KR20240142487A - Glut1 발현을 위한 아데노-관련 바이러스 벡터 및 이의 용도 - Google Patents

Glut1 발현을 위한 아데노-관련 바이러스 벡터 및 이의 용도 Download PDF

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KR20240142487A
KR20240142487A KR1020247028432A KR20247028432A KR20240142487A KR 20240142487 A KR20240142487 A KR 20240142487A KR 1020247028432 A KR1020247028432 A KR 1020247028432A KR 20247028432 A KR20247028432 A KR 20247028432A KR 20240142487 A KR20240142487 A KR 20240142487A
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South Korea
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raav
seq
raav virion
glut1
virion
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Korean (ko)
Inventor
크리스토퍼 딘 헤르조그
체스터 비텐코트 새크라멘토
라즈 프라바카
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스페이스크래프트 세븐, 엘엘씨
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    • A61K48/0058—Nucleic acids adapted for tissue specific expression, e.g. having tissue specific promoters as part of a contruct
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KR1020247028432A 2022-02-08 2023-02-08 Glut1 발현을 위한 아데노-관련 바이러스 벡터 및 이의 용도 Withdrawn KR20240142487A (ko)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202263307963P 2022-02-08 2022-02-08
US63/307,963 2022-02-08
PCT/US2023/062231 WO2023154763A2 (en) 2022-02-08 2023-02-08 Adeno-associated viral vector for glut1 expression and uses thereof

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Publication Number Publication Date
KR20240142487A true KR20240142487A (ko) 2024-09-30

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KR1020247028432A Withdrawn KR20240142487A (ko) 2022-02-08 2023-02-08 Glut1 발현을 위한 아데노-관련 바이러스 벡터 및 이의 용도

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US (1) US20250135040A1 (https=)
EP (1) EP4475873A2 (https=)
JP (1) JP2025505662A (https=)
KR (1) KR20240142487A (https=)
CN (1) CN118843473A (https=)
AU (1) AU2023217712A1 (https=)
CA (1) CA3243383A1 (https=)
CL (1) CL2024002376A1 (https=)
IL (1) IL314602A (https=)
MX (1) MX2024009685A (https=)
WO (1) WO2023154763A2 (https=)

Families Citing this family (4)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
HUE055862T2 (hu) 2016-04-20 2021-12-28 Centro De Investig Energeticas Készítmények és eljárások PKLR fokozott génexpressziójára
SG11202002263TA (en) 2017-10-16 2020-04-29 Centro De Investigaciones Energeticas Medioambientales Y Tecnologicas Lentiviral vectors for delivery of pklr to treat pyruvate kinase deficiency
WO2019200167A1 (en) 2018-04-11 2019-10-17 Rocket Pharmaceuticals, Ltd. Compositions and methods for stem cell transplant
MX2020011386A (es) 2018-04-27 2021-01-29 Spacecraft Seven Llc Terapia genica para la degeneracion del snc.

Family Cites Families (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
DE102014207498A1 (de) * 2014-04-17 2015-10-22 Universitätsklinikum Hamburg-Eppendorf Viraler Vektor für den zielgerichteten Gentransfer in Gehirn und Rückenmark
EP3256170B1 (en) * 2015-02-13 2020-09-23 University of Massachusetts Compositions and methods for transient delivery of nucleases
KR20240119152A (ko) * 2015-03-10 2024-08-06 더 트러스티스 오브 컬럼비아 유니버시티 인 더 시티 오브 뉴욕 재조합 glut1 아데노-관련 바이러스 벡터 작제물 및 glut1 발현을 회복하기 위한 관련된 방법

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Publication number Publication date
EP4475873A2 (en) 2024-12-18
WO2023154763A2 (en) 2023-08-17
US20250135040A1 (en) 2025-05-01
AU2023217712A1 (en) 2024-08-08
WO2023154763A3 (en) 2023-09-28
CL2024002376A1 (es) 2025-01-10
IL314602A (en) 2024-09-01
CA3243383A1 (en) 2023-08-17
CN118843473A (zh) 2024-10-25
JP2025505662A (ja) 2025-02-28
MX2024009685A (es) 2024-08-19

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