JP2024542950A5 - - Google Patents

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Publication number
JP2024542950A5
JP2024542950A5 JP2024523457A JP2024523457A JP2024542950A5 JP 2024542950 A5 JP2024542950 A5 JP 2024542950A5 JP 2024523457 A JP2024523457 A JP 2024523457A JP 2024523457 A JP2024523457 A JP 2024523457A JP 2024542950 A5 JP2024542950 A5 JP 2024542950A5
Authority
JP
Japan
Application number
JP2024523457A
Other languages
Japanese (ja)
Other versions
JPWO2023069967A5 (https=
JP2024542950A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/078327 external-priority patent/WO2023069967A2/en
Publication of JP2024542950A publication Critical patent/JP2024542950A/ja
Publication of JPWO2023069967A5 publication Critical patent/JPWO2023069967A5/ja
Publication of JP2024542950A5 publication Critical patent/JP2024542950A5/ja
Pending legal-status Critical Current

Links

JP2024523457A 2021-10-18 2022-10-18 Cdkl5欠損症(cdd)の治療において有用な組成物 Pending JP2024542950A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202163256827P 2021-10-18 2021-10-18
US63/256,827 2021-10-18
PCT/US2022/078327 WO2023069967A2 (en) 2021-10-18 2022-10-18 Compositions useful in treatment of cdkl5 deficiency disorder (cdd)

Publications (3)

Publication Number Publication Date
JP2024542950A JP2024542950A (ja) 2024-11-19
JPWO2023069967A5 JPWO2023069967A5 (https=) 2025-10-20
JP2024542950A5 true JP2024542950A5 (https=) 2025-10-20

Family

ID=86058644

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024523457A Pending JP2024542950A (ja) 2021-10-18 2022-10-18 Cdkl5欠損症(cdd)の治療において有用な組成物

Country Status (11)

Country Link
US (1) US20240425882A1 (https=)
EP (1) EP4419690A4 (https=)
JP (1) JP2024542950A (https=)
KR (1) KR20240100490A (https=)
CN (1) CN118401667A (https=)
AU (1) AU2022369293A1 (https=)
CA (1) CA3235593A1 (https=)
CO (1) CO2024006328A2 (https=)
IL (1) IL312241A (https=)
MX (1) MX2024004723A (https=)
WO (1) WO2023069967A2 (https=)

Families Citing this family (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
IL297635A (en) * 2020-04-27 2022-12-01 Univ Pennsylvania Compositions useful in treatment of cdkl5 deficiency disorder (cdd)
WO2025050032A1 (en) * 2023-08-31 2025-03-06 Ultragenyx Pharmaceutical Inc. Methods of producing cdkl5 proteins and uses of the same

Family Cites Families (6)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
GB2610100B (en) * 2017-10-23 2023-08-16 Stoke Therapeutics Inc Antisense oligomers for treatment of non-sense mediated RNA decay based conditions and diseases
WO2020132455A1 (en) * 2018-12-21 2020-06-25 The Trustees Of The University Of Pennsylvania Compositions for drg-specific reduction of transgene expression
CA3133889A1 (en) * 2019-04-24 2020-10-29 The Trustees Of The University Of Pennsylvania Compositions useful in treatment of rett syndrome
WO2021081217A1 (en) * 2019-10-23 2021-04-29 The Trustees Of The University Of Pennsylvania Compositions for drg-specific reduction of transgene expression
CA3156506A1 (en) * 2019-10-30 2021-05-06 Amicus Therapeutics, Inc. Recombinant cdkl5 proteins, gene therapy and production methods
IL297635A (en) * 2020-04-27 2022-12-01 Univ Pennsylvania Compositions useful in treatment of cdkl5 deficiency disorder (cdd)

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