JP2024539123A5 - - Google Patents
Info
- Publication number
- JP2024539123A5 JP2024539123A5 JP2024523575A JP2024523575A JP2024539123A5 JP 2024539123 A5 JP2024539123 A5 JP 2024539123A5 JP 2024523575 A JP2024523575 A JP 2024523575A JP 2024523575 A JP2024523575 A JP 2024523575A JP 2024539123 A5 JP2024539123 A5 JP 2024539123A5
- Authority
- JP
- Japan
- Prior art keywords
- aav
- aavhu
- aavrh
- approximately
- pharmaceutical composition
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202163271487P | 2021-10-25 | 2021-10-25 | |
| US63/271,487 | 2021-10-25 | ||
| PCT/IB2022/060189 WO2023073526A1 (en) | 2021-10-25 | 2022-10-24 | Methods for improving adeno-associated virus (aav) delivery |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2024539123A JP2024539123A (ja) | 2024-10-28 |
| JP2024539123A5 true JP2024539123A5 (https=) | 2025-10-31 |
Family
ID=84283163
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024523575A Pending JP2024539123A (ja) | 2021-10-25 | 2022-10-24 | アデノ随伴ウイルス（ａａｖ）送達を改善する方法 |
Country Status (5)
| Country | Link |
|---|---|
| US (1) | US20250235554A1 (https=) |
| EP (1) | EP4422613A1 (https=) |
| JP (1) | JP2024539123A (https=) |
| CN (1) | CN118043039A (https=) |
| WO (1) | WO2023073526A1 (https=) |
Families Citing this family (4)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| JPWO2024071362A1 (https=) * | 2022-09-30 | 2024-04-04 | ||
| WO2025101959A1 (en) * | 2023-11-08 | 2025-05-15 | Renbio, Inc. | Plasmid dna constructs for peptide hormone expression |
| WO2025250454A1 (en) * | 2024-05-28 | 2025-12-04 | University Of Rochester | Adeno-associated viruses evolved to specifically target human glial progenitor cells in vivo |
| CN118743768A (zh) * | 2024-06-13 | 2024-10-08 | 浙江大学 | 一种血小板-aav包装复合体及其制备方法和应用 |
Family Cites Families (19)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US5139941A (en) | 1985-10-31 | 1992-08-18 | University Of Florida Research Foundation, Inc. | AAV transduction vectors |
| WO1998033917A1 (en) | 1994-11-14 | 1998-08-06 | The Ludwig Institute For Cancer Research | Vascular endothelial growth factor c (vegf-c) protein and gene, mutants thereof, and uses thereof |
| US6001650A (en) | 1995-08-03 | 1999-12-14 | Avigen, Inc. | High-efficiency wild-type-free AAV helper functions |
| US6410300B1 (en) | 1998-01-12 | 2002-06-25 | The University Of North Carolina At Chapel Hill | Methods and formulations for mediating adeno-associated virus (AAV) attachment and infection and methods for purifying AAV |
| BRPI0511764B8 (pt) | 2004-06-01 | 2021-05-25 | Avigen Inc | método de prevenção de agregação de vírions de vírus adeno-associado recombinante (raav) em uma preparação purificada de virions raav |
| EP3470072A1 (en) | 2005-06-23 | 2019-04-17 | Biogen MA Inc. | Compositions and methods for modulation of smn2 splicing |
| US9415121B2 (en) | 2008-12-19 | 2016-08-16 | Nationwide Children's Hospital | Delivery of MECP2 polynucleotide using recombinant AAV9 |
| ES2699827T3 (es) | 2009-06-17 | 2019-02-13 | Biogen Ma Inc | Composiciones y métodos para la modulación de corte y empalme de SMN2 en un sujeto |
| EP2964270A4 (en) * | 2013-02-21 | 2017-03-22 | University Of Rochester | Methods for evaluating brain-wide paravascular pathway for waste clearance function and methods for treating neurodegenerative disorders based thereon |
| SI3702466T1 (sl) | 2013-08-27 | 2023-04-28 | Research Institute At Nationwide Children's Hospital | Proizvodi in postopki za zdravljenje amiotrofične lateralne skleroze |
| ES2739288T3 (es) | 2013-09-13 | 2020-01-30 | California Inst Of Techn | Recuperación selectiva |
| MX2017009336A (es) | 2015-01-16 | 2017-11-15 | Voyager Therapeutics Inc | Polinucleótidos dirigidos al sistema nervioso central. |
| KR102423442B1 (ko) | 2015-12-11 | 2022-07-20 | 캘리포니아 인스티튜트 오브 테크놀로지 | 아데노-관련 바이러스를 지시하기 위한 타겟팅 펩타이드 |
| WO2019094253A1 (en) | 2017-11-08 | 2019-05-16 | Avexis Inc. | Means and method for preparing viral vectors and uses of same |
| WO2019222329A1 (en) | 2018-05-15 | 2019-11-21 | Voyager Therapeutics, Inc. | Compositions and methods for delivery of aav |
| US20210214749A1 (en) | 2018-05-16 | 2021-07-15 | Voyager Therapeutics, Inc. | Directed evolution |
| US20210207167A1 (en) | 2018-05-16 | 2021-07-08 | Voyager Therapeutics, Inc. | Aav serotypes for brain specific payload delivery |
| WO2020028751A2 (en) | 2018-08-03 | 2020-02-06 | Voyager Therapeutics, Inc. | Aav variants with enhanced tropism |
| CN113226283A (zh) * | 2018-10-04 | 2021-08-06 | 罗切斯特大学 | 通过操纵血浆重量摩尔渗透压浓度改善淋巴递送 |
-
2022
- 2022-10-24 WO PCT/IB2022/060189 patent/WO2023073526A1/en not_active Ceased
- 2022-10-24 CN CN202280063874.4A patent/CN118043039A/zh active Pending
- 2022-10-24 JP JP2024523575A patent/JP2024539123A/ja active Pending
- 2022-10-24 US US18/703,559 patent/US20250235554A1/en active Pending
- 2022-10-24 EP EP22800804.1A patent/EP4422613A1/en active Pending
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