JP2024513949A5 - - Google Patents
Info
- Publication number
- JP2024513949A5 JP2024513949A5 JP2023562535A JP2023562535A JP2024513949A5 JP 2024513949 A5 JP2024513949 A5 JP 2024513949A5 JP 2023562535 A JP2023562535 A JP 2023562535A JP 2023562535 A JP2023562535 A JP 2023562535A JP 2024513949 A5 JP2024513949 A5 JP 2024513949A5
- Authority
- JP
- Japan
- Prior art keywords
- seq
- sequence
- aav capsid
- capsid protein
- amino acid
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202163174434P | 2021-04-13 | 2021-04-13 | |
| US63/174,434 | 2021-04-13 | ||
| PCT/US2022/024603 WO2022221400A2 (en) | 2021-04-13 | 2022-04-13 | Aav compositions having high expression levels in brain |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2024513949A JP2024513949A (ja) | 2024-03-27 |
| JP2024513949A5 true JP2024513949A5 (https=) | 2025-04-18 |
Family
ID=83641102
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023562535A Pending JP2024513949A (ja) | 2021-04-13 | 2022-04-13 | 脳内発現レベルが高いａａｖ組成物 |
Country Status (8)
| Country | Link |
|---|---|
| US (1) | US20240150410A1 (https=) |
| EP (1) | EP4322976A4 (https=) |
| JP (1) | JP2024513949A (https=) |
| KR (1) | KR20240028976A (https=) |
| CN (1) | CN117440820A (https=) |
| AU (1) | AU2022258447A1 (https=) |
| CA (1) | CA3216172A1 (https=) |
| WO (1) | WO2022221400A2 (https=) |
Families Citing this family (10)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| CN115120746A (zh) | 2013-05-15 | 2022-09-30 | 明尼苏达大学董事会 | 腺相关病毒介导的基因向中枢神经系统转移 |
| CN113166208B (zh) | 2018-10-02 | 2024-11-22 | 沃雅戈治疗公司 | 重新定向aav衣壳的嗜性 |
| TWI900553B (zh) | 2020-05-13 | 2025-10-11 | 美商航海家醫療公司 | Aav蛋白殼之趨性重定向 |
| KR20240095539A (ko) | 2021-10-08 | 2024-06-25 | 디노 테라퓨틱스, 인코포레이티드 | 캡시드 변이체 및 이의 사용 방법 |
| EP4426716A1 (en) | 2021-11-02 | 2024-09-11 | Voyager Therapeutics, Inc. | Aav capsid variants and uses thereof |
| WO2024191778A1 (en) | 2023-03-10 | 2024-09-19 | Dyno Therapeutics, Inc. | Capsid polypeptides and methods of use thereof |
| CN121729237A (zh) | 2023-06-30 | 2026-03-24 | 武田药品工业株式会社 | Htt阻遏物及其用途 |
| AU2024332181A1 (en) | 2023-08-31 | 2026-02-12 | Dyno Therapeutics, Inc. | Capsid polypeptides and methods of use thereof |
| TW202545971A (zh) | 2024-02-08 | 2025-12-01 | 美商戴諾治療公司 | 殼體多肽及其使用方法 |
| WO2026064442A2 (en) | 2024-09-18 | 2026-03-26 | Dyno Therapeutics, Inc. | Capsid polypeptides and methods of use thereof |
Family Cites Families (6)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US20110166335A1 (en) * | 2000-06-30 | 2011-07-07 | Corbin David R | Xenorhabdus sp. genome sequences and uses thereof |
| EP2741772A1 (en) * | 2011-08-08 | 2014-06-18 | ETH Zurich | Pasteurellaceae vaccines |
| CA3053154A1 (en) * | 2017-06-30 | 2019-01-03 | The Regents Of The University Of California | Adeno-associated virus virions with variant capsids and methods of use thereof |
| JP2022526018A (ja) * | 2019-04-11 | 2022-05-20 | カリフォルニア インスティテュート オブ テクノロジー | 脳内への特異性が増強されたウイルス組成物 |
| AU2021329527A1 (en) * | 2020-08-21 | 2023-03-23 | Capsida, Inc. | Adeno-associated virus compositions having preferred expression levels |
| WO2022040530A2 (en) * | 2020-08-21 | 2022-02-24 | Capsida, Inc. | Virus compositions for treating mucopolysaccharidosis ii |
-
2022
- 2022-04-13 JP JP2023562535A patent/JP2024513949A/ja active Pending
- 2022-04-13 WO PCT/US2022/024603 patent/WO2022221400A2/en not_active Ceased
- 2022-04-13 US US18/284,408 patent/US20240150410A1/en active Pending
- 2022-04-13 CN CN202280035270.9A patent/CN117440820A/zh active Pending
- 2022-04-13 EP EP22788850.0A patent/EP4322976A4/en active Pending
- 2022-04-13 KR KR1020237038494A patent/KR20240028976A/ko active Pending
- 2022-04-13 AU AU2022258447A patent/AU2022258447A1/en not_active Abandoned
- 2022-04-13 CA CA3216172A patent/CA3216172A1/en active Pending
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