JP2023507741A5 - - Google Patents

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Publication number
JP2023507741A5
JP2023507741A5 JP2022537012A JP2022537012A JP2023507741A5 JP 2023507741 A5 JP2023507741 A5 JP 2023507741A5 JP 2022537012 A JP2022537012 A JP 2022537012A JP 2022537012 A JP2022537012 A JP 2022537012A JP 2023507741 A5 JP2023507741 A5 JP 2023507741A5
Authority
JP
Japan
Prior art keywords
nucleic acid
isolated nucleic
acid according
composition
sequence
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Granted
Application number
JP2022537012A
Other languages
English (en)
Japanese (ja)
Other versions
JP7730327B2 (ja
JP2023507741A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2020/066039 external-priority patent/WO2021127455A1/en
Publication of JP2023507741A publication Critical patent/JP2023507741A/ja
Publication of JP2023507741A5 publication Critical patent/JP2023507741A5/ja
Priority to JP2025135462A priority Critical patent/JP2025166191A/ja
Application granted granted Critical
Publication of JP7730327B2 publication Critical patent/JP7730327B2/ja
Active legal-status Critical Current
Anticipated expiration legal-status Critical

Links

JP2022537012A 2019-12-20 2020-12-18 ハンチントン病を処置するための方法 Active JP7730327B2 (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2025135462A JP2025166191A (ja) 2019-12-20 2025-08-15 ハンチントン病を処置するための方法

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201962951582P 2019-12-20 2019-12-20
US62/951,582 2019-12-20
PCT/US2020/066039 WO2021127455A1 (en) 2019-12-20 2020-12-18 Methods for treating huntington's disease

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2025135462A Division JP2025166191A (ja) 2019-12-20 2025-08-15 ハンチントン病を処置するための方法

Publications (3)

Publication Number Publication Date
JP2023507741A JP2023507741A (ja) 2023-02-27
JP2023507741A5 true JP2023507741A5 (https=) 2023-12-06
JP7730327B2 JP7730327B2 (ja) 2025-08-27

Family

ID=76478540

Family Applications (2)

Application Number Title Priority Date Filing Date
JP2022537012A Active JP7730327B2 (ja) 2019-12-20 2020-12-18 ハンチントン病を処置するための方法
JP2025135462A Pending JP2025166191A (ja) 2019-12-20 2025-08-15 ハンチントン病を処置するための方法

Family Applications After (1)

Application Number Title Priority Date Filing Date
JP2025135462A Pending JP2025166191A (ja) 2019-12-20 2025-08-15 ハンチントン病を処置するための方法

Country Status (7)

Country Link
US (1) US20230340470A1 (https=)
EP (1) EP4076656A4 (https=)
JP (2) JP7730327B2 (https=)
CN (1) CN115443339A (https=)
AU (1) AU2020407119A1 (https=)
CA (1) CA3163034A1 (https=)
WO (1) WO2021127455A1 (https=)

Families Citing this family (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
JP2025503910A (ja) * 2022-01-27 2025-02-06 アスクレピオス バイオファーマシューティカル, インコーポレイテッド 神経疾患を処置するための組成物

Family Cites Families (11)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US20030190746A1 (en) * 2002-04-04 2003-10-09 Xiao Xiao Gene expression control system and its use in recombinant virus packaging cell lines
US8795987B2 (en) * 2005-02-11 2014-08-05 International Business Machines Corporation Ribonucleic acid interference molecules of Oryza sativa
JP5111385B2 (ja) * 2005-10-28 2013-01-09 アルナイラム ファーマシューティカルズ, インコーポレイテッド ハンチンチン遺伝子の発現を抑制するための組成物および方法
EP1991677A2 (en) * 2006-01-26 2008-11-19 Isis Pharmaceuticals, Inc. Compositions and their uses directed to huntingtin
US9920317B2 (en) * 2010-11-12 2018-03-20 The General Hospital Corporation Polycomb-associated non-coding RNAs
WO2015070212A1 (en) * 2013-11-11 2015-05-14 Sangamo Biosciences, Inc. Methods and compositions for treating huntington's disease
WO2015171932A1 (en) * 2014-05-08 2015-11-12 Sangamo Biosciences, Inc. Methods and compositions for treating huntington's disease
AU2015274457A1 (en) * 2014-06-11 2017-01-05 Circuit Therapeutics, Inc. Optogenetic therapies for movement disorders
US10457940B2 (en) * 2016-09-22 2019-10-29 University Of Massachusetts AAV treatment of Huntington's disease
WO2019217483A1 (en) * 2018-05-07 2019-11-14 Spark Therapeutics, Inc. Plasmid free aav vector producing cell lines
EP4022057A1 (en) 2019-08-27 2022-07-06 Vertex Pharmaceuticals Incorporated Compositions and methods for treatment of disorders associated with repetitive dna

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