JP2024517737A5 - - Google Patents

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Publication number
JP2024517737A5
JP2024517737A5 JP2023566490A JP2023566490A JP2024517737A5 JP 2024517737 A5 JP2024517737 A5 JP 2024517737A5 JP 2023566490 A JP2023566490 A JP 2023566490A JP 2023566490 A JP2023566490 A JP 2023566490A JP 2024517737 A5 JP2024517737 A5 JP 2024517737A5
Authority
JP
Japan
Application number
JP2023566490A
Other languages
Japanese (ja)
Other versions
JP2024517737A (ja
JPWO2022231950A5 (https=
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/025834 external-priority patent/WO2022231950A1/en
Publication of JP2024517737A publication Critical patent/JP2024517737A/ja
Publication of JP2024517737A5 publication Critical patent/JP2024517737A5/ja
Publication of JPWO2022231950A5 publication Critical patent/JPWO2022231950A5/ja
Pending legal-status Critical Current

Links

JP2023566490A 2021-04-26 2022-04-21 Ngyl1欠損症を治療する組成物及び方法 Pending JP2024517737A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202163180065P 2021-04-26 2021-04-26
US63/180,065 2021-04-26
PCT/US2022/025834 WO2022231950A1 (en) 2021-04-26 2022-04-21 Compositions and methods for treating ngyl1 deficiency

Publications (3)

Publication Number Publication Date
JP2024517737A JP2024517737A (ja) 2024-04-23
JP2024517737A5 true JP2024517737A5 (https=) 2025-06-02
JPWO2022231950A5 JPWO2022231950A5 (https=) 2025-06-02

Family

ID=83848571

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023566490A Pending JP2024517737A (ja) 2021-04-26 2022-04-21 Ngyl1欠損症を治療する組成物及び方法

Country Status (5)

Country Link
US (1) US20240218396A1 (https=)
EP (1) EP4329824A4 (https=)
JP (1) JP2024517737A (https=)
CA (1) CA3216809A1 (https=)
WO (1) WO2022231950A1 (https=)

Family Cites Families (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
IL248102B (en) * 2014-05-02 2022-07-01 Genzyme Corp aav vectors for gene therapy of the central nervous system and retina
EP3564263A1 (en) * 2018-05-03 2019-11-06 Universitätsklinikum Hamburg-Eppendorf Fusion proteins comprising a cell surface marker specific vhh
WO2020210592A1 (en) * 2019-04-12 2020-10-15 University Of Massachusetts Recombinant aav gene therapy for ngyl1 deficiency

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