TW202120687A - 用於藉由基因療法治療諸如帕金森氏症之突觸核蛋白病變的病毒顆粒 - Google Patents
用於藉由基因療法治療諸如帕金森氏症之突觸核蛋白病變的病毒顆粒 Download PDFInfo
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| EP4192961A2 (en) * | 2020-08-06 | 2023-06-14 | Fundacion para la Investigacion Medica Aplicada | Viral particles for use in treating tauopathies such as alzheimer's diseases by gene therapy |
| WO2023202637A1 (en) * | 2022-04-19 | 2023-10-26 | Shanghai Vitalgen Biopharma Co., Ltd. | Recombinant aav vectors for treating neurodegenerative disorders |
| WO2024074142A1 (en) * | 2022-10-08 | 2024-04-11 | Lingyi Biotech Co., Ltd. | Polynucleotides for the treatment of disease associated with gcase deficiency |
| WO2025063407A1 (ko) * | 2023-09-22 | 2025-03-27 | 주식회사 스탠드업테라퓨티스 | 신규한 파킨슨 병 치료제 |
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| EP3692075A4 (en) * | 2017-10-03 | 2022-02-09 | Prevail Therapeutics, Inc. | GENE THERAPIES FOR LYSOSOMAL DISEASES |
| WO2019068854A1 (en) * | 2017-10-06 | 2019-04-11 | Ospedale San Raffaele S.R.L. | GENE THERAPY OF NEURODEGENERATIVE DISEASES USING VAA VECTORS |
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| IL290357A (en) | 2022-04-01 |
| KR20220099944A (ko) | 2022-07-14 |
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