 2021-01-29 | Spacecraft Seven Llc | Terapia genica para la degeneracion del snc. |
Family Cites Families (3)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| DE102014207498A1 (de) * | 2014-04-17 | 2015-10-22 | Universitätsklinikum Hamburg-Eppendorf | Viraler Vektor für den zielgerichteten Gentransfer in Gehirn und Rückenmark |
| EP3256170B1 (en) * | 2015-02-13 | 2020-09-23 | University of Massachusetts | Compositions and methods for transient delivery of nucleases |
| KR20240119152A (ko) * | 2015-03-10 | 2024-08-06 | 더 트러스티스 오브 컬럼비아 유니버시티 인 더 시티 오브 뉴욕 | 재조합 glut1 아데노-관련 바이러스 벡터 작제물 및 glut1 발현을 회복하기 위한 관련된 방법 |
-
2023
- 2023-02-08 IL IL314602A patent/IL314602A/en unknown
- 2023-02-08 CN CN202380026584.7A patent/CN118843473A/zh not_active Withdrawn
- 2023-02-08 US US18/837,053 patent/US20250135040A1/en active Pending
- 2023-02-08 EP EP23753633.9A patent/EP4475873A2/en not_active Withdrawn
- 2023-02-08 MX MX2024009685A patent/MX2024009685A/es unknown
- 2023-02-08 KR KR1020247028432A patent/KR20240142487A/ko not_active Withdrawn
- 2023-02-08 WO PCT/US2023/062231 patent/WO2023154763A2/en not_active Ceased
- 2023-02-08 AU AU2023217712A patent/AU2023217712A1/en active Pending
- 2023-02-08 CA CA3243383A patent/CA3243383A1/en active Pending
- 2023-02-08 JP JP2024547024A patent/JP2025505662A/ja not_active Withdrawn
-
2024
- 2024-08-08 CL CL2024002376A patent/CL2024002376A1/es unknown
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