JP2023536067A5 - - Google Patents

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Publication number
JP2023536067A5
JP2023536067A5 JP2023503171A JP2023503171A JP2023536067A5 JP 2023536067 A5 JP2023536067 A5 JP 2023536067A5 JP 2023503171 A JP2023503171 A JP 2023503171A JP 2023503171 A JP2023503171 A JP 2023503171A JP 2023536067 A5 JP2023536067 A5 JP 2023536067A5
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JP
Japan
Application number
JP2023503171A
Other languages
Japanese (ja)
Other versions
JP2023536067A (ja
JPWO2022020697A5 (https=
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Publication date
Application filed filed Critical
Priority claimed from PCT/US2021/042930 external-priority patent/WO2022020697A1/en
Publication of JP2023536067A publication Critical patent/JP2023536067A/ja
Publication of JPWO2022020697A5 publication Critical patent/JPWO2022020697A5/ja
Publication of JP2023536067A5 publication Critical patent/JP2023536067A5/ja
Pending legal-status Critical Current

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JP2023503171A 2020-07-23 2021-07-23 最適化されたslc13a5遺伝子および発現カセットならびにそれらの使用 Pending JP2023536067A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202063055795P 2020-07-23 2020-07-23
US63/055,795 2020-07-23
PCT/US2021/042930 WO2022020697A1 (en) 2020-07-23 2021-07-23 Optimized slc13a5 genes and expression cassettes and their use

Publications (3)

Publication Number Publication Date
JP2023536067A JP2023536067A (ja) 2023-08-23
JPWO2022020697A5 JPWO2022020697A5 (https=) 2024-07-09
JP2023536067A5 true JP2023536067A5 (https=) 2024-07-09

Family

ID=79728993

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023503171A Pending JP2023536067A (ja) 2020-07-23 2021-07-23 最適化されたslc13a5遺伝子および発現カセットならびにそれらの使用

Country Status (6)

Country Link
US (1) US20230285595A1 (https=)
EP (2) EP4185700B1 (https=)
JP (1) JP2023536067A (https=)
CA (1) CA3186207A1 (https=)
ES (1) ES3057565T3 (https=)
WO (1) WO2022020697A1 (https=)

Families Citing this family (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US20240342314A1 (en) * 2021-09-30 2024-10-17 The Board Of Regents Of The University Of Texas System Slc13a5 gene therapy vectors and uses thereof

Family Cites Families (22)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US4501729A (en) 1982-12-13 1985-02-26 Research Corporation Aerosolized amiloride treatment of retained pulmonary secretions
US5399346A (en) 1989-06-14 1995-03-21 The United States Of America As Represented By The Department Of Health And Human Services Gene therapy
US5587308A (en) * 1992-06-02 1996-12-24 The United States Of America As Represented By The Department Of Health & Human Services Modified adeno-associated virus vector capable of expression from a novel promoter
US5478745A (en) 1992-12-04 1995-12-26 University Of Pittsburgh Recombinant viral vector system
US6040183A (en) 1995-06-07 2000-03-21 University Of North Carloina At Chapel Hill Helper virus-free AAV production
US6093570A (en) 1995-06-07 2000-07-25 The University Of North Carolina At Chapel Hill Helper virus-free AAV production
CA2265460A1 (en) 1996-09-11 1998-03-19 The Government Of The United States Of America, Represented By The Secre Tary, Department Of Health And Human Services Aav4 vector and uses thereof
US6156303A (en) 1997-06-11 2000-12-05 University Of Washington Adeno-associated virus (AAV) isolates and AAV vectors derived therefrom
EP1082413B1 (en) 1998-05-28 2008-07-23 THE GOVERNMENT OF THE UNITED STATES OF AMERICA, as represented by THE SECRETARY, DEPARTMENT OF HEALTH AND HUMAN SERVICES Aav5 vector and uses thereof
AU774706B2 (en) 1998-09-22 2004-07-08 Johns Hopkins University, The Methods for large-scale production of recombinant AAV vectors
CA2349838C (en) 1998-11-05 2011-06-07 The Trustees Of The University Of Pennsylvania Adeno-associated virus serotype 1 nucleic acid sequences, vectors and host cells containing same
ES2340230T3 (es) 1998-11-10 2010-05-31 University Of North Carolina At Chapel Hill Vectores viricos y sus procedimientos de preparacion y administracion.
NZ522840A (en) * 2000-06-01 2004-12-24 Univ North Carolina A parvovirus vector that carries a duplexed genome resulting in co-packaging of strands of plus and minus polarity tethered together
US7201898B2 (en) 2000-06-01 2007-04-10 The University Of North Carolina At Chapel Hill Methods and compounds for controlled release of recombinant parvovirus vectors
AU2003298675A1 (en) * 2002-11-22 2004-06-18 You-Jun Fei NaCT AS A TARGET FOR LIFESPAN EXPANSION AND WEIGHT REDUCTION
AU2013243948A1 (en) * 2012-04-02 2014-10-30 Moderna Therapeutics, Inc. Modified polynucleotides for the production of proteins associated with human disease
US9636370B2 (en) 2012-09-28 2017-05-02 The University Of North Carolina At Chapel Hill AAV vectors targeted to oligodendrocytes
WO2016081811A1 (en) 2014-11-21 2016-05-26 The University Of North Carolina At Chapel Hill Aav vectors targeted to the central nervous system
EP3443001B1 (en) * 2016-04-11 2025-04-30 Obsidian Therapeutics, Inc. REGULATED BIOCIRCUIT SYSTEMS
RU2764919C2 (ru) * 2016-06-13 2022-01-24 Дзе Юниверсити Оф Норт Каролина Эт Чепел Хилл Оптимизированные гены и экспрессионные кассеты cln1, и их применение
KR102709597B1 (ko) * 2017-10-03 2024-09-26 프리베일 테라퓨틱스, 인크. 리소좀 장애를 위한 유전자 요법
US20240342314A1 (en) * 2021-09-30 2024-10-17 The Board Of Regents Of The University Of Texas System Slc13a5 gene therapy vectors and uses thereof

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