JP2025510975A5 - - Google Patents

Info

Publication number
JP2025510975A5
JP2025510975A5 JP2024557528A JP2024557528A JP2025510975A5 JP 2025510975 A5 JP2025510975 A5 JP 2025510975A5 JP 2024557528 A JP2024557528 A JP 2024557528A JP 2024557528 A JP2024557528 A JP 2024557528A JP 2025510975 A5 JP2025510975 A5 JP 2025510975A5
Authority
JP
Japan
Prior art keywords
amino acid
seq
aav
acid sequence
capsid polypeptide
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024557528A
Other languages
English (en)
Japanese (ja)
Other versions
JP2025510975A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2023/016871 external-priority patent/WO2023192463A2/en
Publication of JP2025510975A publication Critical patent/JP2025510975A/ja
Publication of JP2025510975A5 publication Critical patent/JP2025510975A5/ja
Pending legal-status Critical Current

Links

JP2024557528A 2022-03-30 2023-03-30 網膜細胞に核酸を送達するためのアデノ随伴ウイルスベクター Pending JP2025510975A (ja)

Applications Claiming Priority (27)

Application Number Priority Date Filing Date Title
US202263325541P 2022-03-30 2022-03-30
US202263325542P 2022-03-30 2022-03-30
US202263325548P 2022-03-30 2022-03-30
US202263325558P 2022-03-30 2022-03-30
US202263325553P 2022-03-30 2022-03-30
US202263325544P 2022-03-30 2022-03-30
US202263325543P 2022-03-30 2022-03-30
US202263325540P 2022-03-30 2022-03-30
US202263325559P 2022-03-30 2022-03-30
US202263325562P 2022-03-30 2022-03-30
US202263325551P 2022-03-30 2022-03-30
US202263325550P 2022-03-30 2022-03-30
US202263325555P 2022-03-30 2022-03-30
US63/325,543 2022-03-30
US63/325,555 2022-03-30
US63/325,540 2022-03-30
US63/325,544 2022-03-30
US63/325,553 2022-03-30
US63/325,562 2022-03-30
US63/325,550 2022-03-30
US63/325,551 2022-03-30
US63/325,559 2022-03-30
US63/325,541 2022-03-30
US63/325,542 2022-03-30
US63/325,548 2022-03-30
US63/325,558 2022-03-30
PCT/US2023/016871 WO2023192463A2 (en) 2022-03-30 2023-03-30 Adeno-associated virus vectors for nucleic acid delivery to retinal cells

Publications (2)

Publication Number Publication Date
JP2025510975A JP2025510975A (ja) 2025-04-15
JP2025510975A5 true JP2025510975A5 (https=) 2026-04-07

Family

ID=88203541

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024557528A Pending JP2025510975A (ja) 2022-03-30 2023-03-30 網膜細胞に核酸を送達するためのアデノ随伴ウイルスベクター

Country Status (11)

Country Link
US (1) US20250327092A1 (https=)
EP (1) EP4499848A4 (https=)
JP (1) JP2025510975A (https=)
KR (1) KR20250006360A (https=)
CN (1) CN119213136A (https=)
AU (1) AU2023243048A1 (https=)
CA (1) CA3255255A1 (https=)
IL (1) IL316014A (https=)
MX (1) MX2024011963A (https=)
TW (1) TW202405180A (https=)
WO (1) WO2023192463A2 (https=)

Families Citing this family (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2025072688A2 (en) * 2023-09-27 2025-04-03 University Of Pittsburgh - Of The Commonwealth System Of Higher Education Adeno-associated virus vectors for nucleic acid delivery to retinal cells, for nucleic acid delivery across retinal regions, or for nucleic acid delivery to retinal ganglion cells and/or retinal pigment epithelium cells

Family Cites Families (6)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CN105755044A (zh) * 2011-04-22 2016-07-13 加利福尼亚大学董事会 具有变异衣壳的腺相关病毒病毒体及其使用方法
CN110612353A (zh) * 2017-03-03 2019-12-24 加利福尼亚大学董事会 经由抑制性tRNAs和脱氨酶对突变进行RNA靶向
CA3053154A1 (en) * 2017-06-30 2019-01-03 The Regents Of The University Of California Adeno-associated virus virions with variant capsids and methods of use thereof
AU2019227910B2 (en) * 2018-02-28 2025-07-17 The Regents Of The University Of California A modular system for gene and protein delivery based on AAV
US20220348613A1 (en) * 2019-08-28 2022-11-03 University of Pittsburgh - of the Commonwealath System of Higher Ecucation Adeno-associated viruses and methods and materials for making and using adeno-associated viruses
US20220313722A1 (en) * 2019-09-09 2022-10-06 University Of Pittsburgh - Of The Commonwealth System Of Higher Education Methods of restoring lysosomal function of retinal pigment epithelial cells by activation of tfeb

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