JP2025504478A5 - - Google Patents
Info
- Publication number
- JP2025504478A5 JP2025504478A5 JP2024543149A JP2024543149A JP2025504478A5 JP 2025504478 A5 JP2025504478 A5 JP 2025504478A5 JP 2024543149 A JP2024543149 A JP 2024543149A JP 2024543149 A JP2024543149 A JP 2024543149A JP 2025504478 A5 JP2025504478 A5 JP 2025504478A5
- Authority
- JP
- Japan
- Prior art keywords
- aav
- sequence
- aav vector
- vector genome
- nucleotide sequence
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (5)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202263267046P | 2022-01-21 | 2022-01-21 | |
| US63/267,046 | 2022-01-21 | ||
| US202263382502P | 2022-11-05 | 2022-11-05 | |
| US63/382,502 | 2022-11-05 | ||
| PCT/IB2023/050426 WO2023139496A1 (en) | 2022-01-21 | 2023-01-18 | Gene therapy for gaucher disease |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2025504478A JP2025504478A (ja) | 2025-02-12 |
| JP2025504478A5 true JP2025504478A5 (https=) | 2026-01-26 |
Family
ID=85122738
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024543149A Pending JP2025504478A (ja) | 2022-01-21 | 2023-01-18 | ゴーシェ病の遺伝子療法 |
Country Status (11)
| Country | Link |
|---|---|
| US (1) | US20250257367A1 (https=) |
| EP (1) | EP4465998A1 (https=) |
| JP (1) | JP2025504478A (https=) |
| KR (1) | KR20240134991A (https=) |
| AU (1) | AU2023208274A1 (https=) |
| CA (1) | CA3248631A1 (https=) |
| CO (1) | CO2024011137A2 (https=) |
| IL (1) | IL314294A (https=) |
| MX (1) | MX2024009003A (https=) |
| TW (1) | TWI874898B (https=) |
| WO (1) | WO2023139496A1 (https=) |
Families Citing this family (1)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US20250152747A1 (en) * | 2023-11-15 | 2025-05-15 | Genzyme Corporation | Methods of treating gaucher disease and gba-parkinson’s disease |
Family Cites Families (8)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| ATE318923T1 (de) | 2000-06-01 | 2006-03-15 | Univ North Carolina | Doppelsträngige parvovirus-vektoren |
| IL297919A (en) | 2013-07-22 | 2023-01-01 | Childrens Hospital Philadelphia | Variant aav and compositions, methods and uses for gene transfer to cells, organs and tissues |
| AU2018346104B2 (en) * | 2017-10-03 | 2023-07-27 | Prevail Therapeutics, Inc. | Gene therapies for lysosomal disorders |
| TW202005978A (zh) * | 2018-05-14 | 2020-02-01 | 美商拜奧馬林製藥公司 | 新穎肝靶向腺相關病毒載體 |
| WO2020012149A1 (en) * | 2018-07-13 | 2020-01-16 | Ucl Business Ltd | Glucocerebrosidase gene therapy |
| JP7664848B2 (ja) * | 2019-04-10 | 2025-04-18 | プリベイル セラピューティクス，インコーポレーテッド | リソソーム障害のための遺伝子療法 |
| KR20220098384A (ko) * | 2019-11-19 | 2022-07-12 | 아스클레피오스 바이오파마슈티컬, 인크. | 폼페병 및 리소좀 장애를 치료하기 위한 간-특이적 프로모터를 포함하는 치료적 아데노-관련 바이러스 |
| JP2023520763A (ja) * | 2020-03-24 | 2023-05-19 | ジェネレーション バイオ カンパニー | ゴーシェ治療薬を発現するための非ウイルス性ｄｎａベクター及びその使用 |
-
2023
- 2023-01-18 WO PCT/IB2023/050426 patent/WO2023139496A1/en not_active Ceased
- 2023-01-18 CA CA3248631A patent/CA3248631A1/en active Pending
- 2023-01-18 JP JP2024543149A patent/JP2025504478A/ja active Pending
- 2023-01-18 MX MX2024009003A patent/MX2024009003A/es unknown
- 2023-01-18 EP EP23702374.2A patent/EP4465998A1/en active Pending
- 2023-01-18 AU AU2023208274A patent/AU2023208274A1/en active Pending
- 2023-01-18 IL IL314294A patent/IL314294A/en unknown
- 2023-01-18 US US18/729,960 patent/US20250257367A1/en active Pending
- 2023-01-18 KR KR1020247027707A patent/KR20240134991A/ko active Pending
- 2023-01-19 TW TW112102851A patent/TWI874898B/zh active
-
2024
- 2024-08-16 CO CONC2024/0011137A patent/CO2024011137A2/es unknown
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