KR20220099944A - 유전자 요법으로 파킨슨병과 같은 시누클레인병증을 치료하는 데 사용하기 위한 바이러스 입자 - Google Patents

유전자 요법으로 파킨슨병과 같은 시누클레인병증을 치료하는 데 사용하기 위한 바이러스 입자 Download PDF

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KR20220099944A
KR20220099944A KR1020227003990A KR20227003990A KR20220099944A KR 20220099944 A KR20220099944 A KR 20220099944A KR 1020227003990 A KR1020227003990 A KR 1020227003990A KR 20227003990 A KR20227003990 A KR 20227003990A KR 20220099944 A KR20220099944 A KR 20220099944A
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아세귀놀라자 글로리아 곤잘레즈
페레즈 호세 루이스 란시에고
랄프 미카엘 린덴
Original Assignee
푼다시온 파라 라 인베스티가시온 메디카 아플리카다
콘소르시오 센트로 데 인베스티카시온 비오메디카 엔 레드
유씨비 바이오파마 에스알엘
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First worldwide family litigation filed litigation Critical https://patents.darts-ip.com/?family=67659024&utm_source=google_patent&utm_medium=platform_link&utm_campaign=public_patent_search&patent=KR20220099944(A) "Global patent litigation dataset” by Darts-ip is licensed under a Creative Commons Attribution 4.0 International License.
Application filed by 푼다시온 파라 라 인베스티가시온 메디카 아플리카다, 콘소르시오 센트로 데 인베스티카시온 비오메디카 엔 레드, 유씨비 바이오파마 에스알엘 filed Critical 푼다시온 파라 라 인베스티가시온 메디카 아플리카다
Publication of KR20220099944A publication Critical patent/KR20220099944A/ko
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KR1020227003990A 2019-08-12 2020-08-06 유전자 요법으로 파킨슨병과 같은 시누클레인병증을 치료하는 데 사용하기 위한 바이러스 입자 Pending KR20220099944A (ko)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
EP19382706.0 2019-08-12
EP19382706 2019-08-12
PCT/EP2020/072087 WO2021028299A1 (en) 2019-08-12 2020-08-06 Viral particles for use in treating synucleinopathies such as parkinson's diseases by gene therapy

Publications (1)

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KR20220099944A true KR20220099944A (ko) 2022-07-14

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KR1020227003990A Pending KR20220099944A (ko) 2019-08-12 2020-08-06 유전자 요법으로 파킨슨병과 같은 시누클레인병증을 치료하는 데 사용하기 위한 바이러스 입자

Country Status (18)

Country Link
US (1) US20220298528A1 (https=)
EP (1) EP4013437A1 (https=)
JP (1) JP2023500011A (https=)
KR (1) KR20220099944A (https=)
CN (1) CN114786694A (https=)
AR (1) AR119609A1 (https=)
AU (1) AU2020328827A1 (https=)
BR (1) BR112022002615A2 (https=)
CA (1) CA3149844A1 (https=)
CL (1) CL2022000292A1 (https=)
CO (1) CO2022001192A2 (https=)
EC (1) ECSP22008949A (https=)
IL (1) IL290357A (https=)
MX (1) MX2022001676A (https=)
PE (1) PE20220601A1 (https=)
PH (1) PH12022550282A1 (https=)
TW (1) TW202120687A (https=)
WO (1) WO2021028299A1 (https=)

Cited By (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2025063407A1 (ko) * 2023-09-22 2025-03-27 주식회사 스탠드업테라퓨티스 신규한 파킨슨 병 치료제

Families Citing this family (4)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
BR112021015312A2 (pt) 2019-02-04 2021-11-09 Freeline Therapeutics Ltd Polinucleotídeos, partícula viral e composição
EP4192961A2 (en) * 2020-08-06 2023-06-14 Fundacion para la Investigacion Medica Aplicada Viral particles for use in treating tauopathies such as alzheimer's diseases by gene therapy
WO2023202637A1 (en) * 2022-04-19 2023-10-26 Shanghai Vitalgen Biopharma Co., Ltd. Recombinant aav vectors for treating neurodegenerative disorders
WO2024074142A1 (en) * 2022-10-08 2024-04-11 Lingyi Biotech Co., Ltd. Polynucleotides for the treatment of disease associated with gcase deficiency

Family Cites Families (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP3292206B8 (en) * 2015-05-07 2022-02-09 Takeda Pharmaceutical Company Limited Glucocerebrosidase gene therapy for parkinson's disease
EP3692075A4 (en) * 2017-10-03 2022-02-09 Prevail Therapeutics, Inc. GENE THERAPIES FOR LYSOSOMAL DISEASES
WO2019068854A1 (en) * 2017-10-06 2019-04-11 Ospedale San Raffaele S.R.L. GENE THERAPY OF NEURODEGENERATIVE DISEASES USING VAA VECTORS

Cited By (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2025063407A1 (ko) * 2023-09-22 2025-03-27 주식회사 스탠드업테라퓨티스 신규한 파킨슨 병 치료제

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CN114786694A (zh) 2022-07-22
PE20220601A1 (es) 2022-04-25
AR119609A1 (es) 2021-12-29
ECSP22008949A (es) 2022-03-31
PH12022550282A1 (en) 2022-11-21
EP4013437A1 (en) 2022-06-22
TW202120687A (zh) 2021-06-01
BR112022002615A2 (pt) 2022-05-03
JP2023500011A (ja) 2023-01-04
AU2020328827A1 (en) 2022-03-03
CL2022000292A1 (es) 2022-10-21
CO2022001192A2 (es) 2022-07-19
WO2021028299A1 (en) 2021-02-18
MX2022001676A (es) 2022-05-03
CA3149844A1 (en) 2021-02-18
US20220298528A1 (en) 2022-09-22
IL290357A (en) 2022-04-01

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