JP2021531752A5 - - Google Patents

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Publication number
JP2021531752A5
JP2021531752A5 JP2021500664A JP2021500664A JP2021531752A5 JP 2021531752 A5 JP2021531752 A5 JP 2021531752A5 JP 2021500664 A JP2021500664 A JP 2021500664A JP 2021500664 A JP2021500664 A JP 2021500664A JP 2021531752 A5 JP2021531752 A5 JP 2021531752A5
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JP
Japan
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identity
sequence
seq
lamp
expression
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JP2021500664A
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English (en)
Japanese (ja)
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JPWO2020014523A5 (https=
JP7586810B2 (ja
JP2021531752A (ja
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Priority claimed from PCT/US2019/041465 external-priority patent/WO2020014523A1/en
Publication of JP2021531752A publication Critical patent/JP2021531752A/ja
Publication of JPWO2020014523A5 publication Critical patent/JPWO2020014523A5/ja
Publication of JP2021531752A5 publication Critical patent/JP2021531752A5/ja
Priority to JP2024114749A priority Critical patent/JP2024150588A/ja
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Publication of JP7586810B2 publication Critical patent/JP7586810B2/ja
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JP2021500664A 2018-07-12 2019-07-11 ダノン病治療用遺伝子療法ベクター Active JP7586810B2 (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2024114749A JP2024150588A (ja) 2018-07-12 2024-07-18 ダノン病治療用遺伝子療法ベクター

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201862697302P 2018-07-12 2018-07-12
US62/697,302 2018-07-12
PCT/US2019/041465 WO2020014523A1 (en) 2018-07-12 2019-07-11 Gene therapy vectors for treatment of danon disease

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2024114749A Division JP2024150588A (ja) 2018-07-12 2024-07-18 ダノン病治療用遺伝子療法ベクター

Publications (4)

Publication Number Publication Date
JP2021531752A JP2021531752A (ja) 2021-11-25
JPWO2020014523A5 JPWO2020014523A5 (https=) 2022-07-14
JP2021531752A5 true JP2021531752A5 (https=) 2022-07-14
JP7586810B2 JP7586810B2 (ja) 2024-11-19

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ID=69141704

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JP2021500664A Active JP7586810B2 (ja) 2018-07-12 2019-07-11 ダノン病治療用遺伝子療法ベクター
JP2024114749A Pending JP2024150588A (ja) 2018-07-12 2024-07-18 ダノン病治療用遺伝子療法ベクター

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JP2024114749A Pending JP2024150588A (ja) 2018-07-12 2024-07-18 ダノン病治療用遺伝子療法ベクター

Country Status (12)

Country Link
US (2) US10703797B2 (https=)
EP (1) EP3820537A4 (https=)
JP (2) JP7586810B2 (https=)
KR (1) KR102918544B1 (https=)
CN (1) CN112512596B (https=)
AU (1) AU2019299970B2 (https=)
BR (1) BR112021000509A2 (https=)
CA (1) CA3106010A1 (https=)
IL (1) IL279918A (https=)
MX (1) MX2021000443A (https=)
SG (1) SG11202100022SA (https=)
WO (1) WO2020014523A1 (https=)

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