JP2023509443A5 - - Google Patents
Info
- Publication number
- JP2023509443A5 JP2023509443A5 JP2022540917A JP2022540917A JP2023509443A5 JP 2023509443 A5 JP2023509443 A5 JP 2023509443A5 JP 2022540917 A JP2022540917 A JP 2022540917A JP 2022540917 A JP2022540917 A JP 2022540917A JP 2023509443 A5 JP2023509443 A5 JP 2023509443A5
- Authority
- JP
- Japan
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201962955667P | 2019-12-31 | 2019-12-31 | |
| US62/955,667 | 2019-12-31 | ||
| PCT/US2020/067664 WO2021138559A1 (en) | 2019-12-31 | 2020-12-31 | Improved aav-abcd1 constructs and use for treatment or prevention of adrenoleukodystrophy (ald) and/or adrenomyeloneuropathy (amn) |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2023509443A JP2023509443A (ja) | 2023-03-08 |
| JP2023509443A5 true JP2023509443A5 (https=) | 2023-07-05 |
| JPWO2021138559A5 JPWO2021138559A5 (https=) | 2023-07-05 |
Family
ID=76686949
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022540917A Pending JP2023509443A (ja) | 2019-12-31 | 2020-12-31 | 改善されたａａｖ－ａｂｃｄ１コンストラクトならびに副腎白質ジストロフィー（ａｌｄ）および／または副腎脊髄ニューロパチー（ａｍｎ）の処置または予防のための使用 |
Country Status (11)
| Country | Link |
|---|---|
| US (2) | US11779655B2 (https=) |
| EP (1) | EP4085143B1 (https=) |
| JP (1) | JP2023509443A (https=) |
| KR (1) | KR20220128632A (https=) |
| CN (1) | CN116096904A (https=) |
| AU (1) | AU2020416291A1 (https=) |
| BR (1) | BR112022013027A2 (https=) |
| CA (1) | CA3166374A1 (https=) |
| IL (1) | IL294278A (https=) |
| MX (1) | MX2022008201A (https=) |
| WO (1) | WO2021138559A1 (https=) |
Families Citing this family (4)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| CA3228344A1 (en) * | 2021-08-06 | 2023-02-09 | Wuhan Neurophth Biotechnology Limited Company | Composition and method for treating leber's hereditary optic neuropathy caused by nd4 mutation |
| KR20250009975A (ko) * | 2022-05-12 | 2025-01-20 | 아브너진 인코포레이티드 | 재조합 파르보바이러스 생산을 위한 조성물 및 방법 |
| EP4536862A1 (en) * | 2022-06-09 | 2025-04-16 | Wisconsin Alumni Research Foundation | Generation of next generation recombinant aav gene therapy vectors that adopt 3d conformation |
| AU2024315073A1 (en) * | 2023-07-28 | 2026-01-22 | Regeneron Pharmaceuticals, Inc. | Use of bgh-sv40l tandem polya to enhance transgene expression during unidirectional gene insertion |
Family Cites Families (23)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| NZ532635A (en) | 2001-11-13 | 2007-05-31 | Univ Pennsylvania | A method of identifying unknown adeno-associated virus (AAV) sequences and a kit for the method |
| DK2359869T3 (en) | 2001-12-17 | 2019-04-15 | Univ Pennsylvania | Sequences of adeno-associated virus (AAV) serotype 8, vectors containing these, and uses thereof |
| CN1856576B (zh) | 2003-09-30 | 2011-05-04 | 宾夕法尼亚州立大学托管会 | 腺伴随病毒(aav)进化支、序列、含有这些序列的载体及它们的应用 |
| WO2006110689A2 (en) | 2005-04-07 | 2006-10-19 | The Trustees Of The University Of Pennsylvania | Method of increasing the function of an aav vector |
| US7588772B2 (en) | 2006-03-30 | 2009-09-15 | Board Of Trustees Of The Leland Stamford Junior University | AAV capsid library and AAV capsid proteins |
| US8466271B2 (en) * | 2008-07-23 | 2013-06-18 | Boehringer Ingelheim Pharma Gmbh & Co, Kg | Regulatory elements |
