JP2025513066A5 - - Google Patents

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Publication number
JP2025513066A5
JP2025513066A5 JP2024560442A JP2024560442A JP2025513066A5 JP 2025513066 A5 JP2025513066 A5 JP 2025513066A5 JP 2024560442 A JP2024560442 A JP 2024560442A JP 2024560442 A JP2024560442 A JP 2024560442A JP 2025513066 A5 JP2025513066 A5 JP 2025513066A5
Authority
JP
Japan
Application number
JP2024560442A
Other languages
Japanese (ja)
Other versions
JP2025513066A (ja
JPWO2023198745A5 (https=
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/EP2023/059507 external-priority patent/WO2023198745A1/en
Publication of JP2025513066A publication Critical patent/JP2025513066A/ja
Publication of JP2025513066A5 publication Critical patent/JP2025513066A5/ja
Publication of JPWO2023198745A5 publication Critical patent/JPWO2023198745A5/ja
Pending legal-status Critical Current

Links

JP2024560442A 2022-04-12 2023-04-12 Apoeの核酸制御 Pending JP2025513066A (ja)

Applications Claiming Priority (7)

Application Number Priority Date Filing Date Title
EP22167926.9 2022-04-12
EP22167926 2022-04-12
EP22200272.7 2022-10-07
EP22200272 2022-10-07
EP23162681 2023-03-17
EP23162681.3 2023-03-17
PCT/EP2023/059507 WO2023198745A1 (en) 2022-04-12 2023-04-12 Nucleic acid regulation of apoe

Publications (3)

Publication Number Publication Date
JP2025513066A JP2025513066A (ja) 2025-04-22
JP2025513066A5 true JP2025513066A5 (https=) 2026-04-20
JPWO2023198745A5 JPWO2023198745A5 (https=) 2026-04-20

Family

ID=85873819

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024560442A Pending JP2025513066A (ja) 2022-04-12 2023-04-12 Apoeの核酸制御

Country Status (5)

Country Link
US (1) US20250223590A1 (https=)
EP (1) EP4508213A1 (https=)
JP (1) JP2025513066A (https=)
CN (1) CN119032174A (https=)
WO (1) WO2023198745A1 (https=)

Families Citing this family (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2025090631A1 (en) * 2023-10-23 2025-05-01 The Children's Hospital Of Philadelphia Aav vectors for delivery of apoe2
WO2025213111A2 (en) * 2024-04-05 2025-10-09 Cornell University Aav expression of mirna to suppress human apoe mrna
WO2025219443A1 (en) * 2024-04-19 2025-10-23 Uniqure Biopharma B.V. Nucleic acid for a1at regulation

Family Cites Families (12)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US6103526A (en) 1998-10-08 2000-08-15 Protein Sciences Corporation Spodoptera frugiperda single cell suspension cell line in serum-free media, methods of producing and using
EP2311967B1 (en) 2005-10-20 2017-09-20 UniQure IP B.V. Improved AAV vectors produced in insect cells
KR101589259B1 (ko) 2006-06-21 2016-02-01 유니큐어 아이피 비.브이. 곤충세포 내 aav의 생산에 유용한 aav-rep78의 번역을 위한 변형된 개시 코돈을 갖는 벡터
SI3093345T1 (sl) 2007-07-26 2019-08-30 Uniqure Ip B.V. Bakulovirusni vektorji, ki vsebujejo ponavljajoča kodirna zaporedja z različnimi kodonskimi preferencami
EP3257937B1 (en) 2008-02-19 2022-08-03 uniQure IP B.V. Optimisation of expression of parvoviral rep and cap proteins in insect cells
WO2011122950A1 (en) 2010-04-01 2011-10-06 Amsterdam Molecular Therapeutics (Amt) Ip B.V. Monomeric duplex aav vectors
PT2744895E (pt) 2011-09-08 2016-02-08 Uniqure Ip Bv Remoção de vírus contaminantes de preparações de aav
WO2015137802A1 (en) 2014-03-10 2015-09-17 Uniqure Ip B.V. Further improved aav vectors produced in insect cells
AU2015370903B2 (en) * 2014-12-24 2021-06-17 Uniqure Ip B.V. RNAi induced huntingtin gene suppression
JP7666922B2 (ja) 2017-07-20 2025-04-22 ユニキュアー アイピー ビー.ブイ. 昆虫細胞における向上したaavカプシド産生
EP4045653A1 (en) * 2019-10-16 2022-08-24 Cornell University Gene therapy for alzheimer's disease
EP4065600A1 (en) * 2019-11-25 2022-10-05 Cornell University Apoe gene therapy

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