JP2023545384A5 - - Google Patents

Info

Publication number
JP2023545384A5
JP2023545384A5 JP2023519433A JP2023519433A JP2023545384A5 JP 2023545384 A5 JP2023545384 A5 JP 2023545384A5 JP 2023519433 A JP2023519433 A JP 2023519433A JP 2023519433 A JP2023519433 A JP 2023519433A JP 2023545384 A5 JP2023545384 A5 JP 2023545384A5
Authority
JP
Japan
Prior art keywords
raav vector
capsid protein
capsid
raav
pharmaceutical composition
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2023519433A
Other languages
English (en)
Japanese (ja)
Other versions
JP2023545384A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2021/054058 external-priority patent/WO2022076750A2/en
Publication of JP2023545384A publication Critical patent/JP2023545384A/ja
Publication of JP2023545384A5 publication Critical patent/JP2023545384A5/ja
Pending legal-status Critical Current

Links

JP2023519433A 2020-10-07 2021-10-07 中枢神経系または筋肉送達のための組換えアデノ随伴ウイルス Pending JP2023545384A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202063088988P 2020-10-07 2020-10-07
US63/088,988 2020-10-07
PCT/US2021/054058 WO2022076750A2 (en) 2020-10-07 2021-10-07 Recombinant adeno-associated viruses for cns or muscle delivery

Publications (2)

Publication Number Publication Date
JP2023545384A JP2023545384A (ja) 2023-10-30
JP2023545384A5 true JP2023545384A5 (https=) 2024-10-17

Family

ID=86184347

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023519433A Pending JP2023545384A (ja) 2020-10-07 2021-10-07 中枢神経系または筋肉送達のための組換えアデノ随伴ウイルス

Country Status (9)

Country Link
US (1) US20230374541A1 (https=)
EP (1) EP4225778A2 (https=)
JP (1) JP2023545384A (https=)
KR (1) KR20230082613A (https=)
CN (1) CN116783209A (https=)
AU (1) AU2021358546A1 (https=)
CA (1) CA3193685A1 (https=)
IL (1) IL301563A (https=)
MX (1) MX2023003807A (https=)

Families Citing this family (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US20260055144A1 (en) * 2022-08-24 2026-02-26 Regenxbio Inc. Recombinant adeno-associated viruses and uses thereof

Family Cites Families (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2018119330A2 (en) * 2016-12-22 2018-06-28 Oregon Health & Science University Adeno associated viral vectors
US11905312B2 (en) * 2017-02-15 2024-02-20 The University Of North Carolina At Chapel Hill Methods and compositions for gene transfer across the vasculature
WO2020160508A1 (en) * 2019-01-31 2020-08-06 Oregon Health & Science University Methods for using transcription-dependent directed evolution of aav capsids

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