| US8865881B2 (en) * | 2011-02-22 | 2014-10-21 | California Institute Of Technology | Delivery of proteins using adeno-associated virus (AAV) vectors |
| RU2014100160A (ru) * | 2011-06-10 | 2015-07-20 | Блуберд Байо, Инк. | Векторы генной терапии адренолейкодистрофии и адреномиелонейропатии |
| US9163259B2 (en) * | 2012-05-04 | 2015-10-20 | Novartis Ag | Viral vectors for the treatment of retinal dystrophy |
| EP2940131B1 (en) * | 2012-12-25 | 2019-02-20 | Takara Bio Inc. | Aav variant |
| WO2015153889A2 (en) * | 2014-04-02 | 2015-10-08 | University Of Florida Research Foundation, Incorporated | Materials and methods for the treatment of latent viral infection |
| JP2018510160A (ja) * | 2015-03-20 | 2018-04-12 | ブルーバード バイオ， インコーポレイテッド | ベクター製剤 |
| CA3019315A1 (en) * | 2015-04-23 | 2016-10-27 | University Of Massachusetts | Modulation of aav vector transgene expression |
| MX2018005689A (es) | 2015-11-05 | 2018-08-01 | Massachusetts Gen Hospital | Administracion intratecal de secuencias de acido nucleico que codifican abcd1 para el tratamiento de la adrenomieloneuropatia. |
| PL3411484T3 (pl) * | 2016-02-05 | 2024-02-19 | Emory University | Wstrzykiwanie jednoniciowego lub samokomplementarnego wirusa adenosatelitarnego 9 do płynu mózgowego |
| EP3413925A1 (en) * | 2016-02-12 | 2018-12-19 | Combigene AB | Vector |
| CN107287239B (zh) * | 2016-04-11 | 2020-09-22 | 厦门继景生物技术有限责任公司 | 一种用于视网膜色素变性的基因治疗载体及药物 |
| CN109843306A (zh) * | 2016-08-19 | 2019-06-04 | 卡琳缪恩股份有限公司 | 使用自身互补型重组腺相关病毒治疗病症的方法和组合物 |
| WO2018136434A1 (en) * | 2017-01-17 | 2018-07-26 | Children's Medical Center Corporation | Compositions and methods for diagnosing and treating peroxisomal diseases |
| EP3592137B1 (en) * | 2017-03-10 | 2024-08-07 | The Medical College of Wisconsin, Inc. | Riboswitch modulated gene therapy for retinal diseases |
| WO2019060649A1 (en) * | 2017-09-22 | 2019-03-28 | Voyager Therapeutics, Inc. | COMPOSITIONS AND METHODS FOR TREATING HUNTINGTON'S DISEASE |
| MX2020004092A (es) * | 2017-10-18 | 2021-01-08 | Composiciones de virus adenoasociados para restaurar la funcion del gen hbb y metodos de uso de estas. | |
| GB201817470D0 (en) * | 2018-10-26 | 2018-12-12 | Univ Oxford Innovation Ltd | Gene therapy |
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2020
- 2020-12-31 EP EP20909162.8A patent/EP4085143B1/en active Active
- 2020-12-31 BR BR112022013027A patent/BR112022013027A2/pt unknown
- 2020-12-31 AU AU2020416291A patent/AU2020416291A1/en active Pending
- 2020-12-31 WO PCT/US2020/067664 patent/WO2021138559A1/en not_active Ceased
- 2020-12-31 CA CA3166374A patent/CA3166374A1/en active Pending
- 2020-12-31 MX MX2022008201A patent/MX2022008201A/es unknown
- 2020-12-31 IL IL294278A patent/IL294278A/en unknown
- 2020-12-31 JP JP2022540917A patent/JP2023509443A/ja active Pending
- 2020-12-31 CN CN202080097613.5A patent/CN116096904A/zh active Pending
- 2020-12-31 KR KR1020227026264A patent/KR20220128632A/ko not_active Ceased
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2021
- 2021-12-21 US US17/557,409 patent/US11779655B2/en active Active
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2023
- 2023-08-30 US US18/458,665 patent/US20240009326A1/en active Pending