JP2023500011A5 - - Google Patents
Info
- Publication number
- JP2023500011A5 JP2023500011A5 JP2022507566A JP2022507566A JP2023500011A5 JP 2023500011 A5 JP2023500011 A5 JP 2023500011A5 JP 2022507566 A JP2022507566 A JP 2022507566A JP 2022507566 A JP2022507566 A JP 2022507566A JP 2023500011 A5 JP2023500011 A5 JP 2023500011A5
- Authority
- JP
- Japan
- Prior art keywords
- seq
- aav
- itr
- promoter
- sequence
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Withdrawn
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| EP19382706.0 | 2019-08-12 | ||
| EP19382706 | 2019-08-12 | ||
| PCT/EP2020/072087 WO2021028299A1 (en) | 2019-08-12 | 2020-08-06 | Viral particles for use in treating synucleinopathies such as parkinson's diseases by gene therapy |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2023500011A JP2023500011A (ja) | 2023-01-04 |
| JP2023500011A5 true JP2023500011A5 (https=) | 2023-08-08 |
Family
ID=67659024
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022507566A Withdrawn JP2023500011A (ja) | 2019-08-12 | 2020-08-06 | 遺伝子療法によるパーキンソン病などのシヌクレイノパチーの治療に使用するためのウイルス粒子 |
Country Status (18)
| Country | Link |
|---|---|
| US (1) | US20220298528A1 (https=) |
| EP (1) | EP4013437A1 (https=) |
| JP (1) | JP2023500011A (https=) |
| KR (1) | KR20220099944A (https=) |
| CN (1) | CN114786694A (https=) |
| AR (1) | AR119609A1 (https=) |
| AU (1) | AU2020328827A1 (https=) |
| BR (1) | BR112022002615A2 (https=) |
| CA (1) | CA3149844A1 (https=) |
| CL (1) | CL2022000292A1 (https=) |
| CO (1) | CO2022001192A2 (https=) |
| EC (1) | ECSP22008949A (https=) |
| IL (1) | IL290357A (https=) |
| MX (1) | MX2022001676A (https=) |
| PE (1) | PE20220601A1 (https=) |
| PH (1) | PH12022550282A1 (https=) |
| TW (1) | TW202120687A (https=) |
| WO (1) | WO2021028299A1 (https=) |
Families Citing this family (5)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| KR20210148101A (ko) | 2019-02-04 | 2021-12-07 | 프리라인 테라퓨틱스 리미티드 | 폴리뉴클레오티드 |
| CN116390773A (zh) * | 2020-08-06 | 2023-07-04 | 应用医学研究基金会 | 用于通过基因疗法治疗诸如阿尔茨海默病的Tau蛋白病的病毒颗粒 |
| EP4511482A4 (en) * | 2022-04-19 | 2026-03-18 | Shanghai Vitalgen Biopharma Co Ltd | Recombinant AAV vectors for the treatment of neurodegenerative disorders |
| CN118715316B (zh) * | 2022-10-08 | 2025-09-19 | 凌意(杭州)生物科技有限公司 | 用于治疗GCase缺乏相关疾病的多核苷酸 |
| WO2025063407A1 (ko) * | 2023-09-22 | 2025-03-27 | 주식회사 스탠드업테라퓨티스 | 신규한 파킨슨 병 치료제 |
Family Cites Families (3)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| CA2985235A1 (en) * | 2015-05-07 | 2016-11-10 | Shire Human Genetic Therapies, Inc. | Glucocerebrosidase gene therapy for parkinson's disease |
| AU2018346104B2 (en) * | 2017-10-03 | 2023-07-27 | Prevail Therapeutics, Inc. | Gene therapies for lysosomal disorders |
| WO2019068854A1 (en) * | 2017-10-06 | 2019-04-11 | Ospedale San Raffaele S.R.L. | GENE THERAPY OF NEURODEGENERATIVE DISEASES USING VAA VECTORS |
