JP2022535749A5 - - Google Patents

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Publication number
JP2022535749A5
JP2022535749A5 JP2021570376A JP2021570376A JP2022535749A5 JP 2022535749 A5 JP2022535749 A5 JP 2022535749A5 JP 2021570376 A JP2021570376 A JP 2021570376A JP 2021570376 A JP2021570376 A JP 2021570376A JP 2022535749 A5 JP2022535749 A5 JP 2022535749A5
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item
sequence
aav
expression cassette
expression
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JP2021570376A
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JP2022535749A (ja
JP7432621B2 (ja
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Priority claimed from PCT/US2020/035431 external-priority patent/WO2020243651A1/en
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JP2021570376A 2019-05-29 2020-05-29 選択的遺伝子調節のための組成物および方法 Active JP7432621B2 (ja)

Applications Claiming Priority (7)

Application Number Priority Date Filing Date Title
US201962854238P 2019-05-29 2019-05-29
US62/854,238 2019-05-29
US201962857727P 2019-06-05 2019-06-05
US62/857,727 2019-06-05
US202063008569P 2020-04-10 2020-04-10
US63/008,569 2020-04-10
PCT/US2020/035431 WO2020243651A1 (en) 2019-05-29 2020-05-29 Compositions and methods for selective gene regulation

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JP2022535749A JP2022535749A (ja) 2022-08-10
JP2022535749A5 true JP2022535749A5 (https=) 2022-11-10
JP7432621B2 JP7432621B2 (ja) 2024-02-16

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US (2) US12516350B2 (https=)
EP (2) EP3976798B1 (https=)
JP (1) JP7432621B2 (https=)
KR (1) KR102808368B1 (https=)
CN (1) CN114174520B (https=)
AU (2) AU2020282352B2 (https=)
BR (1) BR112021024055A2 (https=)
CA (1) CA3141900C (https=)
CL (1) CL2021003151A1 (https=)
CO (1) CO2021017544A2 (https=)
ES (1) ES3062644T3 (https=)
IL (1) IL288313A (https=)
MX (1) MX2021014460A (https=)
PL (1) PL3976798T3 (https=)
SG (1) SG11202113048SA (https=)
TW (1) TWI872078B (https=)
WO (1) WO2020243651A1 (https=)

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JP2024545923A (ja) * 2021-12-30 2024-12-13 リーゲル セラピューティクス,インコーポレイティッド ナトリウム電位依存性チャネルアルファサブユニット1の発現を調節するための組成物、及びその使用
CN114507693A (zh) * 2022-02-09 2022-05-17 中国人民解放军陆军军医大学第一附属医院 重组腺相关病毒表达载体及其应用
JP2026504390A (ja) * 2023-02-01 2026-02-05 アレン インスティテュート インテインを介した電位依存性ナトリウムチャネルの機能の再構築
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