JP2023551254A5 - - Google Patents

Info

Publication number
JP2023551254A5
JP2023551254A5 JP2023532127A JP2023532127A JP2023551254A5 JP 2023551254 A5 JP2023551254 A5 JP 2023551254A5 JP 2023532127 A JP2023532127 A JP 2023532127A JP 2023532127 A JP2023532127 A JP 2023532127A JP 2023551254 A5 JP2023551254 A5 JP 2023551254A5
Authority
JP
Japan
Prior art keywords
nucleic acid
isolated nucleic
protein
christchurch
pharmaceutical composition
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2023532127A
Other languages
English (en)
Japanese (ja)
Other versions
JP2023551254A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2021/060731 external-priority patent/WO2022115535A1/en
Publication of JP2023551254A publication Critical patent/JP2023551254A/ja
Publication of JP2023551254A5 publication Critical patent/JP2023551254A5/ja
Pending legal-status Critical Current

Links

JP2023532127A 2020-11-25 2021-11-24 神経変性疾患のための遺伝子治療 Pending JP2023551254A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202063118060P 2020-11-25 2020-11-25
US63/118,060 2020-11-25
PCT/US2021/060731 WO2022115535A1 (en) 2020-11-25 2021-11-24 Gene therapies for neurodegenerative disease

Publications (2)

Publication Number Publication Date
JP2023551254A JP2023551254A (ja) 2023-12-07
JP2023551254A5 true JP2023551254A5 (https=) 2024-12-04

Family

ID=81754891

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023532127A Pending JP2023551254A (ja) 2020-11-25 2021-11-24 神経変性疾患のための遺伝子治療

Country Status (10)

Country Link
US (1) US20230405149A1 (https=)
EP (1) EP4251276A4 (https=)
JP (1) JP2023551254A (https=)
KR (1) KR20230112672A (https=)
CN (1) CN116670291A (https=)
AU (1) AU2021386390A1 (https=)
CA (1) CA3203006A1 (https=)
IL (1) IL303156A (https=)
MX (1) MX2023006153A (https=)
WO (1) WO2022115535A1 (https=)

Families Citing this family (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP4065600A1 (en) 2019-11-25 2022-10-05 Cornell University Apoe gene therapy
CN121335984A (zh) * 2023-04-18 2026-01-13 康奈尔大学 用于治疗和预防阿尔茨海默病的方法和apoe药物组合物

Family Cites Families (5)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP1121429A2 (en) * 1998-10-16 2001-08-08 Introgene B.V. Gene therapy of alzheimer's disease by delivery of an encoded apolipoprotein e
AU5323301A (en) * 2000-04-06 2001-10-23 Kos Pharma Inc Compounds and methods for lowering cholesterol levels without inducing hypertriglyceridemia
CN104540952A (zh) * 2012-05-18 2015-04-22 衣阿华大学研究基金会 用于治疗淀粉状蛋白沉积的方法和组合物
JP7616995B2 (ja) * 2018-11-28 2025-01-17 プリベイル セラピューティクス，インコーポレーテッド 神経変性疾患のための遺伝子治療
EP4065600A1 (en) * 2019-11-25 2022-10-05 Cornell University Apoe gene therapy

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