JP2024543211A5 - - Google Patents

Info

Publication number
JP2024543211A5
JP2024543211A5 JP2024532790A JP2024532790A JP2024543211A5 JP 2024543211 A5 JP2024543211 A5 JP 2024543211A5 JP 2024532790 A JP2024532790 A JP 2024532790A JP 2024532790 A JP2024532790 A JP 2024532790A JP 2024543211 A5 JP2024543211 A5 JP 2024543211A5
Authority
JP
Japan
Prior art keywords
raav
sequence
seq
item
capsid
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024532790A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024543211A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/051452 external-priority patent/WO2023102079A1/en
Publication of JP2024543211A publication Critical patent/JP2024543211A/ja
Publication of JP2024543211A5 publication Critical patent/JP2024543211A5/ja
Pending legal-status Critical Current

Links

JP2024532790A 2021-12-01 2022-11-30 全身投与用の機能的aavカプシド Pending JP2024543211A (ja)

Applications Claiming Priority (9)

Application Number Priority Date Filing Date Title
US202163284977P 2021-12-01 2021-12-01
US63/284,977 2021-12-01
US202263342032P 2022-05-13 2022-05-13
US63/342,032 2022-05-13
US202263354635P 2022-06-22 2022-06-22
US63/354,635 2022-06-22
US202263399164P 2022-08-18 2022-08-18
US63/399,164 2022-08-18
PCT/US2022/051452 WO2023102079A1 (en) 2021-12-01 2022-11-30 Functional aav capsids for systemic administration

Publications (2)

Publication Number Publication Date
JP2024543211A JP2024543211A (ja) 2024-11-19
JP2024543211A5 true JP2024543211A5 (https=) 2025-12-08

Family

ID=84627347

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024532790A Pending JP2024543211A (ja) 2021-12-01 2022-11-30 全身投与用の機能的aavカプシド

Country Status (6)

Country Link
US (1) US20250205363A1 (https=)
EP (1) EP4440696A1 (https=)
JP (1) JP2024543211A (https=)
AU (1) AU2022401548A1 (https=)
CA (1) CA3239452A1 (https=)
WO (1) WO2023102079A1 (https=)

Families Citing this family (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2025194009A1 (en) * 2024-03-13 2025-09-18 Sangamo Therapeutics, Inc. Zinc finger proteins for treating prion disease
WO2026036118A1 (en) 2024-08-09 2026-02-12 Shape Therapeutics Inc. Engineered aav capsid polypeptides and methods of use
WO2026064444A1 (en) * 2024-09-18 2026-03-26 Dyno Therapeutics, Inc. Capsid polypeptides and methods of use thereof

Family Cites Families (6)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
ES2525067T3 (es) 2005-04-07 2014-12-17 The Trustees Of The University Of Pennsylvania Método de incremento de la función de un vector de AAV
US10081659B2 (en) * 2015-04-06 2018-09-25 The United States Of America, As Represented By The Secretary, Dept. Of Health And Human Services Adeno-associated vectors for enhanced transduction and reduced immunogenicity
PT3589730T (pt) 2017-02-28 2024-02-28 Univ Pennsylvania Vetor de vírus adenoassociado (aav) de clado f e suas utilizações
EP3833745A1 (en) 2018-08-10 2021-06-16 REGENXBIO Inc. Scalable method for recombinant aav production
EP3856762A1 (en) * 2018-09-28 2021-08-04 Voyager Therapeutics, Inc. Frataxin expression constructs having engineered promoters and methods of use thereof
EP3947700A4 (en) * 2019-04-01 2023-01-04 Tenaya Therapeutics, Inc. Adeno-associated virus with engineered capsid

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