-
2020
- 2020-08-06 US US17/634,112 patent/US20220298528A1/en not_active Abandoned
- 2020-08-06 PH PH1/2022/550282A patent/PH12022550282A1/en unknown
- 2020-08-06 AR ARP200102236A patent/AR119609A1/es not_active Application Discontinuation
- 2020-08-06 KR KR1020227003990A patent/KR20220099944A/ko active Pending
- 2020-08-06 CA CA3149844A patent/CA3149844A1/en active Pending
- 2020-08-06 AU AU2020328827A patent/AU2020328827A1/en not_active Abandoned
- 2020-08-06 WO PCT/EP2020/072087 patent/WO2021028299A1/en not_active Ceased
- 2020-08-06 BR BR112022002615A patent/BR112022002615A2/pt not_active IP Right Cessation
- 2020-08-06 JP JP2022507566A patent/JP2023500011A/ja not_active Withdrawn
- 2020-08-06 PE PE2022000219A patent/PE20220601A1/es unknown
- 2020-08-06 EP EP20750277.4A patent/EP4013437A1/en not_active Withdrawn
- 2020-08-06 TW TW109126665A patent/TW202120687A/zh unknown
- 2020-08-06 CN CN202080064577.2A patent/CN114786694A/zh active Pending
- 2020-08-06 MX MX2022001676A patent/MX2022001676A/es unknown
-
2022
- 2022-02-04 CO CONC2022/0001192A patent/CO2022001192A2/es unknown
- 2022-02-04 EC ECSENADI20228949A patent/ECSP22008949A/es unknown
- 2022-02-04 CL CL2022000292A patent/CL2022000292A1/es unknown
- 2022-02-06 IL IL290357A patent/IL290357A/en unknown
Similar Documents
| Publication | Publication Date | Title |
|---|---|---|
| JP2023500011A5 (https=) | ||
| JP7497247B2 (ja) | 組換えアデノ随伴ウイルス９の髄腔内送達 | |
| Tal | Adeno-associated virus-based vectors in gene therapy | |
| CN113301956B (zh) | 控制器官功能的基因治疗方法 | |
| JP2024513949A5 (https=) | ||
| TW201629225A (zh) | 第九因子基因療法 | |
| EP2391388A1 (en) | Methods for distributing high levels of therapeutic agent throughout the cortex to treat neurological disorders | |
| JP2024543211A5 (https=) | ||
| CN119487053A (zh) | 具有优选脑、脊髓和/或心脏表达水平的选定腺相关病毒组合物 | |
| CN112029773B (zh) | 编码bdnf的核酸及其应用 | |
| JP2020510433A5 (https=) | ||
| CN114126667A (zh) | 使用糖苷水解酶的基因疗法载体向视网膜细胞的改进递送 | |
| TW202317769A (zh) | 來自腺相關病毒血清型９（ａａｖ９）的分離的修飾衣殼蛋白ｖｐ１、基於其的衣殼和載體 | |
| RU2022102652A (ru) | Вирусные частицы для применения в лечении синуклеинопатий, таких как болезнь паркинсона, методами генной терапии | |
| Yang et al. | 526. Intravasuclar Delivery of RAAVRH. 8 Generates Widespreading Transduction of Neuronal and Glial Cell Types in the Adult Mouse Central Nervous System | |
| AU2024298945A1 (en) | Brain-tropic aav mutant | |
| KR20250097939A (ko) | 투여 경로 | |
| EA048714B1 (ru) | Выделенный модифицированный белок vp1 капсида аденоассоциированного вируса 9 серотипа (aav9), капсид и вектор на его основе | |
| CN119894920A (zh) | 用于靶向神经系统的新型aav衣壳及其用途 | |
| HK40004543B (en) | Intrathecal delivery of recombinant adeno-associated virus 9 | |
| HK40004543A (en) | Intrathecal delivery of recombinant adeno-associated virus 9 | |
| HK40042522A (en) | Intrathecal delivery of recombinant adeno-associated virus 9 |