JP2023550581A5 - - Google Patents

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Publication number
JP2023550581A5
JP2023550581A5 JP2023526506A JP2023526506A JP2023550581A5 JP 2023550581 A5 JP2023550581 A5 JP 2023550581A5 JP 2023526506 A JP2023526506 A JP 2023526506A JP 2023526506 A JP2023526506 A JP 2023526506A JP 2023550581 A5 JP2023550581 A5 JP 2023550581A5
Authority
JP
Japan
Prior art keywords
seq
capsid
deamidated
nucleic acid
positions
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Withdrawn
Application number
JP2023526506A
Other languages
English (en)
Japanese (ja)
Other versions
JP2023550581A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2021/057201 external-priority patent/WO2022094180A1/en
Publication of JP2023550581A publication Critical patent/JP2023550581A/ja
Publication of JP2023550581A5 publication Critical patent/JP2023550581A5/ja
Withdrawn legal-status Critical Current

Links

JP2023526506A 2020-10-29 2021-10-29 Aavカプシド及びそれを含有する組成物 Withdrawn JP2023550581A (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US202063107030P 2020-10-29 2020-10-29
US63/107,030 2020-10-29
US202163214530P 2021-06-24 2021-06-24
US63/214,530 2021-06-24
PCT/US2021/057201 WO2022094180A1 (en) 2020-10-29 2021-10-29 Aav capsids and compositions containing same

Publications (2)

Publication Number Publication Date
JP2023550581A JP2023550581A (ja) 2023-12-04
JP2023550581A5 true JP2023550581A5 (https=) 2024-11-07

Family

ID=78851102

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023526506A Withdrawn JP2023550581A (ja) 2020-10-29 2021-10-29 Aavカプシド及びそれを含有する組成物

Country Status (9)

Country Link
US (1) US20230407333A1 (https=)
EP (1) EP4236975A1 (https=)
JP (1) JP2023550581A (https=)
CN (1) CN117042787A (https=)
AU (1) AU2021369793A1 (https=)
CA (1) CA3196499A1 (https=)
MX (1) MX2023005113A (https=)
TW (1) TW202233844A (https=)
WO (1) WO2022094180A1 (https=)

Families Citing this family (5)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2023034996A1 (en) * 2021-09-03 2023-03-09 Biomarin Pharmaceutical Inc. Aav capsid compositions and methods for delivery
EP4522633A2 (en) * 2022-05-13 2025-03-19 The Broad Institute, Inc. Adeno-associated viral vectors and uses thereof
US20260021205A1 (en) * 2022-07-15 2026-01-22 The Trustees Of The University Of Pennsylvania Recombinant aav having aav clade d and clade e capsids and compositions containing same
WO2024077089A2 (en) * 2022-10-04 2024-04-11 Siren Biotechnology, Inc. Modified cpg dinucleotides for recombinant viral vector production
WO2025212884A1 (en) * 2024-04-05 2025-10-09 University Of Massachusetts Discovery of novel aav capsid proteins through directed evolution of the vp1u region

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