JP2022553406A5 - - Google Patents
Info
- Publication number
- JP2022553406A5 JP2022553406A5 JP2022524118A JP2022524118A JP2022553406A5 JP 2022553406 A5 JP2022553406 A5 JP 2022553406A5 JP 2022524118 A JP2022524118 A JP 2022524118A JP 2022524118 A JP2022524118 A JP 2022524118A JP 2022553406 A5 JP2022553406 A5 JP 2022553406A5
- Authority
- JP
- Japan
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Applications Claiming Priority (17)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201962924970P | 2019-10-23 | 2019-10-23 | |
| US62/924,970 | 2019-10-23 | ||
| US201962934915P | 2019-11-13 | 2019-11-13 | |
| US62/934,915 | 2019-11-13 | ||
| USPCT/US2019/067872 | 2019-12-20 | ||
| PCT/US2019/067872 WO2020132455A1 (en) | 2018-12-21 | 2019-12-20 | Compositions for drg-specific reduction of transgene expression |
| US202062972404P | 2020-02-10 | 2020-02-10 | |
| US62/972,404 | 2020-02-10 | ||
| US202063005894P | 2020-04-06 | 2020-04-06 | |
| US63/005,894 | 2020-04-06 | ||
| US202063023602P | 2020-05-12 | 2020-05-12 | |
| US63/023,602 | 2020-05-12 | ||
| US202063038514P | 2020-06-12 | 2020-06-12 | |
| US63/038,514 | 2020-06-12 | ||
| US202063043600P | 2020-06-24 | 2020-06-24 | |
| US63/043,600 | 2020-06-24 | ||
| PCT/US2020/056881 WO2021081217A1 (en) | 2019-10-23 | 2020-10-22 | Compositions for drg-specific reduction of transgene expression |
Publications (4)
| Publication Number | Publication Date |
|---|---|
| JP2022553406A JP2022553406A (ja) | 2022-12-22 |
| JPWO2021081217A5 JPWO2021081217A5 (https=) | 2023-10-18 |
| JP2022553406A5 true JP2022553406A5 (https=) | 2023-10-18 |
| JP7697943B2 JP7697943B2 (ja) | 2025-06-24 |
Family
ID=75620360
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022524118A Active JP7697943B2 (ja) | 2019-10-23 | 2020-10-22 | 導入遺伝子発現のｄｒｇ特異的低減のための組成物 |
Country Status (8)
| Country | Link |
|---|---|
| US (1) | US20220389457A1 (https=) |
| EP (1) | EP4048785A4 (https=) |
| JP (1) | JP7697943B2 (https=) |
| KR (1) | KR20220105158A (https=) |
| AU (1) | AU2020369570A1 (https=) |
| CA (1) | CA3155154A1 (https=) |
| IL (1) | IL292372A (https=) |
| WO (1) | WO2021081217A1 (https=) |
Families Citing this family (7)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US20230304034A1 (en) * | 2020-05-12 | 2023-09-28 | The Trustees Of The University Of Pennsylvania | Compositions for drg-specific reduction of transgene expression |
| BR112023003310A2 (pt) * | 2020-08-24 | 2023-05-02 | Univ Pennsylvania | Vetores virais que codificam fusões de agonistas do receptor de glp-1 e usos dos mesmos no tratamento de doenças metabólicas |
| AU2022369293A1 (en) * | 2021-10-18 | 2024-05-16 | The Trustees Of The University Of Pennsylvania | Compositions useful in treatment of cdkl5 deficiency disorder (cdd) |
| CA3236188A1 (en) * | 2021-10-27 | 2023-05-04 | The University Of North Carolina At Chapel Hill | Aav-idua vector for treatment of mps i |
| EP4551253A1 (en) * | 2022-07-08 | 2025-05-14 | Ospedale San Raffaele S.r.l. | Transgene cassettes |
| CN116064593B (zh) * | 2023-02-09 | 2024-05-14 | 四川大学 | 一种毛白杨pgag基因及其应用 |
| US20250276095A1 (en) * | 2024-03-04 | 2025-09-04 | Kate Therapeutics, Inc. | Adeno-associated virus compositions for the treatment of duchenne muscular dystrophy |
Family Cites Families (8)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| AU2013243948A1 (en) * | 2012-04-02 | 2014-10-30 | Moderna Therapeutics, Inc. | Modified polynucleotides for the production of proteins associated with human disease |
| FR3004463A1 (fr) * | 2013-04-11 | 2014-10-17 | Genethon | Systeme d'expression pour une therapie genique selective |
| IL248102B (en) * | 2014-05-02 | 2022-07-01 | Genzyme Corp | aav vectors for gene therapy of the central nervous system and retina |
| HK1256341A1 (zh) * | 2015-05-15 | 2019-09-20 | 明尼苏达大学董事会 | 用於治疗性递送到中枢神经系统的腺相关物 |
| EP3411488A1 (en) * | 2016-02-03 | 2018-12-12 | The Trustees Of The University Of Pennsylvania | Gene therapy for treating mucopolysaccharidosis type i |
| KR20180109945A (ko) * | 2016-02-22 | 2018-10-08 | 더 유니버시티 오브 노쓰 캐롤라이나 엣 채플 힐 | Ｍｐｓ ｉ－ 연관 실명의 치료를 위한 ａａｖ－ｉｄｕａ 벡터 |
| MA50016A (fr) * | 2017-07-06 | 2020-07-08 | Univ Pennsylvania | Thérapie génique médiée par aav9 pour traiter la mucopolysaccharidose de type i |
| SG11202002276VA (en) * | 2017-09-20 | 2020-04-29 | 4D Molecular Therapeutics Inc | Adeno-associated virus variant capsids and methods of use thereof |
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2020
- 2020-10-22 WO PCT/US2020/056881 patent/WO2021081217A1/en not_active Ceased
- 2020-10-22 KR KR1020227016895A patent/KR20220105158A/ko active Pending
- 2020-10-22 IL IL292372A patent/IL292372A/en unknown
- 2020-10-22 EP EP20880317.1A patent/EP4048785A4/en active Pending
- 2020-10-22 AU AU2020369570A patent/AU2020369570A1/en active Pending
- 2020-10-22 CA CA3155154A patent/CA3155154A1/en active Pending
- 2020-10-22 JP JP2022524118A patent/JP7697943B2/ja active Active
- 2020-10-22 US US17/770,137 patent/US20220389457A1/en active Pending