JP2024543211A5 - - Google Patents
Info
- Publication number
- JP2024543211A5 JP2024543211A5 JP2024532790A JP2024532790A JP2024543211A5 JP 2024543211 A5 JP2024543211 A5 JP 2024543211A5 JP 2024532790 A JP2024532790 A JP 2024532790A JP 2024532790 A JP2024532790 A JP 2024532790A JP 2024543211 A5 JP2024543211 A5 JP 2024543211A5
- Authority
- JP
- Japan
- Prior art keywords
- raav
- sequence
- seq
- item
- capsid
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (9)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202163284977P | 2021-12-01 | 2021-12-01 | |
| US63/284,977 | 2021-12-01 | ||
| US202263342032P | 2022-05-13 | 2022-05-13 | |
| US63/342,032 | 2022-05-13 | ||
| US202263354635P | 2022-06-22 | 2022-06-22 | |
| US63/354,635 | 2022-06-22 | ||
| US202263399164P | 2022-08-18 | 2022-08-18 | |
| US63/399,164 | 2022-08-18 | ||
| PCT/US2022/051452 WO2023102079A1 (en) | 2021-12-01 | 2022-11-30 | Functional aav capsids for systemic administration |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2024543211A JP2024543211A (ja) | 2024-11-19 |
| JP2024543211A5 true JP2024543211A5 (https=) | 2025-12-08 |
Family
ID=84627347
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024532790A Pending JP2024543211A (ja) | 2021-12-01 | 2022-11-30 | 全身投与用の機能的aavカプシド |
Country Status (6)
| Country | Link |
|---|---|
| US (1) | US20250205363A1 (https=) |
| EP (1) | EP4440696A1 (https=) |
| JP (1) | JP2024543211A (https=) |
| AU (1) | AU2022401548A1 (https=) |
| CA (1) | CA3239452A1 (https=) |
| WO (1) | WO2023102079A1 (https=) |
Families Citing this family (3)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| WO2025194009A1 (en) * | 2024-03-13 | 2025-09-18 | Sangamo Therapeutics, Inc. | Zinc finger proteins for treating prion disease |
| WO2026036118A1 (en) | 2024-08-09 | 2026-02-12 | Shape Therapeutics Inc. | Engineered aav capsid polypeptides and methods of use |
| WO2026064444A1 (en) * | 2024-09-18 | 2026-03-26 | Dyno Therapeutics, Inc. | Capsid polypeptides and methods of use thereof |
Family Cites Families (6)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| ES2525067T3 (es) | 2005-04-07 | 2014-12-17 | The Trustees Of The University Of Pennsylvania | Método de incremento de la función de un vector de AAV |
| US10081659B2 (en) * | 2015-04-06 | 2018-09-25 | The United States Of America, As Represented By The Secretary, Dept. Of Health And Human Services | Adeno-associated vectors for enhanced transduction and reduced immunogenicity |
| PT3589730T (pt) | 2017-02-28 | 2024-02-28 | Univ Pennsylvania | Vetor de vírus adenoassociado (aav) de clado f e suas utilizações |
| EP3833745A1 (en) | 2018-08-10 | 2021-06-16 | REGENXBIO Inc. | Scalable method for recombinant aav production |
| EP3856762A1 (en) * | 2018-09-28 | 2021-08-04 | Voyager Therapeutics, Inc. | Frataxin expression constructs having engineered promoters and methods of use thereof |
| EP3947700A4 (en) * | 2019-04-01 | 2023-01-04 | Tenaya Therapeutics, Inc. | Adeno-associated virus with engineered capsid |
-
2022
- 2022-11-30 EP EP22830661.9A patent/EP4440696A1/en active Pending
- 2022-11-30 US US18/714,511 patent/US20250205363A1/en active Pending
- 2022-11-30 JP JP2024532790A patent/JP2024543211A/ja active Pending
- 2022-11-30 WO PCT/US2022/051452 patent/WO2023102079A1/en not_active Ceased
- 2022-11-30 AU AU2022401548A patent/AU2022401548A1/en active Pending
- 2022-11-30 CA CA3239452A patent/CA3239452A1/en active Pending
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