JP2022548270A5 - - Google Patents
Info
- Publication number
- JP2022548270A5 JP2022548270A5 JP2022516687A JP2022516687A JP2022548270A5 JP 2022548270 A5 JP2022548270 A5 JP 2022548270A5 JP 2022516687 A JP2022516687 A JP 2022516687A JP 2022516687 A JP2022516687 A JP 2022516687A JP 2022548270 A5 JP2022548270 A5 JP 2022548270A5
- Authority
- JP
- Japan
- Prior art keywords
- nucleic acid
- fxn
- human
- promoter
- acid construct
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201962899953P | 2019-09-13 | 2019-09-13 | |
| US62/899,953 | 2019-09-13 | ||
| PCT/US2020/050551 WO2021050991A1 (en) | 2019-09-13 | 2020-09-11 | Compositions and methods for treatment of friedreich's ataxia |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2022548270A JP2022548270A (ja) | 2022-11-17 |
| JP2022548270A5 true JP2022548270A5 (https=) | 2023-07-25 |
Family
ID=74865919
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022516687A Pending JP2022548270A (ja) | 2019-09-13 | 2020-09-11 | フリードライヒ運動失調症の治療のための組成物及び方法 |
Country Status (6)
| Country | Link |
|---|---|
| US (1) | US20220211737A1 (https=) |
| EP (1) | EP4028027A4 (https=) |
| JP (1) | JP2022548270A (https=) |
| AU (1) | AU2020346914A1 (https=) |
| CA (1) | CA3151073A1 (https=) |
| WO (1) | WO2021050991A1 (https=) |
Families Citing this family (3)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| EP4426845A4 (en) * | 2021-11-01 | 2025-10-01 | Univ Florida | AAV-MEDIATED THERAPIES FOR VISION LOSS ASSOCIATED WITH FRIEDREICH ATAXIA |
| JP2025537125A (ja) * | 2022-11-01 | 2025-11-14 | プリベイル・セラピューティクス・インコーポレイテッド | フリードライヒ運動失調症の治療のための組成物及び方法 |
| WO2025157942A2 (en) * | 2024-01-23 | 2025-07-31 | Icm (Institut Du Cerveau Et De La Moelle Épinière) | Encapsulated engineered cells for treating a disease or condition affecting the nervous system |
Family Cites Families (8)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| MX2017009336A (es) * | 2015-01-16 | 2017-11-15 | Voyager Therapeutics Inc | Polinucleótidos dirigidos al sistema nervioso central. |
| US10617770B2 (en) * | 2015-04-24 | 2020-04-14 | University Of Florida Research Foundation, Incorporated | AAV vector for treatment of Friedreich's ataxia |
| MX2018004755A (es) * | 2015-10-29 | 2018-12-19 | Voyager Therapeutics Inc | Entrega de polinucleotidos dirigidos al sistema nervioso central. |
| SG11201802408RA (en) * | 2015-11-05 | 2018-05-30 | Bamboo Therapeutics Inc | Modified friedreich ataxia genes and vectors for gene therapy |
| WO2018089527A1 (en) * | 2016-11-09 | 2018-05-17 | Intrexon Corporation | Frataxin expression constructs |
| EP3641834B1 (en) * | 2017-06-19 | 2023-10-04 | Translate Bio, Inc. | Messenger rna therapy for the treatment of friedreich's ataxia |
| WO2019000093A1 (en) * | 2017-06-29 | 2019-01-03 | UNIVERSITé LAVAL | PLATINUM TALE AND USE THEREOF TO INCREASE THE EXPRESSION OF FRATAXIN |
| EP4089173A1 (en) * | 2017-10-17 | 2022-11-16 | Fundació Institut d'Investigació en Ciències de la Salut Germans Trias i Pujol | Vectors for the treatment of friedreich's ataxia |
-
2020
- 2020-09-11 AU AU2020346914A patent/AU2020346914A1/en active Pending
- 2020-09-11 EP EP20863569.8A patent/EP4028027A4/en active Pending
- 2020-09-11 JP JP2022516687A patent/JP2022548270A/ja active Pending
- 2020-09-11 WO PCT/US2020/050551 patent/WO2021050991A1/en not_active Ceased
- 2020-09-11 US US17/434,318 patent/US20220211737A1/en not_active Abandoned
- 2020-09-11 CA CA3151073A patent/CA3151073A1/en active Pending
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