JP2022548270A5 - - Google Patents

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Publication number
JP2022548270A5
JP2022548270A5 JP2022516687A JP2022516687A JP2022548270A5 JP 2022548270 A5 JP2022548270 A5 JP 2022548270A5 JP 2022516687 A JP2022516687 A JP 2022516687A JP 2022516687 A JP2022516687 A JP 2022516687A JP 2022548270 A5 JP2022548270 A5 JP 2022548270A5
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JP
Japan
Application number
JP2022516687A
Other languages
Japanese (ja)
Other versions
JPWO2021050991A5 (https=
JP2022548270A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2020/050551 external-priority patent/WO2021050991A1/en
Publication of JP2022548270A publication Critical patent/JP2022548270A/ja
Publication of JPWO2021050991A5 publication Critical patent/JPWO2021050991A5/ja
Publication of JP2022548270A5 publication Critical patent/JP2022548270A5/ja
Pending legal-status Critical Current

Links

JP2022516687A 2019-09-13 2020-09-11 フリードライヒ運動失調症の治療のための組成物及び方法 Pending JP2022548270A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201962899953P 2019-09-13 2019-09-13
US62/899,953 2019-09-13
PCT/US2020/050551 WO2021050991A1 (en) 2019-09-13 2020-09-11 Compositions and methods for treatment of friedreich's ataxia

Publications (3)

Publication Number Publication Date
JP2022548270A JP2022548270A (ja) 2022-11-17
JPWO2021050991A5 JPWO2021050991A5 (https=) 2023-07-25
JP2022548270A5 true JP2022548270A5 (https=) 2023-07-25

Family

ID=74865919

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2022516687A Pending JP2022548270A (ja) 2019-09-13 2020-09-11 フリードライヒ運動失調症の治療のための組成物及び方法

Country Status (6)

Country Link
US (1) US20220211737A1 (https=)
EP (1) EP4028027A4 (https=)
JP (1) JP2022548270A (https=)
AU (1) AU2020346914A1 (https=)
CA (1) CA3151073A1 (https=)
WO (1) WO2021050991A1 (https=)

Families Citing this family (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP4426845A4 (en) * 2021-11-01 2025-10-01 Univ Florida AAV-MEDIATED THERAPIES FOR VISION LOSS ASSOCIATED WITH FRIEDREICH ATAXIA
WO2024097772A1 (en) * 2022-11-01 2024-05-10 Lacerta Therapeutics, Inc. Compositions and methods for treatment of friedreich's ataxia
WO2025157942A2 (en) * 2024-01-23 2025-07-31 Icm (Institut Du Cerveau Et De La Moelle Épinière) Encapsulated engineered cells for treating a disease or condition affecting the nervous system

Family Cites Families (8)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP3245221A4 (en) * 2015-01-16 2018-06-13 Voyager Therapeutics, Inc. Central nervous system targeting polynucleotides
WO2016172659A1 (en) * 2015-04-24 2016-10-27 University Of Florida Research Foundation, Inc. Aav vector for treatment of friedreich's ataxia
WO2017075338A2 (en) * 2015-10-29 2017-05-04 Voyager Therapeutics, Inc. Delivery of central nervous system targeting polynucleotides
RU2021102893A (ru) * 2015-11-05 2021-03-03 Бамбу Терапьютикс, Инк. Модифицированные гены атаксии фридрейха и векторы для генной терапии
CN110139933B (zh) * 2016-11-09 2024-03-08 英特瑞克斯顿股份有限公司 共济蛋白表达构建体
EP3641834B1 (en) * 2017-06-19 2023-10-04 Translate Bio, Inc. Messenger rna therapy for the treatment of friedreich's ataxia
WO2019000093A1 (en) * 2017-06-29 2019-01-03 UNIVERSITé LAVAL PLATINUM TALE AND USE THEREOF TO INCREASE THE EXPRESSION OF FRATAXIN
WO2019076973A1 (en) * 2017-10-17 2019-04-25 Fundació Institut D'investigació En Ciències De La Salut Germans Trias I Pujol VECTORS FOR THE TREATMENT OF FRIEDREICH ATAXIA

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