JP2023529315A5 - - Google Patents
Info
- Publication number
- JP2023529315A5 JP2023529315A5 JP2022572556A JP2022572556A JP2023529315A5 JP 2023529315 A5 JP2023529315 A5 JP 2023529315A5 JP 2022572556 A JP2022572556 A JP 2022572556A JP 2022572556 A JP2022572556 A JP 2022572556A JP 2023529315 A5 JP2023529315 A5 JP 2023529315A5
- Authority
- JP
- Japan
- Prior art keywords
- item
- capsid polypeptide
- engineered aav
- aav
- engineered
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (9)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202063030038P | 2020-05-26 | 2020-05-26 | |
| US63/030,038 | 2020-05-26 | ||
| US202063119554P | 2020-11-30 | 2020-11-30 | |
| US63/119,554 | 2020-11-30 | ||
| US202163134885P | 2021-01-07 | 2021-01-07 | |
| US63/134,885 | 2021-01-07 | ||
| US202163181037P | 2021-04-28 | 2021-04-28 | |
| US63/181,037 | 2021-04-28 | ||
| PCT/US2021/034329 WO2021242909A1 (en) | 2020-05-26 | 2021-05-26 | High throughput engineering of functional aav capsids |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2023529315A JP2023529315A (ja) | 2023-07-10 |
| JP2023529315A5 true JP2023529315A5 (https=) | 2024-06-04 |
Family
ID=78722738
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022572556A Pending JP2023529315A (ja) | 2020-05-26 | 2021-05-26 | 機能的ａａｖカプシドのハイスループット工学操作 |
Country Status (7)
| Country | Link |
|---|---|
| US (2) | US20230048732A1 (https=) |
| EP (1) | EP4158037A1 (https=) |
| JP (1) | JP2023529315A (https=) |
| CN (1) | CN116390934A (https=) |
| AU (1) | AU2021282257A1 (https=) |
| CA (1) | CA3173450A1 (https=) |
| WO (1) | WO2021242909A1 (https=) |
Families Citing this family (21)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| CN113166208B (zh) | 2018-10-02 | 2024-11-22 | 沃雅戈治疗公司 | 重新定向aav衣壳的嗜性 |
| TWI900553B (zh) | 2020-05-13 | 2025-10-11 | 美商航海家醫療公司 | Aav蛋白殼之趨性重定向 |
| KR20240095539A (ko) | 2021-10-08 | 2024-06-25 | 디노 테라퓨틱스, 인코포레이티드 | 캡시드 변이체 및 이의 사용 방법 |
| EP4426716A1 (en) | 2021-11-02 | 2024-09-11 | Voyager Therapeutics, Inc. | Aav capsid variants and uses thereof |
| CA3249551A1 (en) | 2022-02-08 | 2023-08-17 | Voyager Therapeutics, Inc. | AAV Capsid Variants and Their Uses |
| WO2023152229A1 (en) | 2022-02-09 | 2023-08-17 | Teitur Trophics Aps | Novel peptides |
| CA3259902A1 (en) | 2022-06-28 | 2024-01-04 | Voyager Therapeutics, Inc. | AAV Capsid Variants and Their Uses |
| US20250388626A1 (en) | 2022-07-06 | 2025-12-25 | Voyager Therapeutics, Inc. | Aav capsid variants and uses thereof |
| EP4626906A1 (en) * | 2022-11-29 | 2025-10-08 | Vacino Biotech Co., Ltd. | Transporter peptides and application thereof |
| CN118307648A (zh) * | 2023-01-09 | 2024-07-09 | 广东克冠达医药科技有限公司 | 腺相关病毒衣壳蛋白衍生多肽及其用途 |
| EP4410988A1 (en) * | 2023-01-31 | 2024-08-07 | Universitätsklinikum Hamburg-Eppendorf | An aav2-vector variant for targeted transfer of genes |
| WO2024191778A1 (en) | 2023-03-10 | 2024-09-19 | Dyno Therapeutics, Inc. | Capsid polypeptides and methods of use thereof |
| TW202523846A (zh) | 2023-08-16 | 2025-06-16 | 美商航海家醫療公司 | 用於治療與共濟蛋白(frataxin)不足有關之疾病之組合物及方法 |
