JP2017510298A5 - - Google Patents

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JP2017510298A5
JP2017510298A5 JP2017501101A JP2017501101A JP2017510298A5 JP 2017510298 A5 JP2017510298 A5 JP 2017510298A5 JP 2017501101 A JP2017501101 A JP 2017501101A JP 2017501101 A JP2017501101 A JP 2017501101A JP 2017510298 A5 JP2017510298 A5 JP 2017510298A5
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pharmaceutical composition
nucleic acid
seq
cell
inhibitory nucleic
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JP2017510298A (ja
JP6756700B2 (ja
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JP2017501101A 2014-03-18 2015-03-18 筋萎縮性側索硬化症を処置するためのrAAVベースの組成物および方法 Active JP6756700B2 (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201461955189P 2014-03-18 2014-03-18
US61/955,189 2014-03-18
PCT/US2015/021321 WO2015143078A1 (en) 2014-03-18 2015-03-18 Raav-based compositions and methods for treating amyotrophic lateral sclerosis

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JP2019159514A Division JP7051118B2 (ja) 2014-03-18 2019-09-02 筋萎縮性側索硬化症を処置するためのrAAVベースの組成物および方法

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JP2017510298A JP2017510298A (ja) 2017-04-13
JP2017510298A5 true JP2017510298A5 (https=) 2018-04-26
JP6756700B2 JP6756700B2 (ja) 2020-09-16

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JP2017501101A Active JP6756700B2 (ja) 2014-03-18 2015-03-18 筋萎縮性側索硬化症を処置するためのrAAVベースの組成物および方法
JP2019159514A Active JP7051118B2 (ja) 2014-03-18 2019-09-02 筋萎縮性側索硬化症を処置するためのrAAVベースの組成物および方法
JP2021093003A Pending JP2021152030A (ja) 2014-03-18 2021-06-02 筋萎縮性側索硬化症を処置するためのrAAVベースの組成物および方法
JP2024000089A Pending JP2024032730A (ja) 2014-03-18 2024-01-04 筋萎縮性側索硬化症を処置するためのrAAVベースの組成物および方法

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JP2019159514A Active JP7051118B2 (ja) 2014-03-18 2019-09-02 筋萎縮性側索硬化症を処置するためのrAAVベースの組成物および方法
JP2021093003A Pending JP2021152030A (ja) 2014-03-18 2021-06-02 筋萎縮性側索硬化症を処置するためのrAAVベースの組成物および方法
JP2024000089A Pending JP2024032730A (ja) 2014-03-18 2024-01-04 筋萎縮性側索硬化症を処置するためのrAAVベースの組成物および方法

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US (6) US10280418B2 (https=)
EP (3) EP3750907A3 (https=)
JP (4) JP6756700B2 (https=)
AU (3) AU2015231294B2 (https=)
CA (2) CA2942515C (https=)
DK (1) DK3119797T3 (https=)
ES (1) ES2856403T3 (https=)
WO (1) WO2015143078A1 (https=)

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