JP2023500011A - 遺伝子療法によるパーキンソン病などのシヌクレイノパチーの治療に使用するためのウイルス粒子 - Google Patents
遺伝子療法によるパーキンソン病などのシヌクレイノパチーの治療に使用するためのウイルス粒子 Download PDFInfo
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| EP19382706 | 2019-08-12 | ||
| PCT/EP2020/072087 WO2021028299A1 (en) | 2019-08-12 | 2020-08-06 | Viral particles for use in treating synucleinopathies such as parkinson's diseases by gene therapy |
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| JP2023500011A true JP2023500011A (ja) | 2023-01-04 |
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| EP4192961A2 (en) * | 2020-08-06 | 2023-06-14 | Fundacion para la Investigacion Medica Aplicada | Viral particles for use in treating tauopathies such as alzheimer's diseases by gene therapy |
| WO2023202637A1 (en) * | 2022-04-19 | 2023-10-26 | Shanghai Vitalgen Biopharma Co., Ltd. | Recombinant aav vectors for treating neurodegenerative disorders |
| WO2024074142A1 (en) * | 2022-10-08 | 2024-04-11 | Lingyi Biotech Co., Ltd. | Polynucleotides for the treatment of disease associated with gcase deficiency |
| WO2025063407A1 (ko) * | 2023-09-22 | 2025-03-27 | 주식회사 스탠드업테라퓨티스 | 신규한 파킨슨 병 치료제 |
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| EP3692075A4 (en) * | 2017-10-03 | 2022-02-09 | Prevail Therapeutics, Inc. | GENE THERAPIES FOR LYSOSOMAL DISEASES |
| WO2019068854A1 (en) * | 2017-10-06 | 2019-04-11 | Ospedale San Raffaele S.R.L. | GENE THERAPY OF NEURODEGENERATIVE DISEASES USING VAA VECTORS |
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