| WO2025038796A1 (en) | 2023-08-16 | 2025-02-20 | Voyager Therapeutics, Inc. | Compositions and methods for the treatment of disorders related to cdkl5 deficiency |
| WO2025038805A1 (en) | 2023-08-16 | 2025-02-20 | Voyager Therapeutics, Inc. | Compositions and methods for the treatment of disorders related to glucosylceramidase beta 1 deficiency |
| WO2025038795A1 (en) | 2023-08-16 | 2025-02-20 | Voyager Therapeutics, Inc. | Compositions and methods for the treatment of disorders related to dystrophia myotonica protein kinase |
| AU2024332181A1 (en) | 2023-08-31 | 2026-02-12 | Dyno Therapeutics, Inc. | Capsid polypeptides and methods of use thereof |
| WO2025137219A1 (en) | 2023-12-21 | 2025-06-26 | Voyager Therapeutics, Inc. | Compositions and methods for the treatment of disorders related to dystrophia myotonica protein kinase |
| WO2025147436A1 (en) | 2024-01-03 | 2025-07-10 | Voyager Therapeutics, Inc. | Aav capsid variants and uses thereof |
| TW202545971A (zh) | 2024-02-08 | 2025-12-01 | 美商戴諾治療公司 | 殼體多肽及其使用方法 |
| WO2026064442A2 (en) | 2024-09-18 | 2026-03-26 | Dyno Therapeutics, Inc. | Capsid polypeptides and methods of use thereof |
Family Cites Families (9)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| ES2525067T3 (es) | 2005-04-07 | 2014-12-17 | The Trustees Of The University Of Pennsylvania | Método de incremento de la función de un vector de AAV |
| EP3003391B1 (en) * | 2013-05-31 | 2021-09-22 | The Regents of The University of California | Adeno-associated virus variants and methods of use thereof |
| WO2015048534A1 (en) * | 2013-09-26 | 2015-04-02 | University Of Florida Research Foundation, Inc. | Synthetic combinatorial aav capsid library for targeted gene therapy |
| EP3200830B1 (en) * | 2014-10-03 | 2020-09-09 | University of Massachusetts | High efficiency library-identified aav vectors |
| WO2017075335A1 (en) * | 2015-10-28 | 2017-05-04 | Voyager Therapeutics, Inc. | Regulatable expression using adeno-associated virus (aav) |
| SG11201808812RA (en) * | 2016-04-15 | 2018-11-29 | Univ Pennsylvania | Novel aav8 mutant capsids and compositions containing same |
| PT3589730T (pt) | 2017-02-28 | 2024-02-28 | Univ Pennsylvania | Vetor de vírus adenoassociado (aav) de clado f e suas utilizações |
| JP2020534788A (ja) * | 2017-08-28 | 2020-12-03 | ザ リージェンツ オブ ザ ユニバーシティ オブ カリフォルニア | アデノ随伴ウイルスカプシド変異体及びその使用方法 |
| EP3833745A1 (en) | 2018-08-10 | 2021-06-16 | REGENXBIO Inc. | Scalable method for recombinant aav production |
-
2021
- 2021-05-26 CN CN202180058369.6A patent/CN116390934A/zh active Pending
- 2021-05-26 WO PCT/US2021/034329 patent/WO2021242909A1/en not_active Ceased
- 2021-05-26 EP EP21742555.2A patent/EP4158037A1/en not_active Withdrawn
- 2021-05-26 AU AU2021282257A patent/AU2021282257A1/en not_active Abandoned
- 2021-05-26 JP JP2022572556A patent/JP2023529315A/ja active Pending
- 2021-05-26 US US17/331,462 patent/US20230048732A1/en not_active Abandoned
- 2021-05-26 CA CA3173450A patent/CA3173450A1/en active Pending
-
2025
- 2025-01-17 US US19/027,134 patent/US20260002177A1/en active Pending
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