JP2022514271A5 - - Google Patents
Info
- Publication number
- JP2022514271A5 JP2022514271A5 JP2021534702A JP2021534702A JP2022514271A5 JP 2022514271 A5 JP2022514271 A5 JP 2022514271A5 JP 2021534702 A JP2021534702 A JP 2021534702A JP 2021534702 A JP2021534702 A JP 2021534702A JP 2022514271 A5 JP2022514271 A5 JP 2022514271A5
- Authority
- JP
- Japan
- Prior art keywords
- sequence
- raav
- nucleic acid
- composition according
- acid molecule
- Prior art date
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201862781380P | 2018-12-18 | 2018-12-18 | |
| US62/781,380 | 2018-12-18 | ||
| PCT/US2019/067247 WO2020132115A1 (en) | 2018-12-18 | 2019-12-18 | Methods and compositions for treating glycogen storage diseases |
Publications (4)
| Publication Number | Publication Date |
|---|---|
| JP2022514271A JP2022514271A (ja) | 2022-02-10 |
| JPWO2020132115A5 JPWO2020132115A5 (https=) | 2022-05-20 |
| JP2022514271A5 true JP2022514271A5 (https=) | 2022-05-20 |
| JP7486274B2 JP7486274B2 (ja) | 2024-05-17 |
Family
ID=69400618
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2021534702A Active JP7486274B2 (ja) | 2018-12-18 | 2019-12-18 | 糖原病を処置するための方法および組成物 |
Country Status (15)
| Country | Link |
|---|---|
| US (1) | US20220017922A1 (https=) |
| EP (1) | EP3898981B1 (https=) |
| JP (1) | JP7486274B2 (https=) |
| KR (1) | KR20210105390A (https=) |
| CN (1) | CN113454226B (https=) |
| AU (1) | AU2019405758B2 (https=) |
| BR (1) | BR112021012104A2 (https=) |
| CA (1) | CA3123841A1 (https=) |
| DK (1) | DK3898981T5 (https=) |
| ES (1) | ES2969222T3 (https=) |
| IL (1) | IL283956A (https=) |
| MX (1) | MX2021007379A (https=) |
| PL (1) | PL3898981T3 (https=) |
| PT (1) | PT3898981T (https=) |
| WO (1) | WO2020132115A1 (https=) |
Families Citing this family (1)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US20250222134A1 (en) * | 2021-10-19 | 2025-07-10 | University Of Connecticut | Compositions and methods for the treatment of glycogen storage disorders |
Family Cites Families (11)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US6759050B1 (en) | 1998-12-03 | 2004-07-06 | Avigen, Inc. | Excipients for use in adeno-associated virus pharmaceutical formulations, and pharmaceutical formulations made therewith |
| JP2002191363A (ja) * | 1999-07-29 | 2002-07-09 | Herikkusu Kenkyusho:Kk | 全長ｃＤＮＡ合成用プライマー、およびその用途 |
| DE602004030327D1 (de) | 2003-05-21 | 2011-01-13 | Genzyme Corp | Verfahren zur herstellung von präparationen rekombinanter aav-virionen, die weitgehend frei von leeren capsiden sind |
| DK2242840T3 (da) | 2008-01-29 | 2019-10-21 | Applied Genetic Tech Corporation | Produktion af rekombinant adeno-associeret virus under anvendelse af bhk-celler i suspension |
| US8679837B2 (en) | 2009-04-02 | 2014-03-25 | University Of Florida Research Foundation, Inc. | Inducible system for highly efficient production of recombinant Adeno-associated virus (rAAV) vectors |
| DK2529020T3 (en) | 2010-01-28 | 2018-08-06 | Childrens Hospital Philadelphia | SCALABLE PREPARATION PLATF FOR CLEANING VIRAL VECTORS AND CLEANED VIRAL VECTORS FOR USE IN GENTHERAPY |
| AU2014216160B2 (en) | 2013-02-15 | 2017-03-30 | The United States Of America, As Represented By The Secretary, Department Of Health And Human Services | AAV8 retinoschisin expression vector for treating X-linked retinoschisis |
| WO2015081101A1 (en) * | 2013-11-26 | 2015-06-04 | The United States Of America, As Represented By The Secretary Department Of Health And Human Services | Adeno-associated virus vectors for treatment of glycogen storage disease |
| JP6824169B2 (ja) | 2014-12-23 | 2021-02-03 | ザ ユナイテッド ステイツ オブ アメリカ， アズ リプレゼンテッド バイ ザ セクレタリー， デパートメント オブ ヘルス アンド ヒューマン サービシーズ | 改変ｇ６ｐｃをコードするアデノ随伴ウイルスベクターおよびその使用 |
| PL3436593T3 (pl) | 2016-03-28 | 2023-03-27 | Ultragenyx Pharmaceutical Inc. | Sposoby inaktywacji termicznej adenowirusów |
| AU2018212002A1 (en) * | 2017-01-30 | 2019-08-29 | The United States Of America, As Represented By The Secretary, Department Of Health And Human Services | Recombinant virus vectors for the treatment of glycogen storage disease |
-
2019
- 2019-12-18 ES ES19845789T patent/ES2969222T3/es active Active
- 2019-12-18 MX MX2021007379A patent/MX2021007379A/es unknown
- 2019-12-18 PL PL19845789.7T patent/PL3898981T3/pl unknown
- 2019-12-18 KR KR1020217022096A patent/KR20210105390A/ko active Pending
- 2019-12-18 PT PT198457897T patent/PT3898981T/pt unknown
- 2019-12-18 JP JP2021534702A patent/JP7486274B2/ja active Active
- 2019-12-18 DK DK19845789.7T patent/DK3898981T5/da active
- 2019-12-18 US US17/311,869 patent/US20220017922A1/en active Pending
- 2019-12-18 EP EP19845789.7A patent/EP3898981B1/en active Active
- 2019-12-18 AU AU2019405758A patent/AU2019405758B2/en active Active
- 2019-12-18 CN CN201980083410.8A patent/CN113454226B/zh active Active
- 2019-12-18 BR BR112021012104-8A patent/BR112021012104A2/pt unknown
- 2019-12-18 WO PCT/US2019/067247 patent/WO2020132115A1/en not_active Ceased
- 2019-12-18 CA CA3123841A patent/CA3123841A1/en active Pending
-
2021
- 2021-06-13 IL IL283956A patent/IL283956A/en unknown
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