JP2023536067A5 - - Google Patents
Info
- Publication number
- JP2023536067A5 JP2023536067A5 JP2023503171A JP2023503171A JP2023536067A5 JP 2023536067 A5 JP2023536067 A5 JP 2023536067A5 JP 2023503171 A JP2023503171 A JP 2023503171A JP 2023503171 A JP2023503171 A JP 2023503171A JP 2023536067 A5 JP2023536067 A5 JP 2023536067A5
- Authority
- JP
- Japan
- Prior art keywords
- pharmaceutical composition
- expression cassette
- vector
- slc13a5
- aav
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202063055795P | 2020-07-23 | 2020-07-23 | |
| US63/055,795 | 2020-07-23 | ||
| PCT/US2021/042930 WO2022020697A1 (en) | 2020-07-23 | 2021-07-23 | Optimized slc13a5 genes and expression cassettes and their use |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2023536067A JP2023536067A (ja) | 2023-08-23 |
| JP2023536067A5 true JP2023536067A5 (https=) | 2024-07-09 |
Family
ID=79728993
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023503171A Pending JP2023536067A (ja) | 2020-07-23 | 2021-07-23 | 最適化されたｓｌｃ１３ａ５遺伝子および発現カセットならびにそれらの使用 |
Country Status (6)
| Country | Link |
|---|---|
| US (1) | US20230285595A1 (https=) |
| EP (2) | EP4700126A2 (https=) |
| JP (1) | JP2023536067A (https=) |
| CA (1) | CA3186207A1 (https=) |
| ES (1) | ES3057565T3 (https=) |
| WO (1) | WO2022020697A1 (https=) |
Families Citing this family (1)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| WO2023056367A1 (en) * | 2021-09-30 | 2023-04-06 | The Board Of Regents Of The Universityof Texas System | Slc13a5 gene therapy vectors and uses thereof |
Family Cites Families (22)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US4501729A (en) | 1982-12-13 | 1985-02-26 | Research Corporation | Aerosolized amiloride treatment of retained pulmonary secretions |
| US5399346A (en) | 1989-06-14 | 1995-03-21 | The United States Of America As Represented By The Department Of Health And Human Services | Gene therapy |
| US5587308A (en) * | 1992-06-02 | 1996-12-24 | The United States Of America As Represented By The Department Of Health & Human Services | Modified adeno-associated virus vector capable of expression from a novel promoter |
| US5478745A (en) | 1992-12-04 | 1995-12-26 | University Of Pittsburgh | Recombinant viral vector system |
| US6040183A (en) | 1995-06-07 | 2000-03-21 | University Of North Carloina At Chapel Hill | Helper virus-free AAV production |
| US6093570A (en) | 1995-06-07 | 2000-07-25 | The University Of North Carolina At Chapel Hill | Helper virus-free AAV production |
| WO1998011244A2 (en) | 1996-09-11 | 1998-03-19 | The Government Of The United States Of America, Represented By The Secretary, Department Of Health And Human Services | Aav4 vector and uses thereof |
| US6156303A (en) | 1997-06-11 | 2000-12-05 | University Of Washington | Adeno-associated virus (AAV) isolates and AAV vectors derived therefrom |
| WO1999061601A2 (en) | 1998-05-28 | 1999-12-02 | The Government Of The United States Of America, As Represented By The Secretary, Department Of Health And Human Services | Aav5 vector and uses thereof |
| AU774706B2 (en) | 1998-09-22 | 2004-07-08 | Johns Hopkins University, The | Methods for large-scale production of recombinant AAV vectors |
| ATE362542T1 (de) | 1998-11-05 | 2007-06-15 | Univ Pennsylvania | Nukleinsäuresequenzen des adeno-assoziierten virus des serotyps i, und vektoren und wirtszellen, die diese enthalten |
| AU780231B2 (en) | 1998-11-10 | 2005-03-10 | University Of North Carolina At Chapel Hill, The | Virus vectors and methods of making and administering the same |
| US7201898B2 (en) | 2000-06-01 | 2007-04-10 | The University Of North Carolina At Chapel Hill | Methods and compounds for controlled release of recombinant parvovirus vectors |
| ATE318923T1 (de) * | 2000-06-01 | 2006-03-15 | Univ North Carolina | Doppelsträngige parvovirus-vektoren |
| AU2003298675A1 (en) * | 2002-11-22 | 2004-06-18 | You-Jun Fei | NaCT AS A TARGET FOR LIFESPAN EXPANSION AND WEIGHT REDUCTION |
| WO2013151665A2 (en) * | 2012-04-02 | 2013-10-10 | modeRNA Therapeutics | Modified polynucleotides for the production of proteins associated with human disease |
| EP2900686B1 (en) | 2012-09-28 | 2020-06-10 | The University of North Carolina At Chapel Hill | Aav vectors targeted to oligodendrocytes |
| EP4344741A3 (en) | 2014-11-21 | 2024-08-28 | The University of North Carolina at Chapel Hill | Aav vectors targeted to the central nervous system |
| US11446398B2 (en) * | 2016-04-11 | 2022-09-20 | Obsidian Therapeutics, Inc. | Regulated biocircuit systems |
| CN109415730A (zh) * | 2016-06-13 | 2019-03-01 | 北卡罗来纳大学教堂山分校 | 优化的cln1基因和表达盒以及它们的应用 |
| BR112020006661A2 (pt) * | 2017-10-03 | 2020-10-13 | Prevail Therapeutics, Inc. | terapias de genes para distúrbios lipossomais |
| WO2023056367A1 (en) * | 2021-09-30 | 2023-04-06 | The Board Of Regents Of The Universityof Texas System | Slc13a5 gene therapy vectors and uses thereof |
-
2021
- 2021-07-23 CA CA3186207A patent/CA3186207A1/en active Pending
- 2021-07-23 EP EP25214109.8A patent/EP4700126A2/en active Pending
- 2021-07-23 JP JP2023503171A patent/JP2023536067A/ja active Pending
- 2021-07-23 ES ES21845857T patent/ES3057565T3/es active Active
- 2021-07-23 EP EP21845857.8A patent/EP4185700B1/en active Active
- 2021-07-23 US US18/006,278 patent/US20230285595A1/en active Pending
- 2021-07-23 WO PCT/US2021/042930 patent/WO2022020697A1/en not_active Ceased
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