JP2025503910A5 - - Google Patents

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Publication number
JP2025503910A5
JP2025503910A5 JP2024543337A JP2024543337A JP2025503910A5 JP 2025503910 A5 JP2025503910 A5 JP 2025503910A5 JP 2024543337 A JP2024543337 A JP 2024543337A JP 2024543337 A JP2024543337 A JP 2024543337A JP 2025503910 A5 JP2025503910 A5 JP 2025503910A5
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JP
Japan
Prior art keywords
composition
disease
combination according
disorder
cns
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024543337A
Other languages
English (en)
Japanese (ja)
Other versions
JP2025503910A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2023/011746 external-priority patent/WO2023147058A2/en
Publication of JP2025503910A publication Critical patent/JP2025503910A/ja
Publication of JP2025503910A5 publication Critical patent/JP2025503910A5/ja
Pending legal-status Critical Current

Links

JP2024543337A 2022-01-27 2023-01-27 神経疾患を処置するための組成物 Pending JP2025503910A (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US202263303673P 2022-01-27 2022-01-27
US63/303,673 2022-01-27
US202263321335P 2022-03-18 2022-03-18
US63/321,335 2022-03-18
PCT/US2023/011746 WO2023147058A2 (en) 2022-01-27 2023-01-27 Compositions for treating neurological disease

Publications (2)

Publication Number Publication Date
JP2025503910A JP2025503910A (ja) 2025-02-06
JP2025503910A5 true JP2025503910A5 (https=) 2026-01-19

Family

ID=87472585

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024543337A Pending JP2025503910A (ja) 2022-01-27 2023-01-27 神経疾患を処置するための組成物

Country Status (7)

Country Link
US (1) US20250109398A1 (https=)
EP (1) EP4469156A4 (https=)
JP (1) JP2025503910A (https=)
CN (1) CN119677545A (https=)
AU (1) AU2023211606A1 (https=)
CA (1) CA3248890A1 (https=)
WO (1) WO2023147058A2 (https=)

Families Citing this family (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CN118599984B (zh) * 2024-04-22 2025-12-09 暨南大学附属第一医院(广州华侨医院) Chchd2在制备促进神经干细胞增殖与分化产品中的应用

Family Cites Families (10)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
HRP20190992T1 (hr) * 2014-12-24 2019-09-20 Uniqure Ip B.V. Suprimiranje gena za huntingtin inducirano s rnai
JP2018500037A (ja) * 2014-12-31 2018-01-11 シンセティック ジェノミクス インコーポレーテッド 高効率なインビボゲノム編集のための組成物及び方法
KR102427379B1 (ko) * 2016-05-18 2022-08-02 보이저 테라퓨틱스, 인크. 헌팅톤 질환을 치료하기 위한 조성물 및 방법
US10457940B2 (en) * 2016-09-22 2019-10-29 University Of Massachusetts AAV treatment of Huntington's disease
SG11202000840YA (en) * 2017-07-31 2020-02-27 Reflection Biotechnologies Ltd Cellular models of and therapies for ocular diseases
US11364309B2 (en) * 2017-11-10 2022-06-21 Norwegian University Of Science And Technology (Ntnu) Neuronal enhancers
AU2019382824A1 (en) * 2018-11-19 2021-06-03 Uniqure Ip B.V. Method and means to deliver miRNA to target cells
CN115443339A (zh) * 2019-12-20 2022-12-06 阿斯克肋匹奥生物制药公司 用于治疗亨廷顿病的方法
GB202005732D0 (en) * 2020-04-20 2020-06-03 Synpromics Ltd Regulatory nucleic acid sequences
EP4213891A4 (en) * 2020-09-21 2025-07-23 Askbio Inc METHODS OF TREATING NEUROLOGICAL DISEASE

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